Recent Updates
Recently added Catalysts

CTX-471

Phase 2

Neuroendocrine Neoplasm | Small molecule | Oncology |Compass Therapeutics, Inc.|Last Updated: Jul 6, 2026

Target and mechanism

Molecular targetCD137
Target classProtein
ModalitySmall molecule

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

RandomizedCONTROLLED
Total Trials1
Total Enrollment58

FDA Designations

No designations recorded

Clinical trial landscape

CTX-471 · 2 trials · 10 indications

Phase 2 1Phase 1 1
NCT07684170Study of CTX-471 in Patients With Neural Cell Adhesion Molecule (NCAM) Positive Neuroendocrine NeoplasmsNeuroendocrine Neoplasm
NOT YET_RECRUITING58 Analytics
PHASE2NOT YET_RECRUITING
Study of CTX-471 in Patients With Neural Cell Adhesion Molecule (NCAM) Positive Neuroendocrine Neoplasms
Neuroendocrine NeoplasmUnlock trial analytics

Study Endpoints

Primary Endpoints

Evaluate the clinical activity of CTX-471
Baseline until confirmed disease progression (up to 1 year)

Objective Response Rate (ORR) (Percentage of Participants With Objective Response) as per Response Evaluation Criteria in Solid Tumors (RECIST) Version 1.1

Evaluate the safety of CTX-471
From first dose of CTX-471 (Cycle 1 Day 1, Cycle = 2 weeks) until 30 days after the last dose of CTX-471

Incidence of treatment emergent adverse events (TEAEs), treatment-related AEs (TREAEs), and serious adverse events (SAEs)

Determine the recommended phase 2 dose (RP2D) for CTX-471
From first dose of CTX-471 (Cycle 1 Day 1, Cycle = 2 weeks) until 30 days after the last dose of CTX-471

Efficacy, exposure, safety events, and markers of response will be aggregated to select a Phase 2 dose

Number of participants with dose limiting toxicities (DLTs), treatment-emergent adverse events (TEAEs), and/or changes in clinical laboratory abnormalities
From first dose of CTX-471 (Week 1 Day 1) until 60 days after the last CTX-471 injection (up to 2 years)

Secondary Endpoints

Duration of Response (DOR) as per Response Evaluation Criteria in Solid Tumors (RECIST) Version 1.1
From the date of first confirmed PR or CR until date of progression or death, whichever occurs first (up to 1 year)
Disease Control Rate (DCR) as per Response Evaluation Criteria in Solid Tumors (RECIST) Version 1.1
From first dose of CTX-471 (Cycle 1 Day 1,Cycle = 2 weeks) until until disease progression or death, whichever occurs first (up to 1 year)
Progression-Free Survival (PFS) as per Response Evaluation Criteria in Solid Tumors (RECIST) Version 1.1
From first dose of CTX-471(Cycle 1 Day 1,Cycle = 2 weeks ) until disease progression or death, whichever occurs first (up to 1 year)
Unlock Study Endpoints

Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Dose Level 0.3 mg/kgEXPERIMENTAL -
Dose Level 0.6 mg/kgEXPERIMENTAL -
Arm 1 Part 1 Dose EscalationEXPERIMENTALEscalating doses of CTX-471 depending on cohort at enrollment
Arm 1 Part 2 Dose ExpansionEXPERIMENTALTwo dose groups of CTX-471 (0.3 mg/kg and 0.6 mg/kg)
Arm 2 Part 1 Dose EscalationEXPERIMENTALEscalating doses of CTX-471 in combination with pembrolizumab (KEYTRUDA® ) depending on cohort at enrollment
Arm 2 Part 2 Dose ExpansionEXPERIMENTALTwo cohorts of CTX-471 (0.3 mg/kg and 0.6 mg/kg) in combination with pembrolizumab (KEYTRUDA® ) (400 mg) in three tumor type subgroups. Cohort 1 - Group 1A - NSCLC , Group 1B -SCLC and Group 1C - Melanoma. Cohort 2 Group 2A - NSCLC, Group 2B - SCLC and Group 2C -Melanoma.

Interventions

NameTypeDescription
CTX-471DRUGPatients will receive CTX-471 as an intravenous (IV) infusion every 2 weeks until disease progression or unacceptable toxicity.
Pembrolizumab (KEYTRUDA®)DRUGIV infusion every 6 weeks
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo

Inclusion Criteria: 1. Age 18 years or older. 2. Positive immunohistochemical staining for NCAM (defined as ≥ 1% of malignant cells with membranous/cytoplasmic staining of any intensity) on an archived (≤ 3 months) or freshly taken biopsy specimen (centrally tested) with histologically confirmed di...

Countries:United States
Unlock Eligibility Criteria

Recent Changes (Last 90 Days)

LOWJul 6, 2026NCT07684170NEW_TRIAL: changed
LOWJul 6, 2026NCT07684170NEW_TRIAL: changed

Frequently asked questions about CTX-471

What is CTX-471 used for?

CTX-471 is an investigational small molecule being developed for oncology indications, including locally advanced solid tumors and neuroendocrine neoplasms. It is being studied in patients with metastatic or locally advanced malignancies, including non-small cell lung cancer, small cell lung cancer, mesothelioma, melanoma, and head and neck cancer, as well as in NCAM-positive neuroendocrine neoplasms.

What does CTX-471 target?

CTX-471 targets CD137, a protein involved in immune cell activation. By targeting CD137, CTX-471 is designed to modulate the immune response against tumors. It is being evaluated as a monotherapy and in combination with pembrolizumab in patients who have previously received PD-1/PD-L1 inhibitors.

Who makes CTX-471?

CTX-471 is being developed by Compass Therapeutics, Inc., a biopharmaceutical company traded on the Nasdaq under the ticker symbol CMPX. The company is conducting clinical trials to evaluate the safety and efficacy of CTX-471 in various oncology indications.

What phase is CTX-471 in?

CTX-471 is in Phase 1 and Phase 2 clinical development. A Phase 1 study has been completed, and a Phase 2 study is planned but has not yet started recruiting. The drug is investigational and has not been approved by regulatory authorities.

What clinical trials is CTX-471 in?

CTX-471 has been studied in clinical trial NCT03881488, a Phase 1 trial evaluating it as a monotherapy or in combination with pembrolizumab in patients with metastatic or locally advanced malignancies. A Phase 2 trial, NCT07684170, is planned to study CTX-471 in patients with NCAM-positive neuroendocrine neoplasms.

Is CTX-471 the same as any other drug?

CTX-471 is the sole name provided for this investigational drug. It is being studied under this name in clinical trials, and no alternative names have been reported. The drug is a small molecule targeting CD137 and is being developed by Compass Therapeutics.