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AEZS-130

Phase 3

Diagnosis of Adult Growth Hormone Deficiency (AGDH) | Small molecule | Endocrine |COSCIENS Biopharma Inc.|Last Updated: Jul 23, 2019

Success Probability

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Market & Valuation

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Trial Design

RandomizedACTIVE_CONTROLLEDBiomarker
Total Trials1
Total Enrollment101

FDA Designations

No designations recorded

Clinical trial landscape

AEZS-130 · 1 trial · 1 indication

Phase 3 1
NCT00448747Investigation of a New, Oral Growth Hormone Secretagogue, AEZS-130 as a Growth Hormone Stimulation Test.Diagnosis of Adult Growth Hormone Deficiency (AGDH)
COMPLETED101 Analytics
PHASE3COMPLETED
Investigation of a New, Oral Growth Hormone Secretagogue, AEZS-130 as a Growth Hormone Stimulation Test.
Diagnosis of Adult Growth Hormone Deficiency (AGDH)Unlock trial analytics

Study Endpoints

Primary Endpoints

Receiver Operating Characteristic (ROC) Analysis on Peak GH (Growth Hormon) Concentrations
GH sampling: pre-dose and 30, 45, 60, 75, 90, 120, 150 min post-dose

The primary endpoint for each individual is the peak GH concentration following AEZS-130 (macimorelin) administration.

Secondary Endpoints

Peak Insulin-Like Growth Factor (IGF)-1 Concentration Following Treatment
15 min. before macimorelin administration and at 150 min after macimorelin administration
Classification and Regression Tree (CART) Analysis of Peak Growth Hormone (GH) Following Macimorelin Administration
GH sampling: pre-dose and 30, 45, 60, 75, 90, 120, 150 min post-dose
Number of Participants With Drug Related Adverse Events (AEs)
14 days
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Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelCROSSOVER
PurposeDIAGNOSTIC

Treatment Arms

ArmTypeDescription
AEZS-130 ( formerly ARD-07)EXPERIMENTALA single oral administration of AEZS-130 (0.5 mg/kg po) as Growth Hormone Stimulation Test
L-ARG+GHRHACTIVE_COMPARATORThis trial was set up as a multi-center, randomized, cross-over study investigating AEZS-130 as a Growth Hormone Stimulation Tests in terms of safety and efficacy compared to L-ARG+GHRH. When GHRH became unavailable on the US market, this comparator arm was no longer available, which was addressed by Amendment No. 3 (version 27-March-2010). Control subject enrolled under Amendment No. 3 were not randomized as there was no cross-over due to unavailability of L-ARG+GHRH. These control subjects received only AEZS-130

Interventions

NameTypeDescription
AEZS-130 (formerly ARD-07)DRUGA single oral administration of AEZS-130 as Growth Hormone Stimulation Test
L-ARG+GHRHDRUGA single administration of L-ARG+GHRH (iv bolus) followed by a 30min infusion of L-ARG as Growth Hormone Stimulation Test
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersYes
Study Sites13

Inclusion for Matched Control Subjects: * Undergone normal growth and development * Normal serum prolactin (PRL) concentrations * Females should have a history of regular, age-appropriate menses * Males should have normal serum testosterone concentrations * Matched GHD subject already enrolled in s...

Countries:United States
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Frequently asked questions about AEZS-130

What is AEZS-130 used for?

AEZS-130 is used for the diagnosis of Adult Growth Hormone Deficiency (AGDH). It is an oral small molecule being developed as a growth hormone stimulation test to help diagnose this condition in adults.

What does AEZS-130 target?

AEZS-130 is a growth hormone secretagogue, which means it stimulates the release of growth hormone. It is used as a diagnostic agent to test for Adult Growth Hormone Deficiency (AGDH) by provoking a growth hormone response.

Who makes AEZS-130?

AEZS-130 is being developed by COSCIENS Biopharma Inc., a company traded under the ticker CSCI. The drug is an investigational small molecule intended for use in diagnosing Adult Growth Hormone Deficiency.

What phase is AEZS-130 in?

AEZS-130 is in Phase 3 clinical development. It is an investigational drug and has not been approved by regulatory authorities. It is being studied for its use in diagnosing Adult Growth Hormone Deficiency (AGDH).

What clinical trials is AEZS-130 in?

AEZS-130 has one completed Phase 3 clinical trial, identified as NCT00448747. This trial investigated the drug as an oral growth hormone secretagogue for use as a growth hormone stimulation test in diagnosing Adult Growth Hormone Deficiency. The trial enrolled 101 participants in the United States.

Is AEZS-130 the same as macimorelin?

AEZS-130 is also known as macimorelin. It is an orally administered growth hormone secretagogue being developed for the diagnosis of Adult Growth Hormone Deficiency (AGDH). The drug is currently in Phase 3 clinical development.