Recent Updates
Recently added Catalysts

Pembrolizumab

Phase 3

UC (Urothelial Cancer) | Small molecule | Oncology |Incyte Corporation|Last Updated: May 22, 2026

Success Probability
Subscribe to view
Market & Valuation
Subscribe to view
Trial Design
RandomizedACTIVE_CONTROLLEDDMC
Total Trials2
Total Enrollment177
FDA Designations
No designations recorded
Clinical trial landscape

Pembrolizumab · 9 trials · 12 indications

Phase 3 4Phase 2 4Phase 1 1
NCT03374488Pembrolizumab + Epacadostat vs Pembrolizumab + Placebo in Recurrent or Progressive Metastatic Urothelial CarcinomaUC (Urothelial Cancer)
COMPLETED84 Analytics
NCT03260894Pembrolizumab (MK-3475) Plus Epacadostat vs Standard of Care in mRCC (KEYNOTE-679/ECHO-302)Renal Cell Carcinoma (RCC)
COMPLETED129 Analytics
NCT03361865Pembrolizumab in Combination With Epacadostat or Placebo in Cisplatin-ineligible Urothelial Carcinoma (KEYNOTE-672/ECHO-307)UC (Urothelial Cancer)
COMPLETED93 Analytics
NCT03358472Pembrolizumab Plus Epacadostat, Pembrolizumab Monotherapy, and the EXTREME Regimen in Recurrent or Metastatic Head and Neck Squamous Cell Carcinoma (KEYNOTE-669/ECHO-304)Head and Neck Cancer
COMPLETED89 Analytics
PHASE3COMPLETED
Pembrolizumab + Epacadostat vs Pembrolizumab + Placebo in Recurrent or Progressive Metastatic Urothelial Carcinoma
UC (Urothelial Cancer)Unlock trial analytics
PHASE3COMPLETED
Pembrolizumab (MK-3475) Plus Epacadostat vs Standard of Care in mRCC (KEYNOTE-679/ECHO-302)
Renal Cell Carcinoma (RCC)Unlock trial analytics
PHASE3COMPLETED
Pembrolizumab in Combination With Epacadostat or Placebo in Cisplatin-ineligible Urothelial Carcinoma (KEYNOTE-672/ECHO-307)
UC (Urothelial Cancer)Unlock trial analytics
PHASE3COMPLETED
Pembrolizumab Plus Epacadostat, Pembrolizumab Monotherapy, and the EXTREME Regimen in Recurrent or Metastatic Head and Neck Squamous Cell Carcinoma (KEYNOTE-669/ECHO-304)
Head and Neck CancerUnlock trial analytics
Study Endpoints
Primary Endpoints
Objective Response Rate (ORR) With Pembrolizumab + Epacadostat Versus Pembrolizumab + Placebo
up to 9 weeks +14 days

ORR was defined as the percentage of participants who had a complete response (CR), disappearance of all target lesions or partial response (PR), \>=30% decrease in the sum of the longest diameter of target lesions per RECIST v1.1 by investigator determination.

Objective Response Rate (ORR) of Pembrolizumab + Epacadostat Versus Standard of Care (SOC)
up to approximately 8 months

ORR was defined as the percentage of participants who had complete response (CR) or partial response (PR) per RECIST v1.1 by investigator determination.

Objective Response Rate (ORR) of Pembrolizumab + Epacadostat, Pembrolizumab Monotherapy and the EXTREME Regimen
Minimum Week 9

ORR was defined as the percentage of participants who had a complete response (CR), disappearance of all target lesions or partial response (PR), \>=30% decrease in the sum of the longest diameter of target lesions per RECIST v1.1 by investigator determination. Responses are based on investigator assessments per RECIST 1.1 without confirmation using all available scans.

Overall Response Rate (ORR)
From start of study treatment until subject proceeds to standard of care treatment, up to 2 years.

The proportion of patients with confirmed PR or CR per RECIST v1.1, assessed from the start of study treatment (defined as from first dose of pembrolizumab) for up to two years. ORR in the non-targeted, unirradiated lesion(s) as defined by CR or PR per iRECIST. Objective response will be assessed separately in all sites that are not irradiated.

Pathological complete response (pCR) rate.
From treatment start date until the time of curative-intent treatment, approximately 7 weeks.

The proportion of patients with absence of invasive disease in the breast and lymph nodes at the time of SOC curative-intent treatment.

