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amilo-5MER

Phase 1

Inflammatory Disease | Small molecule | Other |Galmed Pharmaceuticals Ltd.|Last Updated: May 12, 2023

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindCONTROLLEDBiomarker
Total Trials1
Total Enrollment55
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT05857215A First-in-Human Study of Single and Multiple Doses of Amilo-5MER in Healthy SubjectsPHASE1 COMPLETED 55Mar 5, 2021Jul 1, 2021May 12, 20231 United Kingdom
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Study Endpoints
Primary Endpoints
Safety and tolerability of amilo-5ER
10 days

Assess and characterize the number of participants with clinically significant changes in safety assessments, including adverse events, physical examination findings, vital signs, clinical laboratory assessments, and urinalysis.

Secondary Endpoints
PK- Area under the concentration-time curve (AUC)
10 days
PK- Time of maximum observed concentration (Tmax)
10 days
PK- Maximum observed concentration (Cmax)
10 days
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Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelSEQUENTIAL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
A- amilo-5MER solution for subcutaneous administration or matching placebo- 10 mgEXPERIMENTALAmilo-5MER solution for subcutaneous administration or matching placebo at a dose of 10 mg
B- amilo-5MER solution for subcutaneous administration or matching placebo- 30 mgEXPERIMENTALAmilo-5MER solution for subcutaneous administration or matching placebo at a dose of 30 mg
C- amilo-5MER solution for subcutaneous administration or matching placebo- 90 mgEXPERIMENTALAmilo-5MER solution for subcutaneous administration or matching placebo at a dose of 90 mg
D- amilo-5MER solution for subcutaneous administration or matching placebo- 180 mgEXPERIMENTALAmilo-5MER solution for subcutaneous administration or matching placebo at a dose of 180 mg
E- amilo-5MER solution for subcutaneous administration or matching placebo- 360mgEXPERIMENTALAmilo-5MER solution for subcutaneous administration or matching placebo at a dose of 360 mg
Interventions
NameTypeDescription
amilo-5MERDRUGamilo-5MER is a 5 amino acid synthetic peptide MTADV (Methionine, Threonine, Alanine, Aspartic acid, Valine).
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Eligibility Criteria
Age Range18 Years — 80 Years
SexALL
Healthy VolunteersYes
Study Sites1

Inclusion Criteria: 1. Healthy males (all parts) or healthy females (Part 3 only). 2. Aged 18 to 45 years (Parts 1 and 2) or aged 65 to 80 years (Part 3) inclusive at the time of signing informed consent. 3. Body mass index (BMI) of 19.0 to 31.0 kg/m2, with a body weight \<95 kg, as measured at scr...

Countries:United Kingdom
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