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Mifepristone

Phase 3

Cushing's Disease | Small molecule | Endocrine |Corcept Therapeutics Incorporated|Last Updated: Dec 6, 2024

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Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment4

FDA Designations

No designations recorded

Clinical trial landscape

Mifepristone · 13 trials · 9 indications

Phase 3 8Phase 2 2Phase 1 3
NCT01371565Compassionate Use of CORLUX® (Mifepristone) in the Treatment of Signs and Symptoms of Endogenous Cushing's SyndromeCushing's Disease
COMPLETED4 Analytics
NCT00936741An Extension Study of CORLUX in the Treatment of Endogenous Cushing's SyndromeCushing's Syndrome
COMPLETED30 Analytics
NCT00569582A Study of the Efficacy and Safety of CORLUX in the Treatment of Endogenous Cushing's SyndromeCushing's Syndrome
COMPLETED50 Analytics
NCT00128505An International Extension Study of Corlux for Recurrent Psychotic Symptoms in Psychotic Major DepressionMajor Depressive Disorder
COMPLETED104 Analytics
NCT00146523An International Study of the Safety and Tolerability of Corlux for Psychotic Symptoms in Psychotic Major DepressionMajor Depressive Disorder
COMPLETED247 Analytics
NCT00208156A United States Extension Study of Corlux for Recurrent Psychotic Symptoms in Psychotic Major DepressionDepressive Disorder, Major
COMPLETED87 Analytics
NCT00128479A United States Study of the Safety and Tolerability of Corlux for Psychotic Symptoms in Psychotic Major DepressionMajor Depressive Disorder
COMPLETED443 Analytics
NCT00130676A United States Study of Corlux for Psychotic Symptoms in Psychotic Major DepressionMajor Depressive Disorder
COMPLETED257 Analytics
PHASE3COMPLETED
Compassionate Use of CORLUX® (Mifepristone) in the Treatment of Signs and Symptoms of Endogenous Cushing's Syndrome
Cushing's DiseaseUnlock trial analytics
PHASE3COMPLETED
An Extension Study of CORLUX in the Treatment of Endogenous Cushing's Syndrome
Cushing's SyndromeUnlock trial analytics
PHASE3COMPLETED
A Study of the Efficacy and Safety of CORLUX in the Treatment of Endogenous Cushing's Syndrome
Cushing's SyndromeUnlock trial analytics
PHASE3COMPLETED
An International Extension Study of Corlux for Recurrent Psychotic Symptoms in Psychotic Major Depression
Major Depressive DisorderUnlock trial analytics
PHASE3COMPLETED
An International Study of the Safety and Tolerability of Corlux for Psychotic Symptoms in Psychotic Major Depression
Major Depressive DisorderUnlock trial analytics
PHASE3COMPLETED
A United States Extension Study of Corlux for Recurrent Psychotic Symptoms in Psychotic Major Depression
Depressive Disorder, MajorUnlock trial analytics
PHASE3COMPLETED
A United States Study of the Safety and Tolerability of Corlux for Psychotic Symptoms in Psychotic Major Depression
Major Depressive DisorderUnlock trial analytics
PHASE3COMPLETED
A United States Study of Corlux for Psychotic Symptoms in Psychotic Major Depression
Major Depressive DisorderUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of Participants With Adverse Events
6 months

Safety was assessed at all visits and adverse events were recorded.

Improvement in Diabetes and/or Glucose Intolerance.
Baseline to Week 24

Responder is defined as subject with a decrease greater than or equal to 25% in area under the curve for glucose on 2-hour oral glucose test from baseline to week 24 or last visit, for Cushing's patients with type-2 diabetes mellitus/impaired glucose tolerance.

Decrease in Diastolic Blood Pressure.
Baseline to Week 24

Responder is defined as subject with a decrease greater than or equal to 5mm Hg in diastolic blood pressure from baseline to week 24 or last visit.

To evaluate the safety and tolerability of Corlux (mifepristone) for the treatment of recurrent psychotic symptoms with major depression with psychotic features (PMD) who previously participated in Corcept Therapeutics Protocol C-1073-09
The change in a measure of psychosis
screening and on Days 0, 7, 14, 28, 42, and 56
To evaluate the safety and tolerability of Corlux (mifepristone) for the treatment of recurrent psychotic symptoms with major depression with psychotic features (PMD) who previously participated in Corcept Therapeutics Protocol C-1073-07
Depressive symptom severity at post-treatment
6 weeks after the start of the intervention

Depressive symptom severity in patients with CT-related depression, measured with the Inventory of Depressive Symptomatology - Self Report (IDS-SR, with a total score ranging from 0 to 84, where higher scores indicate higher severity of depressive symptoms)

To determine the efficacy of mifepristone in the prevention of olanzapine-induced weight gain in healthy male volunteers.
Cmax of mifepristone of period 1 vs Cmax of mifepristone of period 3
18 days

Maximum (peak) plasma drug concentration (Cmax)

AUC0-tz of mifepristone of period 1 vs AUC0-tz of mifepristone of period 3
18 days

Area under the concentration-time curve from zero up to the last concentration above the lower limit of quantification of the assay (AUC0-tz)

AUCinf of mifepristone of period 1 vs AUCinf of mifepristone of period 3
18 days

Area under the plasma concentration-time curve from time zero to infinity (AUCinf)

