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LJPC-401

Phase 2

Hereditary Hemochromatosis | Small molecule | Rare Disease |Innoviva, Inc.|Last Updated: Jun 9, 2022

Success Probability

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Trial Design

RandomizedPLACEBO_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment70

FDA Designations

No designations recorded

Clinical trial landscape

LJPC-401 · 1 trial · 1 indication

Phase 2 1
NCT03395704A Study of LJPC-401 for the Treatment of Iron Overload in Adult Patients With Hereditary HemochromatosisHereditary Hemochromatosis
COMPLETED70 Analytics
PHASE2COMPLETED
A Study of LJPC-401 for the Treatment of Iron Overload in Adult Patients With Hereditary Hemochromatosis
Hereditary HemochromatosisUnlock trial analytics

Study Endpoints

Primary Endpoints

Effect of LJPC-401 Versus Placebo on Blood Iron Levels
16 Weeks

Percentage change in transferrin saturation (TSAT) as measured by blood laboratory tests.

Secondary Endpoints

Effect of LJPC-401 Versus Placebo on Number of Phlebotomies
16 Weeks
Effect of LJPC-401 Versus Placebo on Blood Iron Levels
16 Weeks
Effect of LJPC-401 Versus Placebo on the Total Number of Treatment-emergent Adverse Events
20 Weeks
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Study Design & Arms

AllocationRANDOMIZED
MaskingSINGLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
LJPC-401ACTIVE_COMPARATORLJPC-401 solution for subcutaneous injection only, 5mg/1 mL (5mg/mL) or 10mg/1mL (10mg/mL) single use vial
PlaceboPLACEBO_COMPARATOR0.9% Sodium Chloride Injection, USP, or equivalent

Interventions

NameTypeDescription
LJPC-401DRUGLJPC-401 subcutaneous injection, up to 20 mg weekly for 16 weeks. The minimum weekly dose will be 5 mg and the maximum weekly dose of LJPC-401 will be 20 mg.
PlaceboDRUG0.9% Sodium Chloride Injection, USP, or equivalent
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites31

Inclusion Criteria: 1. Patients with clinical diagnosis of hereditary hemochromatosis 2. Patients who are prescribed therapeutic phlebotomy for treatment of hereditary hemochromatosis 3. Patients with serum ferritin and TSAT levels above treatment guidelines 4. Female patients of child bearing pote...

Countries:United StatesAustraliaFranceUnited Kingdom
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Frequently asked questions about LJPC-401

What is LJPC-401 used for?

LJPC-401 is an investigational small molecule being developed for the treatment of iron overload in adult patients with hereditary hemochromatosis, a rare disease. It is currently in Phase 2 clinical development and is not yet approved by regulatory authorities.

Who makes LJPC-401?

LJPC-401 is being developed by Innoviva, Inc., a biopharmaceutical company traded on the NASDAQ under the ticker symbol INVA. The drug is in Phase 2 clinical development for hereditary hemochromatosis.

What phase is LJPC-401 in?

LJPC-401 is in Phase 2 clinical development. It is an investigational drug and has not been approved by the FDA or any other regulatory agency. A Phase 2 clinical trial for the drug has been completed.

What clinical trials is LJPC-401 in?

LJPC-401 has one completed Phase 2 clinical trial, identified as NCT03395704, which studied the drug for the treatment of iron overload in adult patients with hereditary hemochromatosis. The trial enrolled 70 participants and was conducted in the United States, Australia, France, and the United Kingdom.

Is LJPC-401 the same as hepcidin?

No, LJPC-401 is not the same as hepcidin. LJPC-401 is a small molecule being developed by Innoviva, Inc. for hereditary hemochromatosis. Hepcidin is a naturally occurring hormone that regulates iron levels, but LJPC-401 is a distinct investigational drug.