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Plasma-derived AT-III

Phase 2

Antithrombin III Deficiency | Small molecule | Hematology |Grifols, S.A.|Last Updated: Aug 25, 2023

Target and mechanism

ModalitySmall molecule

Also known as Plasma-derived AT-III concentrate

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDDMC
Total Trials1
Total Enrollment30

FDA Designations

No designations recorded

Clinical trial landscape

Plasma-derived AT-III · 1 trial · 1 indication

Phase 2 1
NCT00319228Safety, Pharmacokinetics and Efficacy of an ATIII ConcentrateAntithrombin III Deficiency
ACTIVE NOT_RECRUITING30 Analytics
PHASE2ACTIVE NOT_RECRUITING
Safety, Pharmacokinetics and Efficacy of an ATIII Concentrate
Antithrombin III DeficiencyUnlock trial analytics

Study Endpoints

Primary Endpoints

The primary objectives of this clinical study are to:
2 years
Assess the pharmacokinetic (PK) profile of AT-III in congenital AT-III deficient patients
1 year
To measure the in vivo recovery and half-life of AT-III.
1 year
To assess the clinical safety and tolerability of AT-III-DAF/DI.
1 year

Secondary Endpoints

To assess clinical efficacy by preventing thromboembolic or thrombotic events (prophylaxis) in individuals with congenital AT-III deficiency who are undergoing surgical procedures or who are pregnant and undergoing parturition.
1 year
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposePREVENTION

Treatment Arms

ArmTypeDescription
Antithrombin IIIEXPERIMENTAL -

Interventions

NameTypeDescription
Plasma-derived AT-III concentrateDRUGSegment I: A single dose IV infusion of 50 IU/kg of ATIII-DAF/DI will be administered to each patient. Segment II: A single dose or multiple doses depending on the subject's ATIII plasma levels and patient's specific treatment plan.
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Eligibility Criteria

Age Range12 Years to N/A
SexALL
Healthy VolunteersNo

Inclusion Criteria: * Congenital ATIII deficiency documented by determination of plasma levels of ATIII off all therapies. Specifically, the baseline levels of ATIII activity should be equal to or less than 60%. * Age \>12 years with a body weight of no less than 30 kg. * Have not participated in a...

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Frequently asked questions about Plasma-derived AT-III

What is Plasma-derived AT-III used for?

Plasma-derived AT-III is an investigational therapy being studied for the treatment of Antithrombin III Deficiency, a hematologic condition. It is currently in Phase 2 clinical development and has not been approved by regulatory authorities.

Who makes Plasma-derived AT-III?

Plasma-derived AT-III is being developed by Grifols, S.A., a biopharmaceutical company traded on the NASDAQ under the ticker symbol GRFS. The company is conducting clinical trials to evaluate the safety and efficacy of this product.

What phase is Plasma-derived AT-III in?

Plasma-derived AT-III is currently in Phase 2 clinical development. It is an investigational product, meaning it has not yet received regulatory approval and is still being studied in clinical trials to assess its safety and effectiveness.

What clinical trials is Plasma-derived AT-III in?

Plasma-derived AT-III is being studied in a Phase 2 clinical trial registered as NCT00319228, titled 'Safety, Pharmacokinetics and Efficacy of an ATIII Concentrate.' This trial is active but not recruiting, with an estimated enrollment of 30 participants aged 12 years and older.

Is Plasma-derived AT-III the same as Plasma-derived AT-III concentrate?

Yes, Plasma-derived AT-III is also known as Plasma-derived AT-III concentrate. Both names refer to the same investigational product being developed by Grifols for Antithrombin III Deficiency.