Recent Updates
Recently added Catalysts

CYT387

Phase 1

Primary Myelofibrosis | Small molecule | Oncology |GSK plc|Last Updated: Feb 1, 2019

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment166

FDA Designations

No designations recorded

Clinical trial landscape

CYT387 · 1 trial · 3 indications

Phase 1 1
NCT00935987Safety and Efficacy Study of CYT387 in Primary Myelofibrosis (PMF) or Post-polycythemia Vera (PV) or Post-essential Thrombocythemia (ET)Primary Myelofibrosis
COMPLETED166 Analytics
PHASE1COMPLETED
Safety and Efficacy Study of CYT387 in Primary Myelofibrosis (PMF) or Post-polycythemia Vera (PV) or Post-essential Thrombocythemia (ET)
Primary MyelofibrosisUnlock trial analytics

Study Endpoints

Primary Endpoints

Safety and tolerability, dose-limiting toxicities (DLTs) and maximum tolerated dose (MTD) of orally-administered CYT387 in patients with PMF or post-ET/PV MF.
Ongoing throughout therapy up until 30 days after last dose of CYT387
Objective Response Rate (ORR), as measured by complete response (CR) rate, partial response (PR) rate and clinical improvement (CI) rate according to International Working Group for Myelofibrosis Research and Treatment (IWG-MRT) consensus criteria
Baseline to study completion

The Objective Response Rate (ORR), as measured by complete response (CR) rate, partial response (PR) rate and clinical improvement (CI) rate according to International Working Group for Myelofibrosis Research and Treatment (IWG-MRT) is to be measured at the end of every cycle of therapy.

Pharmacokinetics of CYT387 in patients with PMF or post-ET/PV MF
Baseline to end of Cycle 1

The pharmacokinetics (PK) of CYT387 in patients with PMF or post-ET/PV MF is to be assessed on Day 1 and Day 28 in Cycle 1 of therapy

Secondary Endpoints

Effect of CYT387 on bone marrow or peripheral blood cytogenetic findings in patients with PMF or post-ET/PV MF.
Baseline to study completion
Effect of CYT387 on peripheral blood granulocyte JAK2V617F allele burden in patients with PMF or post-ET/PV MF.
Baseline to study completion
Effect of CYT387 on peripheral blood endogenous myeloid colony formation in patients with PMF or post-ET/PV MF.
Baseline to study completion
Unlock Study Endpoints

Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
CYT387EXPERIMENTAL -

Interventions

NameTypeDescription
CYT387DRUGFor the Part 1 dose-escalation portion of the study, patients will be assigned to dose levels in successive cohorts starting with a dose in the first cohort of 100 mg/day. CYT387 will be orally self-administered as a single daily dose beginning on Day 1 of the study, and thereafter at approximately the same time each day of the 28-day cycle. It is recommended that all doses be preceded by a 2-hour fast from food and beverages, and be followed by a 1-hour post-dose fast from food and beverages. Twenty additional patients will be assigned to a 150 mg BID (twice daily) dosing schedule. CYT387 will be orally self-administered twice-daily with doses approximately 10-12 hours apart beginning on Day 1 of the study, and thereafter at approximately the same times each day of the 28-day cycle. For the Part 2 dose confirmation portion of the study, patients will be assigned to either 150 mg or 300 mg QD (once daily) dose groups.
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites6

Inclusion Criteria: * Diagnosis of PMF or post-polycythemia Vera (PV) or post-essential Thrombocythemia (ET) MF as per revised World Health Organization (WHO) criteria. * High-risk or Intermediate-2 risk MF (as defined by the International Prognostic Scoring System \[IPSS\]; Appendix 13.6); or inte...

Countries:United StatesAustraliaCanada
Unlock Eligibility Criteria

Frequently asked questions about CYT387

What is CYT387 used for in Primary Myelofibrosis?

CYT387 is an investigational small molecule being studied for the treatment of Primary Myelofibrosis, as well as Post-Polycythemia Vera Myelofibrosis and Post-Essential Thrombocythemia Myelofibrosis. It is a targeted therapy designed to address the underlying disease process in these myeloproliferative conditions.

Who makes CYT387?

CYT387 is being developed by GSK plc, a global biopharmaceutical company listed on the stock exchange under the ticker symbol GSK. The company is conducting clinical research to evaluate the safety and efficacy of this investigational drug in patients with myelofibrosis.

What phase is CYT387 in?

CYT387 is in Phase 1 clinical development. It is an investigational drug, meaning it has not been approved by regulatory authorities and is still undergoing clinical trials to assess its safety and effectiveness in patients with Primary Myelofibrosis and related conditions.

What clinical trials is CYT387 in?

CYT387 has been studied in one completed clinical trial, registered as NCT00935987. This Phase 1 study evaluated the safety and efficacy of CYT387 in patients with Primary Myelofibrosis, Post-Polycythemia Vera Myelofibrosis, or Post-Essential Thrombocythemia Myelofibrosis, enrolling 166 participants across the United States, Australia, and Canada.

Is CYT387 the same as momelotinib?

Yes, CYT387 is also known as momelotinib. This alternative name is used in scientific literature and clinical trial registries to refer to the same investigational drug being developed by GSK plc for the treatment of myelofibrosis.