Objective Response Rate (ORR) of Pembrolizumab + Chemotherapy + Epacadostat Versus Pembrolizumab + Chemotherapy + Placebo
Assessed every 12 weeks up to 24 months

ORR is defined as the percentage of participants who have a confirmed complete response (CR) or partial response (PR) per Response Evaluation Criteria in Solid Tumors (RECIST 1.1) based on blinded independent central review (BICR).

Objective Response Rate (ORR) of Pembrolizumab Plus Epacadostat Versus Pembrolizumab Plus Placebo
Up to approximately 6 months

ORR is defined as the proportion of participants who have a confirmed complete response (CR) or partial response (PR) per Response Evaluation Criteria in Solid Tumors (RECIST) v1.1 based on blinded independent central review (BICR).

Part 1: Evaluation of safety and tolerability as measured by the frequency, duration, and severity of adverse events
Duration of study treatment and up to 120 days after the last dose of study drug
Secondary Endpoints
Safety and Tolerability of Pembrolizumab + Epacadostat Versus Pembrolizumab + Placebo as Measured by Number of Participants Experiencing Adverse Events (AEs)
Up to 8 months
Safety and Tolerability of Pembrolizumab + Epacadostat Versus Pembrolizumab + Placebo as Measured by Number of Participants Discontinuing Study Treatment Due to AE
Up to 8 months
Safety and Tolerability of Pembrolizumab + Epacadostat Versus SOC as Measured by the Number of Participants Experiencing Adverse Events (AEs)
Data reported from start of study to data cutoff 28-Feb-2019, up to 15 months.
Unlock Study Endpoints
Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Pembrolizumab 200 mg + Epacadostat 100 mg BIDEXPERIMENTALPembrolizumab + epacadostat
Pembrolizumab 200 mg + placebo BIDACTIVE_COMPARATORPembrolizumab + placebo
Pembrolizumab + EpacadostatEXPERIMENTAL -
SoC (Sunitinib or Pazopanib)ACTIVE_COMPARATORStandard of care (SoC) (sunitinib or pazopanib monotherapy).
PembrolizumabEXPERIMENTAL -
EXTREMEACTIVE_COMPARATOREXTREME regimen includes cetuximab + cisplatin or carboplatin + 5-fluorouracil.
Pembrolizumab, Radiotherapy, AxatilimabEXPERIMENTALPembrolizumab (MK-3475), 200 mg IV Q3W starting at C1D1/Week 1 for up to 2 years, until disease progression, or treatment intolerance. Radiotherapy, 8 Gy x 3 fractions over 3 consecutive days at C1D8/Week 2; Axatilimab (SNDX-6352; INCA034176), 1 mg/kg, IV, Q2W starting 1 week post- RT C1D15/Week 3 until disease progression or treatment intolerance.
Pembrolizumab with Radiation Therapy and AxatilimabEXPERIMENTAL -
Pembrolizumab + Chemotherapy + EpacadostatEXPERIMENTALParticipant received pembrolizumab 200 mg intravenous (IV) infusion, every 3 weeks (Q3W) on Day 1 of each 21 day cycle for up to 35 cycles + epacadostat 100 mg tablets, orally, twice daily (BID) in each 21 day cycle for up to 35 cycles + platinum-doublet chemotherapy (pemetrexed 500 mg/m\^2 IV infusion, Q3W + cisplatin 75 mg/m\^2 IV infusion, Q3W or carboplatin 5-6 mg/mL/min IV infusion Q3W for 4 cycles followed by pemetrexed maintenance; or paclitaxel 200 mg /m\^2 IV infusion, Q3W + carboplatin 5-6 mg/mL/min IV infusion Q3W for 4 cycles).
Pembrolizumab + Chemotherapy + PlaceboEXPERIMENTALParticipant received pembrolizumab 200 mg IV infusion, Q3W on Day 1 of each 21 day cycle for up to 35 cycles + epacadostat matching placebo tablets, orally, BID in each 21 day cycle for up to 35 cycles + platinum-doublet chemotherapy (pemetrexed 500 mg/m\^2 IV infusion, Q3W + cisplatin 75 mg/m\^2 IV infusion, Q3W or carboplatin 5-6 mg/mL/min IV infusion Q3W for 4 cycles followed by pemetrexed maintenance; or paclitaxel 200 mg /m\^2 IV infusion, Q3W + carboplatin 5-6 mg/mL/min IV infusion Q3W for 4 cycles).
Pembrolizumab + PlaceboACTIVE_COMPARATORParticipants received pembrolizumab 200 mg by IV infusion, Q3W starting on Day 1 of each cycle for up to 35 administrations in combination with matching placebo orally, twice daily. Placebo administration was discontinued after the implementation of protocol amendment 05.
pembrolizumab + itacitinibEXPERIMENTALPart 1a Group A will utilize an open-label 3+3 dose-escalation design based on observing each dose level for a period of 21 days. Part 1b Group A-1 and Group A-2 will evaluate the MTD or PAD of itacitinib in combination with pembrolizumab in subjects with select solid tumors.
pembrolizumab + INCB050465EXPERIMENTALPart 1a Group B will utilize an open-label 3+3 dose-escalation design based on observing each dose level for a period of 21 days. Part 1b Group B-1 and Group B-2 will evaluate the MTD or PAD of INCB050465 in combination with pembrolizumab in subjects with select solid tumors. Part 2 will evaluate the combination of INCB050465 in combination with pembrolizumab in subjects with small cell lung cancer, non-small lung cancer and urothelial cancer.
Interventions
NameTypeDescription
PembrolizumabDRUGPembrolizumab administered intravenously Day 1 of each cycle every 3 weeks.
EpacadostatDRUGEpacadostat administered orally twice daily.
PlaceboDRUGMatching placebo administered orally twice daily.
SunitinibDRUGSunitinib 50 mg administered orally once daily; 4 weeks on, 2 weeks off for 6-wk cycle.
PazopanibDRUGPazopanib 800 mg administered orally once daily.
CetuximabDRUGCetuximab administered intravenously on Cycle 1 Day 1 followed by administration every week.
CisplatinDRUGCisplatin administered intravenously every 3 weeks for \</= 6 cycles.
CarboplatinDRUGCarboplatin administered intravenously every 3 weeks for \</= 6 cycles.
5-FluorouracilDRUG5-Fluorouracil administered intravenously every 3 weeks for \</= 6 cycles.
RadiotherapyRADIATIONRT, 8 Gy x 3 fractions over 3 consecutive days at C1D8/Week 2;
AxatilimabDRUGAxatilimab (SNDX-6352; INCA034176), 1 mg/kg, IV, Q2W starting 1 week post- RT C1D15/Week 3 until disease progression or treatment intolerance.
Radiation TherapyRADIATIONRadiation therapy (RT) consists of 8 Gy for 3 fractions over 3 consecutive days at Week 2.
Platinum-based chemotherapyDRUGInvestigator selected one of the following regimens: pemetrexed + cisplatin, pemetrexed + carboplatin, or paclitaxel + carboplatin, depending on histology.
itacitinibDRUGItacitinib tablets administered orally once daily.
INCB050465DRUGINCB050465 tablets administered orally once daily.
Unlock Study Design Details
Eligibility Criteria
Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites135

