Recent Updates
Recently added Catalysts

LGD-4665

Phase 2

Immune Thrombocytopenic Purpura | Small molecule | Other |GSK plc|Last Updated: Dec 16, 2024

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
Premium
Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
Premium
Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDBiomarker
Total Trials1
Total Enrollment23
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00621894Oral LGD-4665 Versus Placebo in Adults With Immune Thrombocytopenic Purpura (ITP) for 6 Weeks Plus Open Treatment ContinuationPHASE2 COMPLETED 23Mar 15, 2008May 15, 2009Dec 16, 202415 United States
Unlock Drug Trial Details
Study Endpoints
Primary Endpoints
Percentage of participants with platelet count >= 50000/µL
At Week 6

Response was defined as platelet count \>= 50 x1000/uL for participants without Baseline steroid uses; or platelet counts \>= 50 x1000/uL and doubling the Baseline platelet counts for participants with baseline steroid uses. Confidence interval of response rate was computed using exact method of binomial proportion.

Secondary Endpoints
Number of participants with time to response by Platelet Counts (platelet counts >= 50,000/µL)
Week 1, 2, 4 and 6 of part 1
Change From Baseline to Last Bleeding Observation During Double-Blind Treatment
Day 1 (Baseline) and Week 6
Duration of platelet counts >= 50,000/µL of LGD4665
Up to Week 6
Unlock Study Endpoints
Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
LGD4665EXPERIMENTALLGD-4665: Experimental Thrombopoietin mimetic
PlaceboPLACEBO_COMPARATORPlacebo
Interventions
NameTypeDescription
LGD-4665DRUGLGD-4665 Thrombopoietin mimetic
PlaceboDRUGPlacebo
Unlock Study Design Details
Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites15

Inclusion Criteria: * Adults 18 years or older * Diagnosis of ITP for at least 3 months consistent with ASH guidelines * Treated with one or more prior therapies for ITP and platelet counts \< 30,000/µL or \< 50,000/µL if on a stable oral corticosteroid for ≥ 4 weeks, supported by 2 platelet counts...

Countries:United States
Unlock Eligibility Criteria