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IONIS FXI-LRx

Phase 1

Healthy Participants | Small molecule | Other |Ionis Pharmaceuticals, Inc.|Last Updated: Jan 18, 2022

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDBiomarker
Total Trials1
Total Enrollment66
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT03582462A Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Single and Multiple Doses of IONIS FXI-LRx in up to 84 Healthy VolunteersPHASE1 COMPLETED 66Jul 9, 2018Apr 26, 2019Jan 18, 20221 Canada
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Study Endpoints
Primary Endpoints
Safety and Tolerability as Measured by the Number of Participants with Treatment-Emergent Adverse Events
Up to 232 Days
Secondary Endpoints
Cmax: maximum observed drug concentration in plasma of IONIS FXI-LRx
Up to 232 Days
Tmax: time taken to reach maximal concentration in plasma of IONIS FXI-LRx
Up to 232 Days
AUC: area under the plasma concentration time curve for IONIS FXI-LRx
Up to 232 Days
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Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
IONIS FXI-LRxEXPERIMENTALAscending single and multiple doses of IONIS FXI-LRx by subcutaneous (SC) injection.
PlaceboPLACEBO_COMPARATORSterile Normal Saline (0.9% NaCl) calculated volume to match active comparator.
Interventions
NameTypeDescription
IONIS FXI-LRxDRUGAscending single and multiple doses of IONIS FXI-LRx by subcutaneous (SC) injection
PlaceboDRUGSterile Normal Saline (0.9% NaCl) calculated volume to match active comparator
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Eligibility Criteria
Age Range18 Years — 65 Years
SexALL
Healthy VolunteersYes
Study Sites1

Inclusion Criteria * Body mass index (BMI) ≤ 35 kg/m2 * Females must be non-pregnant and non-lactating, and either surgically sterile or post-menopausal * Males must be surgically sterile, abstinent or, if engaged in sexual relations with a female of child-bearing potential, the subject must be usi...

Countries:Canada
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