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MBX-8025

Phase 2

Homozygous Familial Hypercholesterolemia | Small molecule | Metabolic |Gilead Sciences, Inc.|Last Updated: Jul 14, 2022

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDDMC
Total Trials1
Total Enrollment13

FDA Designations

No designations recorded

Clinical trial landscape

MBX-8025 · 3 trials · 3 indications

Phase 2 3
NCT02955602Seladelpar (MBX-8025) in Subjects With Primary Biliary Cholangitis (PBC)Primary Biliary Cirrhosis
COMPLETED119 Analytics
NCT02472535Study to Evaluate the Effects of MBX-8025 in Patients With HoFHHomozygous Familial Hypercholesterolemia
COMPLETED13 Analytics
NCT00701883Safety and Benefit of MBX-8025 With and Without Commonly Used Statins in Moderately Overweight Patients With High CholesterolHyperlipidemia
COMPLETED183 Analytics
PHASE2COMPLETED
Seladelpar (MBX-8025) in Subjects With Primary Biliary Cholangitis (PBC)
Primary Biliary CirrhosisUnlock trial analytics
PHASE2COMPLETED
Study to Evaluate the Effects of MBX-8025 in Patients With HoFH
Homozygous Familial HypercholesterolemiaUnlock trial analytics
PHASE2COMPLETED
Safety and Benefit of MBX-8025 With and Without Commonly Used Statins in Moderately Overweight Patients With High Cholesterol
HyperlipidemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Relative Change From Baseline in Serum Alkaline Phosphatase (ALP) at Week 8
8 weeks

Relative change from baseline in serum ALP levels at Week 8 (endpoint). The modified Intent-to-Treat (mITT) analysis set included all randomized subjects with confirmed PBC who received at least one study drug dose and had at least one post baseline ALP evaluation on treatment. n, denotes number of subjects evaluable for the respective timepoints

LDL-C
12-Weeks

Absolute and percentage (%) reduction in serum LDL-C at any point from baseline through Week 16.

Lipid levels will be measured in patients with hyperlipidemia to assess the benefits of the investigational drug
8 week treatment period

Secondary Endpoints

Absolute Change From Baseline in Serum Alkaline Phosphatase (ALP) at Week 12 and Week 52
12 weeks and 52 weeks
Change in Aspartate Aminotransferase (AST) From Baseline to 12 Weeks and 52 Weeks
12 weeks and 52 weeks
Change in Alanine Aminotransferase (ALT) From Baseline to 12 Weeks and 52 Weeks
12 weeks and 52 weeks
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Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
MBX-8025 (2 mg)EXPERIMENTALMBX-8025 2 mg capsule once daily
MBX-8025 (5 mg)EXPERIMENTALMBX-8025 5 mg capsule once daily
MBX-8025 (10 mg)EXPERIMENTALMBX-8025 10 mg capsule once daily
placebo, MBX-8025 50 mg, 100 mg or 200 mg capsulesEXPERIMENTAL -
Placebo/PlaceboPLACEBO_COMPARATOR -
MBX-8025 50 mg/PlaceboEXPERIMENTAL -
MBX-8025 100 mg/PlaceboEXPERIMENTAL -
Placebo/Atorvastatin 20 mgACTIVE_COMPARATOR -
MBX-8025 50 mg/Atorvastatin 20 mgEXPERIMENTAL -
MBX-8025 100 mg/Atorvastatin 20 mgEXPERIMENTAL -

Interventions

NameTypeDescription
MBX-8025 2 mg CapsuleDRUGInitial 8-week treatment: • MBX-8025 2 mg Extension: The 2 mg group will be started after safety and efficacy review of the 5 mg and the 10 mg groups has been completed. Subjects will initially enter the extension on their assigned dose. The dose might be up- or down-titrated after safety and efficacy data review of the first 8 weeks of treatment. During the extension, a subject's dose might be re-adjusted for safety or efficacy reasons.
MBX-8025 5 mg CapsuleDRUGInitial 8-week treatment: • MBX-8025 5 mg Extension: Subjects will initially enter the extension on their assigned dose. The dose might be up- or down-titrated after safety and efficacy data review of the first 8 weeks of treatment. During the extension, a subject's dose might be re-adjusted for safety or efficacy reasons.
MBX-8025 10 mg CapsuleDRUGInitial 8-week treatment: • MBX-8025 10 mg Extension: Subjects will initially enter the extension on their assigned dose. The dose might be up- or down-titrated after safety and efficacy data review of the first 8 weeks of treatment. During the extension, a subject's dose might be re-adjusted for safety or efficacy reasons.
Run-In Period: PlaceboOTHER2 capsules, once a day for two weeks
MBX-8025 50 mg (Dose Escalation Period 1)DRUG1 capsule once a day for 4 weeks (MBX-8025 50 mg capsule)
MBX-8025 50 mg or 100 mg (Dose Escalation Period 2)DRUG1 capsule once a day for 4 weeks (MBX-8025 50 mg or 100 mg capsule)
MBX-8025 50 mg, 100 mg or 200 mg (Dose Escalation Period 3)DRUG1 or 2 capsules once a day for 4 weeks (MBX-8025 50 mg, 100 mg or two (2) 100 mg capsules)
PlaceboDRUG2 capsules, once a day for 8 weeks
MBX-8025DRUG2 capsules, once daily for 8 weeks
AtorvastatinDRUG2 capsules, once daily for 8 weeks
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Eligibility Criteria

Age Range18 Years to 75 Years
SexALL
Healthy VolunteersNo
Study Sites38

Inclusion Criteria: 1. Must have given written informed consent (signed and dated) and any authorizations required by local law 2. 18 to 75 years old (inclusive) 3. Male or female with a diagnosis of PBC, by at least two of the following criteria: * History of AP above ULN for at least six mont...

Countries:United StatesCanadaGermanyUnited KingdomFranceNetherlandsNorway
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Frequently asked questions about MBX-8025

What is MBX-8025 used for?

MBX-8025 is an investigational small molecule being studied for Homozygous Familial Hypercholesterolemia, Primary Biliary Cirrhosis, and Hyperlipidemia. It is in Phase 2 clinical development and has not been approved by the FDA.

Who makes MBX-8025?

MBX-8025 is being developed by Gilead Sciences, Inc., which trades on the NASDAQ under the ticker GILD. The drug is currently in Phase 2 clinical trials for metabolic conditions.

What phase is MBX-8025 in?

MBX-8025 is in Phase 2 clinical development. It is investigational and has not received FDA approval. All three completed trials for the drug were Phase 2 studies.

What clinical trials is MBX-8025 in?

MBX-8025 has completed three Phase 2 trials: NCT00701883 in Hyperlipidemia with 183 patients, NCT02472535 in Homozygous Familial Hypercholesterolemia with 13 patients, and NCT02955602 in Primary Biliary Cirrhosis with 119 patients.

Is MBX-8025 the same as seladelpar?

Yes, MBX-8025 is also known as seladelpar. One of its completed trials, NCT02955602, is titled 'Seladelpar (MBX-8025) in Subjects With Primary Biliary Cholangitis (PBC)', confirming the alternative name.