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INBRX-101/rhAAT-Fc

Phase 1

Alpha-1 Antitrypsin Deficiency | Small molecule | Rare Disease |Inhibrx Biosciences, Inc.|Last Updated: Sep 13, 2022

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDDMC
Total Trials1
Total Enrollment31

FDA Designations

No designations recorded

Clinical trial landscape

INBRX-101/rhAAT-Fc · 1 trial · 2 indications

Phase 1 1
NCT03815396Phase 1 Study to Assess the Safety, PK and PD of INBRX-101 in Adults With Alpha-1 Antitrypsin DeficiencyAlpha-1 Antitrypsin Deficiency
COMPLETED31 Analytics
PHASE1COMPLETED
Phase 1 Study to Assess the Safety, PK and PD of INBRX-101 in Adults With Alpha-1 Antitrypsin Deficiency
Alpha-1 Antitrypsin DeficiencyUnlock trial analytics

Study Endpoints

Primary Endpoints

Frequency of adverse events of INBRX-101
Up to 7 months

Adverse events will be assessed by the National Cancer Institute Common Terminology Criteria for Adverse Events (NCI CTCAE), version 4.03.

Severity of adverse events of INBRX-101
Up to 7 months

Severity of adverse events will be assessed and assigned by the National Cancer Institute Common Terminology Criteria for Adverse Events (NCI CTCAE), version 4.03.

Secondary Endpoints

Area under the serum concentration time curve (AUC) of INBRX-101
Up to 7 months
Maximum observed serum concentration (Cmax) of INBRX-101
Up to 7 months
Trough observed serum concentration (Ctrough) of INBRX-101
Up to 7 months
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Part 1 Single Ascending DoseEXPERIMENTALINBRX-101 will be escalated in subjects with alpha-1 antitrypsin deficiency (AATD).
Part 2 Multiple Ascending DoseEXPERIMENTALINBRX-101 will be escalated in subjects with alpha-1 antitrypsin deficiency (AATD).

Interventions

NameTypeDescription
INBRX-101/rhAAT-FcDRUGINBRX-101 is a recombinant human alpha-1 antitrypsin (AAT) Fc fusion protein (rhAAT-Fc).
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Eligibility Criteria

Age Range18 Years to 80 Years
SexALL
Healthy VolunteersNo
Study Sites10

Inclusion Criteria: * Documented alpha-1 antitrypsin (AAT) serum concentration \<11 μM. * Diagnosis of alpha-1 antitrypsin deficiency (AATD) with any allelic combination with exception of the null/null genotype. * For subjects in Part 2 80 and 120 mg/kg cohorts ONLY: post-bronchodilator FEV1 of at ...

Countries:United StatesNew ZealandUnited Kingdom
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Frequently asked questions about INBRX-101/rhAAT-Fc

What is INBRX-101 used for?

INBRX-101 is an investigational therapy being developed for the treatment of Alpha-1 Antitrypsin Deficiency (AATD), a rare genetic condition. It is designed to address the underlying deficiency of alpha-1 antitrypsin protein. The drug is currently in clinical development and has not been approved by regulatory authorities.

Who is developing INBRX-101?

INBRX-101 is being developed by Inhibrx Biosciences, Inc., a biopharmaceutical company. The company is listed on the stock exchange under the ticker symbol INBX. Inhibrx is conducting clinical trials to evaluate the safety and efficacy of INBRX-101 in patients with Alpha-1 Antitrypsin Deficiency.

What phase is INBRX-101 in?

INBRX-101 is in Phase 1 clinical development. A Phase 1 study has been completed to assess its safety, pharmacokinetics, and pharmacodynamics in adults with Alpha-1 Antitrypsin Deficiency. The drug is still investigational and has not received FDA approval for any indication.

What clinical trials is INBRX-101 in?

INBRX-101 has been studied in a Phase 1 clinical trial with the identifier NCT03815396. This completed trial enrolled 31 participants with Alpha-1 Antitrypsin Deficiency across the United States, New Zealand, and the United Kingdom. The study was controlled but not randomized or double-blinded.

Is INBRX-101 the same as rhAAT-Fc?

Yes, INBRX-101 is also known as rhAAT-Fc. This alternative name refers to the recombinant human alpha-1 antitrypsin with an Fc fusion component. Both names refer to the same investigational drug being developed for Alpha-1 Antitrypsin Deficiency.