Recent Updates
Recently added Catalysts

IONIS-AGT-LRx

Phase 2

Chronic Heart Failure With Reduced Ejection Fraction | Small molecule | Cardiovascular |Ionis Pharmaceuticals, Inc.|Last Updated: Sep 11, 2023

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
Premium
Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
Premium
Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDBiomarker
Total Trials1
Total Enrollment72
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT04836182A Study to Assess the Safety, Tolerability and Efficacy of IONIS-AGT-LRx in Participants With Chronic Heart Failure With Reduced Ejection FractionPHASE2 COMPLETED 72Jun 8, 2021Jan 11, 2023Sep 11, 202319 United States, Hungary +1
Unlock Drug Trial Details
Study Endpoints
Primary Endpoints
Percent Change in Plasma AGT Concentration From Baseline to Study Day 85
Baseline to Day 85
Secondary Endpoints
Absolute Level of Plasma AGT
Baseline to Day 169
Change in Plasma AGT From Baseline to Each Scheduled, Post-Baseline Visit
Baseline to Day 169
Percent Change in Plasma AGT From Baseline to Each Scheduled, Post-Baseline Visit
Baseline to Day 169
Unlock Study Endpoints
Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
IONIS-AGT-LRxEXPERIMENTALIONIS-AGT-LRX by subcutaneous injection once-weekly
PlaceboPLACEBO_COMPARATORMatching placebo by subcutaneous injection once-weekly
Interventions
NameTypeDescription
IONIS-AGT-LRxDRUGMultiple doses of IONIS-AGT-LRx will be administered by SC injection.
PlaceboDRUGIONIS-AGT-LRx-matching placebo will be administered by SC injection.
Unlock Study Design Details
Eligibility Criteria
Age Range18 Years — 80 Years
SexALL
Healthy VolunteersNo
Study Sites19

Inclusion Criteria: 1. Females must be non-pregnant and non-lactating and of non- childbearing potential. 2. Males must be surgically sterile or, abstinent or, if engaged in sexual relations with a woman of child-bearing potential (WOCBP), she must be willing to use a highly effective contraceptive...

Countries:United StatesHungaryPoland
Unlock Eligibility Criteria