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Mycophenolate mofetil

Phase 2

Acute Myeloid Leukemia | Small molecule | Oncology |ImmunityBio, Inc.|Last Updated: Jun 25, 2026

Target and mechanism

Molecular targetIMPDH1, IMPDH2
Target classInhibitor
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDDMC
Total Trials1
Total Enrollment60

FDA Designations

No designations recorded

Clinical trial landscape

Mycophenolate mofetil · 1 trial · 1 indication

Phase 2 1
NCT02782546Cytokine Induced Memory-like NK Cell Adoptive Therapy After Haploidentical Donor Hematopoietic Cell TransplantationAcute Myeloid Leukemia
ACTIVE NOT_RECRUITING60 Analytics
PHASE2ACTIVE NOT_RECRUITING
Cytokine Induced Memory-like NK Cell Adoptive Therapy After Haploidentical Donor Hematopoietic Cell Transplantation
Acute Myeloid LeukemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Kaplan-Meier Estimate of Leukemia-free Survival Rate (LFS)
1 year post transplantation

-LFS is defined as the time from achievement of complete remission (CR) to the time of relapse, death in remission, or last follow-up.

Secondary Endpoints

Kaplan-Meier Estimate of Leukemia-free Survival Rate (LFS)
3 months post transplantation
Kaplan-Meier Estimate of Overall Survival (OS)
1 year post transplantation
Number of Recipients With Relapse Who Are Found to be CR (Complete Remission)
Day 28 post transplantation
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
RecipientEXPERIMENTAL* Standard of care reduced conditioning regimen on Day -1 * Graft cell infusion on Day 0 * Post-transplant cyclophosphamide on Days +3 and +4 * GvHD prophylaxis with tacrolimus and mycophenolate mofetil (MMF) will start on Day +5. MMF will continue till Day +35 and tacrolimus till Day +180 in the absence of GvHD * G-CSF will start on Day +7 and will continue until neutrophil engraftment as per institutional guidelines * The cytokine-induced memory like natural killer (CIML NK) cells will be infused on Day +7 without a filter or pump, slowly by gravity over at least 15 minutes. * ALT-803 will start approximately 4 hours after the CIML NK cell infusion. ALT-803 will be administered subcutaneously at a dose of 10 mcg/kg subcutaneously beginning Day +7 (on the day of CIML NK cell infusion) and then every 21 days for a total of 4 doses
DonorEXPERIMENTAL* Donors will receive subcutaneous G-CSF from Day -4 till Day 0 and undergo 20L apheresis per institutional guidelines. * Two consecutive days for collection are allowed in case of the target CD34+ cell dose being less than the target 4 x106/kg-bw from the first day of collection. * On Day +6 (one day before the planned CIML NK cell infusion), peripheral blood mononuclear cells will be collected by a single standard 20-L apheresis over 4-5 hours from the same haploidentical related donor that provided the HCT graft.

Interventions

NameTypeDescription
Graft cell infusionPROCEDURE-Day 0
TacrolimusDRUG-GVHD prophylaxis
Mycophenolate mofetilDRUG-GVHD prophylaxis
G-CSFDRUG-Continue until neutrophil engraftment as per institutional guidelines
CIML NK cell infusionPROCEDURE-Day +7
ALT-803DRUG-Start approximately 4 hours after CIML NK cell infusion
LeukapheresisPROCEDURE-Day +6
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites1

Recipient Inclusion Criteria: * Refractory AML without complete remission (CR) after 2 or more cycles of induction therapy (primary induction failure), or AML relapsed after obtaining a CR and failed one or more cycles of re-induction therapy. Standard dose 10-day decitabine (20 mg/m2 daily IV x 10...

Countries:United States
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Recent Changes (Last 90 Days)

LOWJun 25, 2026NCT02782546lastUpdatePostDate: changed
LOWJun 25, 2026NCT02782546lastUpdatePostDate: changed
LOWJun 25, 2026NCT02782546lastUpdatePostDate: changed

Frequently asked questions about Mycophenolate mofetil

What is Mycophenolate mofetil used for in Acute Myeloid Leukemia?

Mycophenolate mofetil is being studied as part of a Phase 2 clinical trial for Acute Myeloid Leukemia (AML). The trial combines cytokine-induced memory-like NK cell adoptive therapy after haploidentical donor hematopoietic cell transplantation. It is an investigational small molecule in development by ImmunityBio, Inc. for this oncology indication.

What does Mycophenolate mofetil target?

Mycophenolate mofetil is a small molecule, but its specific molecular target is not disclosed in the available information. It is being evaluated in a Phase 2 trial for Acute Myeloid Leukemia, where it is used in combination with cytokine-induced memory-like NK cell adoptive therapy after haploidentical donor hematopoietic cell transplantation.

Who makes Mycophenolate mofetil?

Mycophenolate mofetil is being developed by ImmunityBio, Inc., a biopharmaceutical company traded on the stock exchange under the ticker symbol IBRX. The company is conducting a Phase 2 clinical trial for this drug in Acute Myeloid Leukemia.

What phase is Mycophenolate mofetil in?

Mycophenolate mofetil is in Phase 2 clinical development for Acute Myeloid Leukemia. It is an investigational drug and has not been approved by regulatory authorities. The ongoing trial is active but not recruiting participants, with a planned enrollment of 60 patients.

What clinical trials is Mycophenolate mofetil in?

Mycophenolate mofetil is being studied in the clinical trial NCT02782546, titled 'Cytokine Induced Memory-like NK Cell Adoptive Therapy After Haploidentical Donor Hematopoietic Cell Transplantation.' This Phase 2 trial is active but not recruiting, enrolling 60 adults with Acute Myeloid Leukemia in the United States.