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S-303 Treated Red Blood Cells

Phase 3

Thalassemia Major | Monoclonal antibody | Hematology |Cerus Corporation|Last Updated: Jul 18, 2018

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindACTIVE_CONTROLLED
Total Trials1
Total Enrollment86

FDA Designations

No designations recorded

Clinical trial landscape

S-303 Treated Red Blood Cells · 1 trial · 1 indication

Phase 3 1
NCT01740531Study to Evaluate Efficacy and Safety of S303 Treated Red Blood Cells (RBCs)in Subjects With Thalassemia Major Requiring Chronic RBC TransfusionThalassemia Major
COMPLETED86 Analytics
PHASE3COMPLETED
Study to Evaluate Efficacy and Safety of S303 Treated Red Blood Cells (RBCs)in Subjects With Thalassemia Major Requiring Chronic RBC Transfusion
Thalassemia MajorUnlock trial analytics

Study Endpoints

Primary Endpoints

Primary Efficacy Endpoint - Hemoglobin consumption
12 months

Hemoglobin consumption measured as total hemoglobin mass transfused per subject adjusted for average body weight and the number of days during the efficacy evaluation period (adjusted hemoglobin (Hgb) consumption units are g Hgb/kg body weight/day).

Primary Safety Endpoint-Incidence of a treatment-emergent antibody with confirmed specificity to S 303 treated red blood cells (RBC)
12 months

Incidence of a treatment-emergent antibody with confirmed specificity to S 303 treated red blood cells (RBC) associated with clinically significant hemolysis

Secondary Endpoints

Secondary Efficacy Endpoint-Hemoglobin increment
12 months
Secondary Efficacy Endpoint-Proportional decline in post transfusion hemoglobin level per day (%/day)
12 months
Secondary Safety Endpoint-Adverse Events
12 months
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Study Design & Arms

AllocationRANDOMIZED
MaskingDOUBLE
ModelCROSSOVER
PurposeOTHER

Treatment Arms

ArmTypeDescription
S-303 Treated Red Blood Cells (RBC)EXPERIMENTALPatients will be randomly assigned to the sequence of administration of Test and Control RBCs; eligible patients are randomly assigned to receive Test RBCs followed by Control RBCs or Control RBCs followed by Test RBCs. Each patient will complete both treatment periods.
Conventional, untreated Red Blood CellsACTIVE_COMPARATORPatients will be randomly assigned to the sequence of administration of Test and Control RBCs; eligible patients are randomly assigned to receive Test RBCs followed by Control RBCs or Control RBCs followed by Test RBCs. Each patient will complete both treatment periods.

Interventions

NameTypeDescription
S-303 Treated Red Blood Cells (RBCs)BIOLOGICAL -
Conventional, untreated Red Blood CellsBIOLOGICAL -
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Eligibility Criteria

Age Range10 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites3

Inclusion Criteria: * Age ≥10 years, of either gender * Diagnosed with thalassemia major and currently participating in a chronic transfusion program * At least a one year history of chronic RBC transfusion support with a stable transfusion requirement (per treating physician) * Intervals of at lea...

Countries:ItalyTurkey (Türkiye)
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Frequently asked questions about S-303 Treated Red Blood Cells

What is S-303 Treated Red Blood Cells used for?

S-303 Treated Red Blood Cells is an investigational therapy being studied for use in thalassemia major, a condition requiring chronic red blood cell transfusions. It is a pathogen-reduced red blood cell product designed for transfusion support in this patient population. The therapy is currently in Phase 3 clinical development.

Who makes S-303 Treated Red Blood Cells?

S-303 Treated Red Blood Cells is being developed by Cerus Corporation, a biopharmaceutical company traded on NASDAQ under the ticker symbol CERS. The company is conducting clinical trials to evaluate the safety and efficacy of this red blood cell product for patients with thalassemia major.

What phase is S-303 Treated Red Blood Cells in?

S-303 Treated Red Blood Cells is in Phase 3 clinical development. A Phase 3 study has been completed to evaluate its efficacy and safety in subjects with thalassemia major requiring chronic RBC transfusion. The therapy remains investigational and has not been approved by regulatory authorities.

What clinical trials is S-303 Treated Red Blood Cells in?

S-303 Treated Red Blood Cells has one completed Phase 3 clinical trial, registered as NCT01740531. This randomized, double-blind, active-controlled study enrolled 86 participants with thalassemia major across Italy and Turkey. The trial evaluated the efficacy and safety of S-303 treated red blood cells in patients requiring chronic transfusion.

Is S-303 Treated Red Blood Cells the same as pathogen-reduced red blood cells?

S-303 Treated Red Blood Cells refers to red blood cells treated with the S-303 pathogen inactivation system, which is designed to reduce infectious agents in donated blood. This product is being studied specifically for transfusion support in thalassemia major patients. It is distinct from standard red blood cell products.