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Pilocarpine, Dose 1

Phase 2

Dry Eye Disease | Small molecule | Ophthalmology |Glaukos Corporation|Last Updated: Sep 1, 2023

Target and mechanism

Molecular targetCHRM1, CHRM3
Target classAgonist
ModalitySmall molecule
ChEMBLCHEMBL550

Also known as Pilocarpine Ophthalmic Topical Cream, Dose 1

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment226

FDA Designations

No designations recorded

Clinical trial landscape

Pilocarpine, Dose 1 · 2 trials · 3 indications

Phase 2 2
NCT05119920Safety and Efficacy of Pilocarpine Ophthalmic Topical Cream for the Treatment of Dry Eye DiseaseDry Eye Disease
COMPLETED226 Analytics
NCT05124275Safety and Efficacy of Pilocarpine Ophthalmic Topical Cream for the Treatment of PresbyopiaPresbyopia
COMPLETED123 Analytics
PHASE2COMPLETED
Safety and Efficacy of Pilocarpine Ophthalmic Topical Cream for the Treatment of Dry Eye Disease
Dry Eye DiseaseUnlock trial analytics
PHASE2COMPLETED
Safety and Efficacy of Pilocarpine Ophthalmic Topical Cream for the Treatment of Presbyopia
PresbyopiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Mean change from baseline in the VAS score at Day 28 visit.
Baseline and Day 28

Mean change from baseline in the VAS score at Day 28 visit. Visual Analogue Scale from 0 (no discomfort) to 100 (maximal discomfort)

Mean change from baseline in Fluorescein Staining at the Day 28 visit.
Baseline and Day 28
Binocular Distance Corrected Near Visual Acuity (DCNVA)
Day 28

Proportion of treatment responders \[subjects gaining 3 lines or more in binocular distance corrected near visual acuity (DCNVA) and not losing more than 5 letters of binocular best corrected distance visual acuity (BCDVA)\] 1 hour post-dose at the Day 28 visit.

Secondary Endpoints

Mean change from baseline in the VAS score at the Day 4, 8, and 14 visits
Baseline and Days 4, 8, and 14
Proportion of treatment responders (as defined for the primary endpoint) at 0.5, 2, 4, and 6 hours post-dose at the day 28 visit.
Day 28
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Pilocarpine Ophthalmic Topical Cream, Dose 1EXPERIMENTALPilocarpine Ophthalmic Topical Cream, Dose 1
Pilocarpine Ophthalmic Topical Cream, Dose 2EXPERIMENTALPilocarpine Ophthalmic Topical Cream, Dose 2
Pilocarpine Ophthalmic Topical Cream, Dose 3EXPERIMENTALPilocarpine Ophthalmic Topical Cream, Dose 3
Placebo Ophthalmic Topical CreamPLACEBO_COMPARATORPlacebo Ophthalmic Topical Cream

Interventions

NameTypeDescription
Pilocarpine Ophthalmic Topical Cream, Dose 1DRUGPilocarpine Ophthalmic Topical Cream, Dose 1
Pilocarpine Ophthalmic Topical Cream, Dose 2DRUGPilocarpine Ophthalmic Topical Cream, Dose 2
Pilocarpine Ophthalmic Topical Cream, Dose 3DRUGPilocarpine Ophthalmic Topical Cream, Dose 3
Placebo Ophthalmic Topical CreamDRUGPlacebo Ophthalmic Topical Cream
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites19

Inclusion Criteria: * Male or female, 18 years of age or older at the Screening Visit * Willing and able to provide written informed consent on the IRB/IEC-approved informed consent form * Diagnosis of dry eye Exclusion Criteria: * Sensitivity or known allergy to pilocarpine or any of the other e...

Countries:United States
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Competitive Landscape -Dry Eye Disease 6 trials

Top 3 of 5 competitors

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Frequently asked questions about Pilocarpine, Dose 1

What is Pilocarpine, Dose 1?

Pilocarpine, Dose 1 is an investigational small molecule developed by Glaukos Corporation for ophthalmic use. It is being studied in Phase 2 clinical development for Dry Eye Disease and Presbyopia, and it is formulated as an ophthalmic topical cream rather than a conventional eye drop.

What is Pilocarpine, Dose 1 used for?

Pilocarpine, Dose 1 is being developed for two eye conditions: Dry Eye Disease and Presbyopia. Both are non-surgical ophthalmic indications, and the program has been studied in adults, including patients aged 40 years and older in the presbyopia trial.

What does Pilocarpine, Dose 1 target?

Pilocarpine, Dose 1 targets the muscarinic acetylcholine receptors CHRM1 and CHRM3, where it acts as an agonist. By activating these receptors, the drug is designed to produce a pharmacological effect in the eye relevant to its Dry Eye Disease and Presbyopia indications.

Who makes Pilocarpine, Dose 1?

Pilocarpine, Dose 1 is being developed by Glaukos Corporation, which trades on the New York Stock Exchange under the ticker GKOS. Glaukos is an ophthalmology-focused company, and this asset is part of its clinical-stage pipeline.

What phase is Pilocarpine, Dose 1 in?

Pilocarpine, Dose 1 is in Phase 2 clinical development. It is investigational and has not been approved by the FDA. The program has one completed Phase 2 trial, and no trials are currently listed as active.

What clinical trials is Pilocarpine, Dose 1 in?

Pilocarpine, Dose 1 has been evaluated in two completed Phase 2 trials. NCT05124275 studied the ophthalmic topical cream in Presbyopia with 123 participants, and NCT05119920 studied it in Dry Eye Disease and keratoconjunctivitis sicca with 226 participants. Both were randomized, double-blind, placebo-controlled trials conducted in the United States.

Is Pilocarpine, Dose 1 the same as Pilocarpine Ophthalmic Topical Cream, Dose 1?

Yes. Pilocarpine, Dose 1 is also known as Pilocarpine Ophthalmic Topical Cream, Dose 1. The two names refer to the same Glaukos Corporation investigational asset, which is a small molecule formulated as a topical cream for ophthalmic administration.