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VAL-083

Phase 2

Glioma | Small molecule | Oncology |TuHURA Biosciences, Inc.|Last Updated: Sep 4, 2025

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDBiomarker
Total Trials3
Total Enrollment202

FDA Designations

No designations recorded

Clinical trial landscape

VAL-083 · 3 trials · 5 indications

Phase 2 2Phase 1 1
NCT03050736Safety Study of VAL-083 and Radiotherapy in Patients With Newly Diagnosed GBM Having Unmethylated MGMT ExpressionGlioma
COMPLETED29 Analytics
NCT02717962Study of VAL-083 in Patients With MGMT Unmethylated, Bevacizumab-naive Glioblastoma in the Adjuvant or Recurrent SettingGlioma
COMPLETED118 Analytics
PHASE2COMPLETED
Safety Study of VAL-083 and Radiotherapy in Patients With Newly Diagnosed GBM Having Unmethylated MGMT Expression
GliomaUnlock trial analytics
PHASE2COMPLETED
Study of VAL-083 in Patients With MGMT Unmethylated, Bevacizumab-naive Glioblastoma in the Adjuvant or Recurrent Setting
GliomaUnlock trial analytics

Study Endpoints

Primary Endpoints

Efficacy evaluation of tumor response in patients, as measured by magnetic resonance imaging
Every 42 days while receiving radiotherapy then every 63 days while remaining on study, from patient randomization until study discontinuation for up to 10 months

Tumor response assessment via MRI, as long as patient continues to demonstrate response or stable disease and tolerates therapy.

Overall Survival
Every 30 days from randomization until patient death

Length of time from start of treatment (Day 1) until patient death

Determination of maximum tolerated dose (MTD)
Study Day 35

The determination of MTD will be based on analysis of tolerance data from the first cycle of therapy in each dose group.

Secondary Endpoints

Safety evaluation of VAL-083 in combination with a standard radiation therapy, as determined by incidence of patient adverse events and changes in laboratory results, ECG and vital signs
Every 30 days, from patient randomization through 28 days following last study treatment for up to 10 months
Ctrough
On Cycle 1 Day 1 pre-dose, and 15, 30, 60, 120, 240 and 360 minutes after study drug administration then Cycle 1 Day 2 pre-dose
Cmax
On Cycle 1 Day 1 pre-dose, and 15, 30, 60, 120, 240 and 360 minutes after study drug administration then Cycle 1 Day 2 pre-dose
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
VAL-083 (Dianhydrogalactitol)EXPERIMENTALVAL-083 given by intravenous infusion with a starting dose of 20 mg/m2 IV. Escalating doses to be administered in sequential dose cohorts.
VAL-083, Dianhydrogalactitol (Group 1)EXPERIMENTALPatients with recurrent/progressive GBM
VAL-083, Dianhydrogalactitol (Group 2)EXPERIMENTALNewly diagnosed GBM patients who have completed chemoradiation treatment with temozolomide and received no subsequent maintenance temozolomide

Interventions

NameTypeDescription
VAL-083 (Dianhydrogalactitol)DRUGVAL-083 given by intravenous infusion with a starting dose of 20 mg/m2 IV. Escalating doses to be administered in sequential dose cohorts.
VAL-083, DianhydrogalactitolDRUGThe dosing regimen for patients will be VAL-083 (30 mg/m2) administered IV for 3 consecutive days at the beginning of every 21-day cycle. Patients will continue to receive VAL 083, for up to 12, 21-day treatment cycles or until they fulfill one of the criteria for study discontinuation.
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Eligibility Criteria

Age Range18 Years to 69 Years
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: 1. Newly diagnosed histologically proven supratentorial GBM 2. Tumor tissue specimens from the GBM surgery or open biopsy must be available for MGMT gene promoter status analysis and central pathology review. 3. Documented unmethylated MGMT gene promoter status 4. Males or femal...

Countries:ChinaUnited States
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Frequently asked questions about VAL-083

What is VAL-083 used for in glioma?

VAL-083 is an investigational small molecule being studied for the treatment of glioma, including glioblastoma and glioblastoma multiforme. It is being developed by TuHURA Biosciences, Inc. (NASDAQ: HURA) and is currently in Phase 2 clinical development for this indication.

What does VAL-083 target?

VAL-083 is a small molecule that has been studied in patients with MGMT unmethylated glioblastoma. It is being evaluated in this biomarker-selected patient population, where the MGMT promoter methylation status is used to identify patients who may be eligible for treatment with VAL-083.

Who is developing VAL-083?

VAL-083 is being developed by TuHURA Biosciences, Inc., a biopharmaceutical company traded on NASDAQ under the ticker symbol HURA. The company is conducting clinical trials of VAL-083 in patients with glioma, including glioblastoma.

What phase is VAL-083 in?

VAL-083 is in Phase 2 clinical development for glioma. It has completed three clinical trials, including two Phase 2 studies and one Phase 1 study. VAL-083 is an investigational drug and has not been approved by regulatory authorities.

What clinical trials has VAL-083 been in?

VAL-083 has been studied in three completed clinical trials. These include NCT01478178, a Phase 1 safety study in patients with recurrent malignant glioma; NCT02717962, a Phase 2 study in patients with MGMT unmethylated, bevacizumab-naive glioblastoma; and NCT03050736, a Phase 2 study of VAL-083 combined with radiotherapy in newly diagnosed glioblastoma patients with unmethylated MGMT expression.

Is VAL-083 the same as any other drug?

VAL-083 is the drug name used in clinical trials for this investigational small molecule. No alternative names for VAL-083 have been reported in the clinical trial information available.