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CGT4859

Phase 1

Intrahepatic Cholangiocarcinoma (Icc) | Small molecule | Oncology |Cogent Biosciences, Inc.|Last Updated: Apr 17, 2026

Target and mechanism

Molecular targetFGFR2
Target classFgfr
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDDMC
Total Trials1
Total Enrollment110

FDA Designations

No designations recorded

Clinical trial landscape

CGT4859 · 1 trial · 12 indications

Phase 1 1
NCT06777316A Study of an FGFR2/3 Inhibitor (CGT4859) in Patients With Cholangiocarcinoma and Other Advanced Solid TumorsIntrahepatic Cholangiocarcinoma (Icc)
ACTIVE NOT_RECRUITING110 Analytics
PHASE1ACTIVE NOT_RECRUITING
A Study of an FGFR2/3 Inhibitor (CGT4859) in Patients With Cholangiocarcinoma and Other Advanced Solid Tumors
Intrahepatic Cholangiocarcinoma (Icc)Unlock trial analytics

Study Endpoints

Primary Endpoints

Phase 1: Determine the maximum tolerated dose (MTD) and RP2D of CGT4859 - AEs
Approximately 12 months

Incidence, severity, and seriousness or treatment-emergent adverse events (AEs) leading to dose modification

Phase 1: Determine the maximum tolerated dose (MTD) and RP2D of CGT4859 - Laboratory results
Approximately 12 months

Clinically significant changes or abnormalities observed from baseline in laboratory results in chemistry, hematology, and coagulation parameters

Phase 1: Determine the maximum tolerated dose (MTD) and RP2D of CGT4859 - ECG results
Approximately 12 months

Clinically significant changes or abnormalities observed from baseline in electrocardiogram (ECG) parameters

Phase 2: Evaluate antitumor activity of CGT4859 - Objective Response Rate (ORR)
Approximately 8 months

Secondary Endpoints

Phase 1: Pharmacokinetics
Approximately 28 days
Phase 1: Evaluate antitumor activity of CGT4859 - Objective Response Rate (ORR)
Approximately 8 months
Phase 1 and Phase 2: Evaluate antitumor activity of CGT4859 - Disease Control Rate (DCR)
Approximately 8 months
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Phase 1: Dose EscalationEXPERIMENTALMultiple doses of CGT4859 for oral administration
Phase 2: Signal SeekingEXPERIMENTALOral dose of CGT4859 at the RP2D as determined in Phase 1

Interventions

NameTypeDescription
CGT4859DRUGCGT4859 is a selective FGFR2/3 inhibitor
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites13

Key Inclusion Criteria: 1. Histologically confirmed locally advanced, metastatic, and/or unresectable iCCA or other solid tumor with documented FGFR2/3 alteration in blood and/or tumor. 2. Previously treated with, not appropriate for, or declined standard-of-care first-line treatment. 3. Have measu...

Countries:United StatesCanada
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Frequently asked questions about CGT4859

What is CGT4859 used for?

CGT4859 is an investigational small molecule being developed for intrahepatic cholangiocarcinoma (ICC) and other advanced solid tumors. It is designed for patients with FGFR2 or FGFR3 genetic alterations, including gene fusions, rearrangements, amplifications, and short variants. The drug is currently in Phase 1 clinical development.

What does CGT4859 target?

CGT4859 targets FGFR2 and FGFR3, which are fibroblast growth factor receptors. It is an FGFR2/3 inhibitor being studied in patients with cholangiocarcinoma and other advanced solid tumors that harbor FGFR2 or FGFR3 genetic alterations, such as gene fusions, rearrangements, amplifications, and short variants.

Who makes CGT4859?

CGT4859 is being developed by Cogent Biosciences, Inc., a biopharmaceutical company traded on the stock exchange under the ticker COGT. The company is conducting a Phase 1 clinical trial of CGT4859 in patients with intrahepatic cholangiocarcinoma and other advanced solid tumors.

What phase is CGT4859 in?

CGT4859 is in Phase 1 clinical development. It is an investigational drug and has not been approved by the FDA. The ongoing Phase 1 study is actively enrolling participants in the United States and Canada to evaluate the drug in patients with cholangiocarcinoma and other advanced solid tumors.

What clinical trials is CGT4859 in?

CGT4859 is being studied in a Phase 1 clinical trial with the identifier NCT06777316. The trial is titled 'A Study of an FGFR2/3 Inhibitor (CGT4859) in Patients With Cholangiocarcinoma and Other Advanced Solid Tumors' and is currently active but not recruiting. The study has a planned enrollment of 110 participants.