Recent Updates
Recently added Catalysts

INCB001158

Phase 1

Biliary Tract Cancer (BTC) | Small molecule | Oncology |Incyte Corporation|Last Updated: Aug 12, 2025

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

CONTROLLED
Total Trials1
Total Enrollment149

FDA Designations

No designations recorded

Clinical trial landscape

INCB001158 · 2 trials · 14 indications

Phase 1 2
NCT03314935A Phase 1/2 Study of INCB001158 in Combination With Chemotherapy in Subjects With Solid TumorsBiliary Tract Cancer (BTC)
COMPLETED149 Analytics
NCT02903914Arginase Inhibitor INCB001158 as a Single Agent and in Combination With Immune Checkpoint Therapy in Patients With Advanced/Metastatic Solid TumorsMetastatic Cancer
COMPLETED260 Analytics
PHASE1COMPLETED
A Phase 1/2 Study of INCB001158 in Combination With Chemotherapy in Subjects With Solid Tumors
Biliary Tract Cancer (BTC)Unlock trial analytics
PHASE1COMPLETED
Arginase Inhibitor INCB001158 as a Single Agent and in Combination With Immune Checkpoint Therapy in Patients With Advanced/Metastatic Solid Tumors
Metastatic CancerUnlock trial analytics

Study Endpoints

Primary Endpoints

Phases 1 and 2: Number of Participants With Any Treatment-emergent Adverse Event (TEAE)
up to 1385 days

An adverse event (AE) was defined as any untoward medical occurrence associated with the use of a drug in humans, whether or not considered drug related, that occurred after a participant provided informed consent. Abnormal laboratory values or test results occurring after informed consent constituted AEs only if they induced clinical signs or symptoms, were considered clinically meaningful, required therapy (e.g., hematologic abnormality that required transfusion), or required changes in the study drug(s). A TEAE was defined as any AE either reported for the first time or the worsening of a pre-existing event after the first dose of study drug.

Phase 1: Number of Participants With Any Dose-limiting Toxicity (DLT)
up to Day 28

A DLT was defined as the occurrence of any protocol-defined toxicity occurring up to and including Day 28, except those with a clear alternative explanation (e.g., disease progression) or transient (≤72 hours) abnormal laboratory values without associated clinically significant signs or symptoms based on investigator determination. All DLTs were assessed by the investigator using Common Terminology Criteria for Adverse Events (CTCAE) v4.03 criteria.

Recommended Phase 2 Dose (RP2D) of INCB001158 When Given in Combination With Each Chemotherapy Regimen
up to Day 580

The RP2D of the combination of INCB001158 and chemotherapy in 21-day (for gemcitabine/cisplatin) or 28-day (for mFOLFOX6 or paclitaxel) treatment cycles in participants with advanced or metastatic solid tumors was determined. After the dose escalation was completed, the INCB001158 dose level that was pharmacologically active and tolerable in combination with each chemotherapy regimen (i.e., maximum tolerated dose or lower) was determined to be the RP2D. The RP2D was then further assessed in tumor expansion cohorts in Phase 2.

Phase 2: Objective Response Rate (ORR)
up to 1385 days

ORR was defined as the percentage of participants with a best overall response of complete response (CR) or partial response (PR), as determined by investigator assessment of radiographic disease as per Response Evaluation Criteria in Solid Tumors (RECIST) version 1.1 (v1.1). CR: disappearance of all target and non-target lesions and no appearance of any new lesions. Any pathological lymph nodes (whether target or non-target) must have a reduction in the short axis to \<10 millimeters (mm). PR: complete disappearance or at least a 30% decrease in the sum of the diameters of target lesions, taking as a reference the baseline sum diameters, no new lesions, and no progression of non-target lesions. Analysis was conducted by cohort (tumor type) in Phase 2 because different tumor types could have different response criteria or different background response rates.

Number of Participants With Any Treatment-emergent Adverse Event (TEAE)
up to study completion (up to approximately 3.5 years)

An adverse event (AE) was defined as any untoward medical occurrence associated with the use of a drug in humans, whether or not considered drug related, that occurred after a participant provided informed consent. Abnormal laboratory values or test results occurring after informed consent constituted AEs only if they induced clinical signs or symptoms, were considered clinically meaningful, required therapy (e.g., hematologic abnormality that required transfusion), or required changes in the study treatment(s). A TEAE was defined as any adverse event that started or worsened after the first dose of study drug.

