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PBCAR20A

Phase 1

Non-Hodgkin's Lymphoma, Relapsed | Gene therapy | Oncology |Precision BioSciences, Inc.|Last Updated: Jan 31, 2023

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
CONTROLLEDBiomarker
Total Trials1
Total Enrollment18
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT04030195Dose-escalation Study of Safety of PBCAR20A in Subjects With r/r NHL or r/r CLL/SLLPHASE1 COMPLETED 18Mar 24, 2020Jun 24, 2021Jan 31, 20235 United States
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Study Endpoints
Primary Endpoints
Maximum Tolerated Dose (MTD)
Day 1 to Day 28

The maximum tolerated dose (MTD) is the dose level at which fewer than 33% of patients experience a dose limiting toxicity (DLT) using a 3+3 strategy.

Number of Participants With Dose-Limiting Toxicities
1 year

Dose-limiting toxicities (DLT) are certain Grade 3 and Grade 4 toxic reactions as defined by the protocol and CTCAE v5.0.

Secondary Endpoints
Objective Response Rate
1 year
Progression-free Survival (PFS)
1 year
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Dose Level 1 of PBCAR20A CAR T cellsEXPERIMENTAL1 x 10\^6 chimeric antigen receptor (CAR) T cells per kg body weight. In this study, PBCAR20A, allogeneic anti-cluster of differentiation (CD20) CAR T Cells, is used to treat patients with relapsed or refractory (r/r) CD20+ Non-Hodgkin Lymphoma (NHL) or r/r Chronic Lymphocytic Leukemia (CLL) or Small Lymphocytic Lymphoma (SLL). Route of Administration: Intravenous infusion (IV) Lymphodepletion Conditioning: Lymphodepletion will be conducted several days prior to PBCAR20A infusion. A combination of fludarabine and cyclophosphamide will be used for lymphodepletion.
Dose Level 2 of PBCAR20A CAR T cellsEXPERIMENTAL240 x 10\^6 CAR T cells (flat dose)
Dose Level 3 of PBCAR20A CAR T cellsEXPERIMENTAL480 x 10\^6 CAR T cells (flat dose)
Interventions
NameTypeDescription
PBCAR20AGENETICSingle dose of Allogeneic Anti-CD20 CAR T cells will be infused, and a classic "3+3" dose escalation will be applied.
FludarabineDRUGFludarabine is used for lymphodepletion (30 mg/m\^2/day, Days -5 to -3).
CyclophosphamideDRUGCyclophosphamide is used for lymphodepletion (500 mg/m\^2/day, Days -5 to -3).
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites5

Key Inclusion Criteria Criteria for NHL: * r/r CD20+ B-cell NHL that is histologically confirmed by archived tumor biopsy tissue from the last relapse and corresponding pathology report. * Measurable or detectable disease according to the Lugano classification. * Primary refractory disease or r/r ...

Countries:United States
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