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Miltefosine

Phase 2

Primary Visceral Leishmaniasis | Small molecule | Other |Gilead Sciences, Inc.|Last Updated: Apr 24, 2017

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedCONTROLLEDDMC
Total Trials1
Total Enrollment151
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT01067443Clinical Trial to Assess the Safety and Efficacy of Sodium Stibogluconate (SSG) and AmBisome® Combination, Miltefosine and AmBisome® and Miltefosine Alone for the Treatment Visceral Leishmaniasis in Eastern AfricaPHASE2 COMPLETED 151Mar 1, 2010Jun 1, 2011Apr 24, 20173 Kenya, Sudan
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Study Endpoints
Primary Endpoints
Initial cure: proportion cured at Day 28
Day 28
Secondary Endpoints
Final cure: proportion cured at day 210
6 months post treatment
Adverse events and serious adverse events occurring in the three study arms
up to day 60
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Amb+SSGEXPERIMENTALAmBisome® one dose of 10mg/kg body weight (IV) on day 1 followed by 10 days of SSG at 20mg/kg body weight (IV/IM) from days 2-11
Amb+MiltEXPERIMENTALAmBisome® one dose of 10mg/kg body weight (IV) on day 1 followed by 10 days Miltefosine at 2.5mg/kg body weight (oral) from days 2-11
MiltEXPERIMENTALMonotherapy course of Miltefosine at 2.5mg/kg body weight (oral) from days 1-28
Interventions
NameTypeDescription
Liposomal amphotericin B (AmBisome®) and sodium stibogluconateDRUGAmBisome® one dose of 10mg/kg body weight (IV) on day 1 followed by 10 days of SSG at 20mg/kg body weight (IV/IM) from days 2-11
Liposomal amphotericin B + miltefosineDRUGAmBisome® one dose of 10mg/kg body weight (IV) on day 1 followed by 10 days Miltefosine at 2.5mg/kg body weight (oral) from days 2-11
MiltefosineDRUGMonotherapy course of Miltefosine at 2.5mg/kg body weight (oral) from days 1-28
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Eligibility Criteria
Age Range7 Years — 60 Years
SexALL
Healthy VolunteersNo
Study Sites3

Inclusion Criteria: * Patients with clinical signs and symptoms of VL and diagnosis confirmed by visualization of parasites in tissue samples (lymph node, bone marrow or spleen where relevant) on microscopy. * Patients aged between 7 (to allow for blood sampling) and 60 years (inclusive) who are ab...

Countries:KenyaSudan
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