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UCART22

Phase 1

B-cell Acute Lymphoblastic Leukemia | Monoclonal antibody | Oncology |Cellectis S.A.|Last Updated: Sep 9, 2025

Target and mechanism

Molecular targetCD22
Target classAntigen
ModalityMonoclonal antibody

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment52

FDA Designations

ORPHAN_DRUG

Clinical trial landscape

UCART22 · 1 trial · 1 indication

Phase 1 1
NCT04150497Phase 1/2 Study of UCART22 in Patients With Relapsed or Refractory CD22+ B-cell Acute Lymphoblastic Leukemia (BALLI-01)B-cell Acute Lymphoblastic Leukemia
RECRUITING52 Analytics
PHASE1RECRUITING
Phase 1/2 Study of UCART22 in Patients With Relapsed or Refractory CD22+ B-cell Acute Lymphoblastic Leukemia (BALLI-01)
B-cell Acute Lymphoblastic LeukemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Incidence of AE/SAE/DLT [Safety and Tolerability]
24 Months

Incidence, nature, and severity of adverse events and serious adverse events (SAEs) throughout the study in relation to UCART22 and/or lymphodepletion

Dose escalation part: Occurrence of Dose Limiting Toxicities (DLTs)
Up to D28 post initial UCART22 infusion

Secondary Endpoints

Investigator assessed overall response rate according to the Response criteria for Acute Lymphoblastic Leukemia (ALL)
At Day 28, Day 56, Day 84, Month 3, Month 6, Month 9, Month 12, Month 15, Month 18, Month 21 and Month 24
Duration of Response
From the date of the initial response to the date of disease progression or death from any cause, whichever occurs first, assessed up to Month 24
Progression Free Survival
From the first day of study treatment to the date of disease progression or death from any cause, whichever occurs first, assessed up to Month 24
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Dose EscalationEXPERIMENTALSeveral tested doses of UCART22 until the Maximum Tolerated Dose (MTD) is identified and establish Recommended Phase 2 Dose (RP2D) Dose Expansion: UCART22 administered at the RP2D

Interventions

NameTypeDescription
UCART22BIOLOGICALAllogeneic engineered T-cells expressing anti-CD22 Chimeric Antigen Receptor given following a lymphodepleting regimen
CLLS52BIOLOGICALA monoclonal antibody that recognizes a CD52 antigen
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Eligibility Criteria

Age Range15 Years to 50 Years
SexALL
Healthy VolunteersNo
Study Sites19

Inclusion Criteria: * B-ALL blast cells expressing CD22 * Diagnosed with R/R B-ALL * Prior therapy must include at least one standard chemotherapy regimen and at least one salvage regimen Exclusion Criteria: -Prior cellular therapy or investigational cellular or gene therapy within 90 days prior ...

Countries:United StatesFrance
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Frequently asked questions about UCART22

What is UCART22 used for?

UCART22 is an investigational cell therapy being studied for the treatment of B-cell Acute Lymphoblastic Leukemia (B-ALL). It is currently in Phase 1 clinical development and has not been approved by the FDA. The drug is being evaluated in patients with relapsed or refractory CD22+ B-cell Acute Lymphoblastic Leukemia.

What does UCART22 target?

UCART22 targets CD22, an antigen expressed on B cells. By binding to CD22, the therapy is designed to recognize and eliminate cancerous B cells in patients with B-cell Acute Lymphoblastic Leukemia. This targeted approach is being studied in a Phase 1 clinical trial.

Who makes UCART22?

UCART22 is being developed by Cellectis S.A., a biopharmaceutical company listed on the stock exchange under the ticker CLLS. The company is conducting clinical trials to evaluate the safety and efficacy of UCART22 in patients with B-cell Acute Lymphoblastic Leukemia.

What phase is UCART22 in?

UCART22 is currently in Phase 1 clinical development. It is an investigational drug, meaning it has not yet been approved by regulatory authorities. The ongoing Phase 1 trial is recruiting patients to assess the treatment's safety and preliminary efficacy in B-cell Acute Lymphoblastic Leukemia.

What clinical trials is UCART22 in?

UCART22 is being studied in a Phase 1/2 clinical trial with the identifier NCT04150497, known as the BALLI-01 study. This trial is recruiting patients with relapsed or refractory CD22+ B-cell Acute Lymphoblastic Leukemia and is being conducted in the United States and France.

Is UCART22 FDA approved?

UCART22 is not FDA approved. It is an investigational drug currently in Phase 1 clinical trials. The FDA has granted UCART22 orphan drug designation for the treatment of B-cell Acute Lymphoblastic Leukemia, which provides certain development incentives, but approval has not been granted.