Cmax of mifepristone at Day 42 compared to Day 28
Day 42 compared to Day 28

Maximum (peak) plasma drug concentration (Cmax)

AUC0-24 of mifepristone at Day 42 compared to Day 28
Day 42 compared to Day 28

Area under the plasma concentration-time curve from zero to 24 hours (AUC0-24)

Change From Baseline in Body Weight
Baseline and 28 days

Secondary Endpoints

The Long-term Benefit of Mifepristone Treatment in Cushing's Syndrome as Measured by Changes in the Score on the Physician's Global Assessment of Disease Severity
Up to three years.
To assess the frequency of retreatment with Corlux in patients with PMD and qualitatively describe the psychotic symptoms for which retreatment is clinically indicated
The change in a measure of depression
screening and on Days 0, 7, 14, 28, 42, and 56
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
mifepristoneEXPERIMENTAL -
1EXPERIMENTAL -
mifepristone 600 mgEXPERIMENTAL -
matching placeboPLACEBO_COMPARATOR -
mifepristone 300 mgEXPERIMENTAL -
placeboPLACEBO_COMPARATOR -
mifepristone 1200 mgEXPERIMENTAL -
Cohort 1EXPERIMENTALMifepristone 300 MG, 1 tablet
Cohort 2EXPERIMENTALMifepristone 1500 MG, 5 tablets
Arm 1EXPERIMENTALMifepristone 300 MG alone or Mifepristone 300 MG with Itraconazole 100 MG will be administered.
Risperidone plus mifepristoneEXPERIMENTALrisperidone plus mifepristone daily for 28 days
Risperidone plus mifepristone-matched placeboPLACEBO_COMPARATORrisperidone plus mifepristone-matched placebo daily for 28 days
Risperidone-matched placebo plus mifepristonePLACEBO_COMPARATORrisperidone-matched placebo plus mifepristone daily for 28 days

Interventions

NameTypeDescription
MifepristoneDRUGmifepristone at doses from 300mg/day up to 1200mg/day
placeboDRUG -
mifepristone matched placeboDRUGdaily for 7 days
mifepristone 600 mgDRUGmifepristone 600 mg daily for 7 days
mifepristone 1200 mgDRUGmifepristone 1200 mg daily for 7 days
matching placeboDRUGdaily for 7 days
Mifepristone 300 MGDRUGmifepristone 300 MG (4 tablets) orally for a total of 1200 mg a day for 14 days; then mifepristone 300 mg (3 tablets) orally for a total of 900 mg a day for 28 days
Itraconazole 100 MGDRUGitraconazole 100 MG (2 capsules) orally for a total of 200 MG for the last 14 days of mifepristone dosing
RisperidoneDRUGrisperidone daily for 28 days
Risperidone-matched placeboDRUGrisperidone-matched placebo daily for 28 days
Mifepristone-matched placeboDRUGmifepristone-matched placebo daily for 28 days
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites5

Inclusion Criteria: 1. Have a confirmed diagnosis of endogenous hypercortisolemia caused by ACTH dependent or ACTH independent etiologies including: * Cushing's Disease that (more than one may apply) * has recurred after primary pituitary surgery * has persisted despite pituitary sur...

Countries:United StatesBulgariaCroatiaRomaniaSerbiaSerbia and MontenegroNetherlandsIndia
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Frequently asked questions about Mifepristone

What is Mifepristone used for?

Mifepristone is being developed by Corcept Therapeutics for Cushing's Syndrome, Cushing's Disease, and Major Depressive Disorder. It is a small molecule in Phase 3 clinical development for these endocrine and psychiatric conditions. The drug is investigational and has not been approved for these indications.

Who makes Mifepristone?

Corcept Therapeutics Incorporated (NASDAQ: CORT) is developing Mifepristone. The company is conducting clinical trials for the drug in indications including Cushing's Syndrome, Cushing's Disease, and Major Depressive Disorder. Corcept Therapeutics is the developer of this investigational small molecule.

What phase is Mifepristone in?

Mifepristone is in Phase 3 clinical development for Cushing's Syndrome, Cushing's Disease, and Major Depressive Disorder. The drug is investigational and has not been approved by regulatory authorities for these indications. Corcept Therapeutics is conducting the clinical development program.

What clinical trials has Mifepristone been in?

Mifepristone has completed five clinical trials. These include NCT00455442, a Phase 2 study in weight-gain prevention; NCT00698022, a Phase 1 study in healthy volunteers; NCT03258372 and NCT03259542, Phase 1 drug-drug interaction studies; and one additional completed trial. All trials are completed with no active studies ongoing.

How does Mifepristone work?

Mifepristone is a small molecule that acts as a glucocorticoid receptor antagonist. By blocking the glucocorticoid receptor, it is being studied for its effects in Cushing's Syndrome, Cushing's Disease, and Major Depressive Disorder. This mechanism is relevant to conditions involving cortisol dysregulation.

Is Mifepristone the same as Korlym?

Mifepristone is the active ingredient in Korlym, a medication approved for Cushing's syndrome. However, the data provided does not specify whether the Mifepristone in development by Corcept Therapeutics is the same product as Korlym. The drug is being studied in Phase 3 trials for related indications.