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Ozanezumab

Phase 2

Amyotrophic Lateral Sclerosis | Small molecule | Neurology |GSK plc|Last Updated: Dec 21, 2017

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials1
Total Enrollment304

FDA Designations

No designations recorded

Clinical trial landscape

Ozanezumab · 1 trial · 1 indication

Phase 2 1
NCT01753076Study of Ozanezumab (GSK1223249) Versus Placebo in the Treatment of Amyotrophic Lateral SclerosisAmyotrophic Lateral Sclerosis
COMPLETED304 Analytics
PHASE2COMPLETED
Study of Ozanezumab (GSK1223249) Versus Placebo in the Treatment of Amyotrophic Lateral Sclerosis
Amyotrophic Lateral SclerosisUnlock trial analytics

Study Endpoints

Primary Endpoints

Joint Rank Scores for Combined Analysis of Function (Amyotrophic Lateral Sclerosis Functional Rating Scale Revised [ALSFRS-R] Score) and 48 Week Overall Survival
Week 48

The joint rank score is a combined assessment of function and survival. Function is assessed using change from Baseline in the ALSFRS-R total score. To calculate joint rank scores, every participant was compared with all other participants in a pair wise manner and assigned a score of -1, 0 or 1 based on their relative outcomes. A subject's joint rank score is the sum of their scores across the pair wise comparisons. The . The ALSFRS-R was a quickly administered (5 min) ordinal rating scale used to determine a participant's assessment of their capability and independence in 12 functional activities. There were 12 questions, graded by the participant 0-4 (4 is normal). Score of 0 (worst) to 48 (best). Reflects speech and swallowing, fine motor skills, large motor skills, and breathing. Lower scores of ALSFRS-R reflect greater impairment.

Secondary Endpoints

Change From Baseline in the ALSFRS-R Total Score at Week 48
Baseline and Week 48
Rate of Decline Over Week 48 in the ALSFRS-R Total Score
Baseline to Week 48
Change From Baseline in Slow Vital Capacity (SVC) at Week 48
Baseline and Week 48
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Study Design & Arms

AllocationRANDOMIZED
MaskingTRIPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Ozanezumab IVEXPERIMENTALAdministered by IV route. Treatment period - 48 Weeks
PlaceboPLACEBO_COMPARATORNormal saline by IV route. Treatment period - 48 weeks

Interventions

NameTypeDescription
OzanezumabDRUGOzanezumab injection solution
PlaceboDRUGNormal saline (0.9% sodium chloride) infusion
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Eligibility Criteria

Age Range18 Years to 80 Years
SexALL
Healthy VolunteersNo
Study Sites35

Inclusion Criteria: * Patients with diagnosis of familial or sporadic ALS * Onset of muscle weakness no more than 30 months before screening visit. * Slow Vital Capacity (SVC) of at least 65% predicted for gender, age, ethnicity and height at Screening. * If on riluzole, the dose must have been sta...

Countries:United StatesAustraliaBelgiumCanadaFranceGermanyItalyJapanNetherlandsSouth KoreaUnited Kingdom
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Frequently asked questions about Ozanezumab

What is Ozanezumab used for?

Ozanezumab is an investigational small molecule being studied for the treatment of Amyotrophic Lateral Sclerosis (ALS), a progressive neurodegenerative disease. It is currently in Phase 2 clinical development and is not approved by regulatory authorities.

Who makes Ozanezumab?

Ozanezumab is being developed by GSK plc, a global pharmaceutical company traded on the London Stock Exchange under the ticker GSK. The company sponsored a Phase 2 clinical trial of the drug in patients with ALS.

What phase is Ozanezumab in?

Ozanezumab is in Phase 2 clinical development. One Phase 2 trial has been completed, and there are no active trials currently enrolling. The drug remains investigational and has not received regulatory approval for any indication.

What clinical trials is Ozanezumab in?

Ozanezumab has one completed clinical trial, identified as NCT01753076. This Phase 2 study compared Ozanezumab (also known as GSK1223249) against placebo in 304 patients with Amyotrophic Lateral Sclerosis across multiple countries, including the United States, Australia, and European nations.

Is Ozanezumab the same as GSK1223249?

Yes, Ozanezumab is also known as GSK1223249. The clinical trial NCT01753076, which evaluated the drug in Amyotrophic Lateral Sclerosis, used this alternative name to identify the investigational treatment in its official title.