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IDRX-42

Phase 3

Gastrointestinal Neoplasms | Small molecule | Oncology |GSK plc|Last Updated: Jun 12, 2026

Success Probability

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Market & Valuation

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Trial Design

RandomizedCONTROLLEDDMCBiomarker
Total Trials2
Total Enrollment728

FDA Designations

No designations recorded

Clinical trial landscape

IDRX-42 · 2 trials · 5 indications

Phase 3 1Phase 1 1
NCT07218926A Study of IDRX-42 (GSK6042981) Versus (vs) Sunitinib in Participants With Gastrointestinal Stromal Tumors After Imatinib TherapyGastrointestinal Neoplasms
RECRUITING450 Analytics
PHASE3RECRUITING
A Study of IDRX-42 (GSK6042981) Versus (vs) Sunitinib in Participants With Gastrointestinal Stromal Tumors After Imatinib Therapy
Gastrointestinal NeoplasmsUnlock trial analytics

Study Endpoints

Primary Endpoints

Progression-Free Survival (PFS)
Up to approximately 130 weeks

PFS is defined as time from the date of randomization to the date of disease progression or death due to any cause, whichever occurs first.

Phase 1 (Dose Escalation) - Safety and Tolerability (Nature, incidence, and severity of any DLTs)
When participant completes 1 cycle (28 days) treatment with safety and tolerability assessment by investigators
Phase 1 (Dose Escalation) - Determination of the MTD and/or RP1bD(s) of orally administered IDRX-42
Approximately 18 months from first participant enrolled
Phase 1 (Dose Escalation) - C-QTc sub-study: QTcF - concentration response analysis
At the end of Cycle 1 Day 1 and at the end of Cycle 2 Day 1 (each cycle is 28 days)
Phase 1b-Number of participants with TEAEs and with laboratory test results
Approximately 18 months
Phase 1b - Objective Response Rate (ORR) mRESIST v1.1
Approximately 18 months
Phase 1b - C-QTcF sub-study: QTcF - concentration response analysis
At the end of Cycle 1 Day 1 and at the end of Cycle 2 Day 1 (each cycle is 28 days)

Secondary Endpoints

Overall Survival (OS)
Up to approximately 261 weeks
Progression-Free Survival (PFS)
Up to approximately 261 weeks
Confirmed Overall Objective Response Rate (ORR)
Up to approximately 261 weeks
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Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
IDRX-42 (GSK6042981)EXPERIMENTAL -
SunitinibACTIVE_COMPARATOR -
Dose Escalation (Phase I)EXPERIMENTALParticipants should have advanced (metastatic and/or surgically unresectable) GIST, following failure of at least prior imatinib therapy due to progression of GIST.
(Phase 1b) Cohort 1 - Participants with GIST progression after first-line imatinib therapyEXPERIMENTALParticipants with advanced GIST who have had GIST progression after first-line imatinib only (second line therapy setting) and refused or are ineligible for other standard of care (SOC) therapies.
(Phase 1b): Cohort 2 - Participants with GIST progression after 2 or more lines of TKI therapyEXPERIMENTALParticipants with metastatic and/or surgically unresectable GIST following progression EITHER after sequential imatinib then sunitinib (third-line therapy setting) OR after imatinib, sunitinib, and then an additional TKI agent (i.e., regorafenib or ripretinib) (fourth-line therapy setting) OR after imatinib, sunitinib, regorafenib, and ripretinib (5th line or greater therapy).
(Phase 1b): Cohort 3 - Participants with GIST who are treatment naïveEXPERIMENTALParticipants with metastatic and/or surgically unresectable GIST who are treatment naïve (first line therapy) and refused or are ineligible for other standard of care (SOC) therapies.
(Phase 1b): Cohort 4EXPERIMENTALParticipants with GIST progression who meet the same criteria as Cohort 2 (third line or greater TKI therapy) and have had prior treatment with investigational agents NB003 or THE-630 or a line of therapy of bezuclastinib plus sunitinib combination.

Interventions

NameTypeDescription
IDRX-42DRUGIDRX-42 will be administered.
SunitinibDRUGSunitinib will be administered.
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites124

Inclusion Criteria: * Participants with histologically or cytologically confirmed GIST that is metastatic and/or surgically unresectable. * Documented disease progression on or intolerance to imatinib administered for first-line treatment of unresectable/metastatic disease. * Documented mutation st...

Countries:United StatesAustraliaBelgiumBrazilCanadaChinaFranceGermanyHungaryItalyJapanNetherlandsNorwayPolandRomaniaSouth KoreaSpainTaiwanUnited Kingdom
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Recent Changes (Last 90 Days)

LOWJun 12, 2026NCT07218926lastUpdatePostDate: changed
LOWJun 12, 2026NCT07218926lastUpdatePostDate: changed

Frequently asked questions about IDRX-42

What is IDRX-42 used for?

IDRX-42 is an investigational small molecule being developed for gastrointestinal neoplasms, specifically gastrointestinal stromal tumors (GIST). It is studied in patients with metastatic and/or unresectable GIST, and in a Phase 3 trial for GIST after imatinib therapy. It is not yet approved and remains in clinical development.

How does IDRX-42 work?

IDRX-42 is a small molecule designed to target specific molecular pathways involved in gastrointestinal stromal tumors. The exact molecular target is not disclosed in the available information, but it is being studied in biomarker-selected patients, suggesting it acts on a defined genetic alteration driving tumor growth.

Who is developing IDRX-42?

IDRX-42 is being developed by GSK plc, a global biopharmaceutical company listed on the stock exchange under the ticker GSK. GSK is conducting clinical trials to evaluate the safety and efficacy of IDRX-42 in patients with gastrointestinal stromal tumors.

What phase is IDRX-42 in?

IDRX-42 is currently in Phase 3 clinical development. A Phase 3 trial is recruiting participants to compare IDRX-42 (also known as GSK6042981) against sunitinib in patients with gastrointestinal stromal tumors after imatinib therapy. An earlier Phase 1 first-in-human study is also ongoing.

What clinical trials is IDRX-42 in?

IDRX-42 is being studied in two active clinical trials. NCT05489237 is a Phase 1 first-in-human study in participants with metastatic and/or unresectable gastrointestinal stromal tumors, enrolling 278 patients. NCT07218926 is a Phase 3 trial comparing IDRX-42 to sunitinib in GIST patients after imatinib, enrolling 450 patients.

Is IDRX-42 the same as GSK6042981?

Yes, IDRX-42 is also known as GSK6042981. The Phase 3 clinical trial NCT07218926 refers to the drug as IDRX-42 (GSK6042981), confirming that both names refer to the same investigational compound being developed by GSK.