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IDRX-42

Phase 3

Gastrointestinal Neoplasms | Small molecule | Oncology |GSK plc|Last Updated: May 27, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedCONTROLLEDDMCBiomarker
Total Trials2
Total Enrollment728
FDA Designations
No designations recorded
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT07218926A Study of IDRX-42 (GSK6042981) Versus (vs) Sunitinib in Participants With Gastrointestinal Stromal Tumors After Imatinib TherapyPHASE3 RECRUITING 450Dec 3, 2025Nov 29, 2030May 27, 2026121 United States, Australia +16
NCT05489237First-in-human Study of IDRX-42 in Participants With Metastatic and/or Unresectable Gastrointestinal Stromal TumorsPHASE1 RECRUITING 278Aug 3, 2022Jun 28, 2028May 4, 202631 United States, Belgium +9
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Study Endpoints
Primary Endpoints
Progression-Free Survival (PFS)
Up to approximately 130 weeks

PFS is defined as time from the date of randomization to the date of disease progression or death due to any cause, whichever occurs first.

Phase 1 (Dose Escalation) - Safety and Tolerability (Nature, incidence, and severity of any DLTs)
When participant completes 1 cycle (28 days) treatment with safety and tolerability assessment by investigators
Phase 1 (Dose Escalation) - Determination of the MTD and/or RP1bD(s) of orally administered IDRX-42
Approximately 18 months from first participant enrolled
Phase 1 (Dose Escalation) - C-QTc sub-study: QTcF - concentration response analysis
At the end of Cycle 1 Day 1 and at the end of Cycle 2 Day 1 (each cycle is 28 days)
Phase 1b-Number of participants with TEAEs and with laboratory test results
Approximately 18 months
Phase 1b - Objective Response Rate (ORR) mRESIST v1.1
Approximately 18 months
Phase 1b - C-QTcF sub-study: QTcF - concentration response analysis
At the end of Cycle 1 Day 1 and at the end of Cycle 2 Day 1 (each cycle is 28 days)
Secondary Endpoints
Overall Survival (OS)
Up to approximately 261 weeks
Progression-Free Survival (PFS)
Up to approximately 261 weeks
Confirmed Overall Objective Response Rate (ORR)
Up to approximately 261 weeks
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
IDRX-42 (GSK6042981)EXPERIMENTAL -
SunitinibACTIVE_COMPARATOR -
Dose Escalation (Phase I)EXPERIMENTALParticipants should have advanced (metastatic and/or surgically unresectable) GIST, following failure of at least prior imatinib therapy due to progression of GIST.
(Phase 1b) Cohort 1 - Participants with GIST progression after first-line imatinib therapyEXPERIMENTALParticipants with advanced GIST who have had GIST progression after first-line imatinib only (second line therapy setting) and refused or are ineligible for other standard of care (SOC) therapies.
(Phase 1b): Cohort 2 - Participants with GIST progression after 2 or more lines of TKI therapyEXPERIMENTALParticipants with metastatic and/or surgically unresectable GIST following progression EITHER after sequential imatinib then sunitinib (third-line therapy setting) OR after imatinib, sunitinib, and then an additional TKI agent (i.e., regorafenib or ripretinib) (fourth-line therapy setting) OR after imatinib, sunitinib, regorafenib, and ripretinib (5th line or greater therapy).
(Phase 1b): Cohort 3 - Participants with GIST who are treatment naïveEXPERIMENTALParticipants with metastatic and/or surgically unresectable GIST who are treatment naïve (first line therapy) and refused or are ineligible for other standard of care (SOC) therapies.
(Phase 1b): Cohort 4EXPERIMENTALParticipants with GIST progression who meet the same criteria as Cohort 2 (third line or greater TKI therapy) and have had prior treatment with investigational agents NB003 or THE-630 or a line of therapy of bezuclastinib plus sunitinib combination.
Interventions
NameTypeDescription
IDRX-42DRUGIDRX-42 will be administered.
SunitinibDRUGSunitinib will be administered.
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites121

Inclusion Criteria: * Participants with histologically or cytologically confirmed GIST that is metastatic and/or surgically unresectable. * Documented disease progression on or intolerance to imatinib administered for first-line treatment of unresectable/metastatic disease. * Tumor tissue must be a...

Countries:United StatesAustraliaBelgiumBrazilCanadaChinaFranceGermanyItalyJapanNetherlandsNorwayPolandRomaniaSouth KoreaSpainTaiwanUnited Kingdom
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Recent Changes (Last 90 Days)
LOWMay 28, 2026NCT07218926lastUpdatePostDate: changed
LOWMay 28, 2026NCT07218926lastUpdatePostDate: changed
LOWMay 26, 2026NCT05489237primaryCompletionDate: changed
LOWMay 26, 2026NCT07218926primaryCompletionDate: changed
LOWMay 24, 2026NCT05489237studyFirstPostDate: changed
LOWMay 24, 2026NCT07218926studyFirstPostDate: changed