Inclusion Criteria: * Histologically-confirmed diagnosis of urothelial carcinoma of the renal pelvis, ureter, bladder, or urethra, that is transitional cell, or mixed transitional/non-transitional (predominantly transitional) cell type. * Progression or recurrence of urothelial carcinoma following ...

Countries:United StatesAustraliaCanadaDenmarkFranceGermanyHungaryIrelandIsraelItalyJapanNetherlandsRussiaSouth KoreaSpainTaiwanTurkey (Türkiye)United KingdomBrazilChileNew ZealandNorwayUkraineBelgiumPolandAustriaPortugalMexicoEstoniaMalaysiaSwitzerland
Unlock Eligibility Criteria
Recent Changes (Last 90 Days)
MEDIUMJun 22, 2026NCT03260894TRIAL_REMOVED: changed
MEDIUMJun 22, 2026NCT03260894TRIAL_REMOVED: changed
MEDIUMJun 22, 2026NCT03260894TRIAL_REMOVED: changed
LOWMay 26, 2026NCT05491226Status: ACTIVE_NOT_RECRUITING → RECRUITING
MEDIUMMay 26, 2026NCT07015853primaryCompletionDate: changed
LOWMay 24, 2026NCT07015853studyFirstPostDate: changed
LOWMay 24, 2026NCT05491226studyFirstPostDate: changed