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Coagulation Factor VIIa variant

Phase 2

Hemophilia A With Inhibitor | Monoclonal antibody | Hematology |Gyre Therapeutics, Inc.|Last Updated: Sep 22, 2021

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLED
Total Trials1
Total Enrollment11
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT03407651Study of Coagulation Factor VIIa Variant Marzeptacog Alfa (Activated) in Adult Subjects With Hemophilia A and BPHASE2 COMPLETED 11Dec 1, 2017Apr 1, 2019Sep 22, 2021 -
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Study Design & Arms
Interventions
NameTypeDescription
Coagulation Factor VIIa variantBIOLOGICALSingle intravenous injection of MarzAA, followed by single subcutaneous injection of MarzAA, followed by daily subcutaneous injection of MarzAA for 50 days at final dose level required.
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