Secondary Endpoints

Phase 1: ORR
up to 580 days
Phases 1 and 2: Duration of Response
up to 368 days
Phases 1 and 2: Disease Control Rate
up to 1385 days
Unlock Study Endpoints

Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Treatment Group AEXPERIMENTALINCB001158 + FOLFOX
Treatment Group BEXPERIMENTALINCB001158 + gemcitabine/cisplatin
Treatment Group CEXPERIMENTALINCB001158 + paclitaxel
INCB00158 was administered as monotherapy at 50mg twice dailyEXPERIMENTALMonotherapy Part 1a: INCB001158 administered orally in patients with advanced/metastatic solid tumors. Escalating doses will be explored to determine the recommended phase 2 dose (RP2D).
INCB00158 was administered as monotherapy at 75mg twice dailyEXPERIMENTALMonotherapy Part 2a: INCB001158 administered orally at the RP2D in patients with advanced/metastatic NSCLC (EGFR and Anaplastic Lymphoma Kinase (ALK) negative) previously treated with Standard of Care (SOC).
INCB00158 was administered as monotherapy at 100mg twice dailyEXPERIMENTALMonotherapy Part 2b: INCB001158 administered orally at the RP2D in patients with advanced/metastatic CRC previously treated with SOC.
INCB00158 was administered as monotherapy at 150mg twice dailyEXPERIMENTALMonotherapy Part 2c: INCB001158 administered orally at the RP2D in patients with Bladder Cancer, Gastric or Gastroesophageal Junction (GEJ) Cancer, Renal Cell Cancer (RCC), Squamous Cell Carcinoma of the Head and Neck (SCCHN), Urothelial Cell Cancer (UCC), or Melanoma, previously treated with SOC.
INCB00158 was administered in combination with pembroluzimab at 50mg twice dailyEXPERIMENTALMonotherapy Part 2d: INCB001158 administered orally at the RP2D in patients with any tumor types in Parts 2a, 2b, or 2c.
INCB00158 was administered in combination with pembroluzimab at 75mg twice dailyEXPERIMENTALCombination Part 1b: INCB001158 and Pembrolizumab administered in patients with advanced/metastatic NSCLC, Melanoma, Urothelial Cell Cancer, MSI CRC, MSS CRC, Gastric or Gastroesophageal Junction (GEJ) Cancer, SCCHN and Mesothelioma. Multiple dose levels will be explored to determine the recommended phase 2 dose (RP2D).
INCB00158 was administered in combination with pembroluzimab at 100mg twice dailyEXPERIMENTALPart 3a: INCB001158 and Pembrolizumab the combination RP2D in patients with advanced/metastatic NSCLC (EGFR and ALK negative) with disease progression on anti-PD-1 therapy or prolonged stable disease on Pembrolizumab in the immediate prior line of therapy.
INCB001158 50 mg BID in combination with pembrolizumabEXPERIMENTALPart C: evaluated a reduced dose of INCB001158 50 mg BID in combination with pembrolizumab with patients with moderately impaired renal function.

Interventions

NameTypeDescription
INCB001158DRUGPhase 1: INCB001158 administered orally twice daily at the protocol-defined dose. Phase 2: INCB001158 administered orally twice daily at the recommended dose from Phase 1.
OxaliplatinDRUGOxaliplatin administered intravenously at the protocol-defined dose and schedule.
LeucovorinDRUGLeucovorin at the protocol-defined dose and regimen.
5-FluorouracilDRUG5-Fluorouracil at the protocol-defined dose and regimen.
GemcitabineDRUGGemcitabine at the protocol-defined dose and regimen.
CisplatinDRUGCisplatin at the protocol-defined dose and regimen.
PaclitaxelDRUGPaclitaxel at the protocol-defined dose and regimen.
PembrolizumabDRUGPD-1 Inhibitor
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites10

Inclusion Criteria: * Histologically or cytologically confirmed diagnosis of selected advanced or metastatic solid tumors. * Presence of measurable disease per RECIST v1.1. * Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1. * Baseline archival tumor specimen available or will...

Countries:United StatesBelgiumUnited KingdomItalyNetherlandsSpain
Unlock Eligibility Criteria

Frequently asked questions about INCB001158

What is INCB001158 used for?

INCB001158 is an investigational small molecule being studied for the treatment of Biliary Tract Cancer (BTC) and Metastatic Cancer. It has been evaluated in clinical trials for advanced or metastatic solid tumors, including colorectal, gastric, head and neck, lung, renal cell, bladder, urothelial, and mesothelioma cancers.

How does INCB001158 work?

INCB001158 is an arginase inhibitor. It works by blocking the enzyme arginase, which is involved in the breakdown of arginine, an amino acid essential for T-cell function. By inhibiting arginase, INCB001158 aims to enhance the immune system's ability to fight cancer cells.

Who is developing INCB001158?

INCB001158 is being developed by Incyte Corporation, a biopharmaceutical company traded on the NASDAQ under the ticker symbol INCY. Incyte is conducting clinical trials to evaluate the safety and efficacy of this investigational drug in patients with various solid tumors.

What phase is INCB001158 in?

INCB001158 is in Phase 1 clinical development. It has completed two Phase 1 trials, one as a single agent and in combination with immune checkpoint therapy, and another in combination with chemotherapy. The drug is investigational and has not been approved by regulatory authorities.

What clinical trials is INCB001158 in?

INCB001158 has been studied in two completed clinical trials. NCT02903914 evaluated it as a single agent and in combination with immune checkpoint therapy in patients with advanced or metastatic solid tumors. NCT03314935 studied it in combination with chemotherapy in subjects with solid tumors, including biliary tract cancer.

Is INCB001158 the same as any other drug?

INCB001158 is also known by the name 1,158 in some contexts, but no other alternative names have been reported. It is a distinct investigational compound developed by Incyte Corporation and is not the same as any approved drug.