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CHIKV VLP/unadjuvanted

Phase 2

Chikungunya Virus Infection | Monoclonal antibody | Other |Emergent BioSolutions Inc.|Last Updated: Jul 3, 2023

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindCONTROLLEDBiomarker
Total Trials1
Total Enrollment445
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT03483961Trial of a Chikungunya Vaccine, PXVX0317 CHIKV-VLP, in Healthy AdultsPHASE2 COMPLETED 445Apr 18, 2018Sep 21, 2020Jul 3, 20233 United States
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Study Endpoints
Primary Endpoints
Anti-CHIKV Neutralizing Antibody Geometric Mean Titer 28 Days After the Last Injection for Groups 2-8.
Day 57 (from Day 1 vaccination), 28 days after the last injection.

To assess the induction of anti-chikungunya virus (CHIKV) neutralizing antibody geometric mean titers by different formulations and schedules, as measured at 28 days after the last injection (Day 57) for Groups 2-8.

Secondary Endpoints
Kinetics of Anti-chikungunya Virus (CHIKV) Neutralizing Antibody Geometric Mean Titer for Groups 2-8.
At Days 8, 15, 22, 29, 36, and 57.
Differences in Persistence of Neutralizing Antibody Geometric Mean Titer for Groups 2-8.
At Days 182, 365, 547, and 760.
Boosting of Vaccine-induced Neutralizing Antibody Geometric Mean Titer by a Booster Dose of PXVX0317 for Group 4 Only.
Antibody levels will be measured at Day 547 prior to the booster dose and again 28 days later on Day 575 and then at Day 760.
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Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposePREVENTION
Treatment Arms
ArmTypeDescription
Group 1: 20 mcg/unadjuvanted (Day 1 & 29)EXPERIMENTAL20 mcg CHIKV VLP/unadjuvanted (Day 1) // Placebo (Day 15) // 20 mcg CHIKV VLP/unadjuvanted (Day 29)
Group 2: 6 mcg/adjuvanted (Day 1 & 29)EXPERIMENTAL6 mcg CHIKV VLP/adjuvanted (Day 1) // Placebo (Day 15) // 6 mcg CHIKV VLP/adjuvanted (Day 29)
Group 3: 10 mcg/adjuvanted (Day 1 & 29)EXPERIMENTAL10 mcg CHIKV VLP/adjuvanted (Day 1) // Placebo (Day 15) // 10 mcg CHIKV VLP/adjuvanted (Day 29)
Group 4: 20mcg/adjuvanted (Day 1 & 29);40mcg/adjuvant (Day 547)EXPERIMENTAL20 mcg CHIKV VLP/adjuvanted (Day 1) // Placebo (Day 15) // 20 mcg CHIKV VLP/adjuvanted (Day 29) // 40 mcg CHIKV (Day 547)
Group 5: 6 mcg/adjuvanted (Day 15 & 29)EXPERIMENTALPlacebo (Day 1) // 6 mcg CHIKV VLP/adjuvanted (Day 15) // 6 mcg CHIKV VLP/adjuvanted (Day 29)
Group 6: 10 mcg/adjuvanted (Day 15 & 29)EXPERIMENTALPlacebo (Day 1) // 10 mcg CHIKV VLP/adjuvanted (Day 15) // 10 mcg CHIKV VLP/adjuvanted (Day 29)
Group 7: 20 mcg/adjuvanted (Day 15 & 29)EXPERIMENTALPlacebo (Day 1) // 20 mcg CHIKV VLP/adjuvanted (Day 15) // 20 mcg CHIKV VLP/adjuvanted (Day 29)
Group 8: 40 mcg/adjuvanted (Day 29)EXPERIMENTALPlacebo (Day 1) // Placebo (Day 15) // 40 mcg CHIKV VLP/adjuvanted (Day 29)
Group 9: 20 mcg/adjuvanted (Day 1 & 29)EXPERIMENTAL20 mcg CHIKV VLP/adjuvanted (Day 1) // 20 mcg CHIKV VLP/adjuvanted (Day 29). This group will also have plasmapheresis performed on Day 57 and Leukapheresis on Day 182
Group 10: 40 mcg/adjuvanted (Day 1)EXPERIMENTAL40 mcg CHIKV VLP/adjuvanted (Day 1). This group will also have plasmapheresis performed on Day 22.
Interventions
NameTypeDescription
CHIKV VLP/unadjuvantedBIOLOGICALVaccine consists of virus-like particles of chikungunya virus antigens
CHIKV VLP/adjuvantedBIOLOGICALAdjuvanted formulation includes Alhydrogel
PlaceboBIOLOGICALPlacebo is vaccine diluent alone
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Eligibility Criteria
Age Range18 Years — 45 Years
SexALL
Healthy VolunteersYes
Study Sites3

Inclusion Criteria: 1. Male or female 2. Age 18 to 45 years old (inclusive) 3. Using an acceptable method of contraception (if female of childbearing potential). 4. Able and willing to provide informed consent for study participation. Exclusion Criteria: 1. Current acute febrile illness. 2. Clini...

Countries:United States
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