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ISIS 325568

Phase 1

Type 2 Diabetes Mellitus | Small molecule | Metabolic |Ionis Pharmaceuticals, Inc.|Last Updated: Aug 19, 2008

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindCONTROLLEDBiomarker
Total Trials1
Total Enrollment60
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00519727Safety Study of ISIS 325568 in Healthy VolunteersPHASE1 COMPLETED 60Aug 1, 2007Jun 1, 2008Aug 19, 20081 Netherlands
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Study Endpoints
Primary Endpoints
safety and tolerability
30 days for single dose, 16 weeks for multi-dose
Secondary Endpoints
Pharmacokinetic profile all doses and Pharmacodynamics for multi-dose groups.
4 days for single dose, 16 weeks for multi-dose
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Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
AEXPERIMENTAL50 mg ISIS 325568 vs Placebo, s.c. injection
BEXPERIMENTAL100 mg ISIS 325568 vs Placebo , s.c. injection
CEXPERIMENTAL200 mg ISIS 325568 vs Placebo , s.c. injection
DEXPERIMENTAL400 mg ISIS 325568 vs Placebo, s.c. injection
AAEXPERIMENTAL50 mg ISIS 325568, 3x over 1 week i.v. infusion, weekly s.c. injection for 5 weeks vs Placebo
BBEXPERIMENTAL100 mg ISIS 325568, 3x over 1 week i.v. infusion, weekly s.c. injection for 5 weeks vs Placebo
CCEXPERIMENTAL200 mg ISIS 325568, 3x over 1 week i.v. infusion, weekly s.c. injection for 5 weeks vs Placebo
DDEXPERIMENTAL400 mg ISIS 325568, 3x over 1 week i.v. infusion, weekly s.c. injection for 5 weeks vs Placebo
Interventions
NameTypeDescription
ISIS 325568DRUG4 arms of single dose s.c. injections: A 50 mg B 100 mg C 200 mg D 400 mg 4 arms of multi-dose: 3 i.v. infusions over 1 week followed by 5 weekly s.c. injections AA 50 mg BB 100 mg CC 200 mg DD 400 mg or EE 50 mg Placebo: 0.9% Sodium Chloride
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Eligibility Criteria
Age Range18 Years — 65 Years
SexALL
Healthy VolunteersYes
Study Sites1

Inclusion Criteria: 1. Age 18 to 65 years 2. Males or females. Females must be non-pregnant and non-lactating, and either surgically sterile (hysterectomy, oophorectomy, or tubal ligation) or post-menopausal. Males must be surgically sterile, abstinent or if engaged in sexual relations of child-bea...

Countries:Netherlands
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