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Mesenchymal stem cells from adipose tissue

Phase 2

Critical Limb Ischemia | Unknown | Other |Design Therapeutics, Inc.|Last Updated: Jul 9, 2018

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedNO_TREATMENT_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment33
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT01745744Application of Cell Regeneration Therapy With Mesenchymal Stem Cells From Adipose Tissue in Critical Chronic Ischemic Syndrome of Lower Limbs (CLI) in Nondiabetic Patients.PHASE2 COMPLETED 33Feb 1, 2011Jul 1, 2018Jul 9, 20182 Spain
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Study Endpoints
Primary Endpoints
Number of adverse events and serious adverse events
12 months.

Number of adverse events and serious adverse events: 24h administration of CeTMAd, 1 month, 3 months, 6 months, 9 months and 12 months.

Secondary Endpoints
Evolution of chronic critical ischemia
1 month, 3 months, 6 months, 9 months and 12 months
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Low doseEXPERIMENTAL\- Infusion of mesenchymal stem cells from adipose tissue: 0.5x106 cells / kg of patient weight.
High doseEXPERIMENTAL\- Infusion of mesenchymal stem cells from adipose tissue: 1x106 cells / kg of patient weight.
ControlNO_INTERVENTIONConventional treatment
Interventions
NameTypeDescription
Mesenchymal stem cells from adipose tissueOTHER\- Infusion of mesenchymal stem cells from adipose tissue administered intraarterially: 0.5x106 cells / kg of patient weight and 1x106 cells / kg of patient weight.
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Eligibility Criteria
Age Range18 Years — 89 Years
SexALL
Healthy VolunteersNo
Study Sites2

Inclusion Criteria: * Patients of both sexes aged ≥ 18 and ≤ 89 years. * Nondiabetic. * Infrapopliteal atherosclerotic vascular disease of severe grade with either severe claudication or Rutherford-Becker grade II-III-IV, of at least one lower limb. It is defined critical ischemia of the lower limb...

Countries:Spain
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