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MYK-461

Phase 2

Cardiomyopathy, Hypertrophic Obstructive | Small molecule | Cardiovascular |Bristol-Myers Squibb Company|Last Updated: Jun 8, 2021

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment21

FDA Designations

No designations recorded

Clinical trial landscape

MYK-461 · 4 trials · 4 indications

Phase 2 1Phase 1 3
NCT02842242A Phase 2 Open-label Pilot Study Evaluating MYK-461 in Subjects With Symptomatic Hypertrophic Cardiomyopathy and Left Ventricular Outflow Tract ObstructionCardiomyopathy, Hypertrophic Obstructive
COMPLETED21 Analytics
PHASE2COMPLETED
A Phase 2 Open-label Pilot Study Evaluating MYK-461 in Subjects With Symptomatic Hypertrophic Cardiomyopathy and Left Ventricular Outflow Tract Obstruction
Cardiomyopathy, Hypertrophic ObstructiveUnlock trial analytics

Study Endpoints

Primary Endpoints

Change in Post-exercise Peak LVOT Gradient From Baseline to Week 12
Baseline and Week 12

Post-exercise peak LVOT gradients are assessed after a treadmill stress test by echocardiography.

Safety as measured by the incidence of adverse events
63 days

Incidence of adverse events

Safety: Incidence of adverse events
28 Days

Secondary Endpoints

Number of Participants Achieving a Post-exercise Peak LVOT Gradient Response of < 30 mmHg. Gradient < 30 mmHg
Baseline and Week 12
Change in Dyspnea Symptom Score From Baseline to Week 12
Baseline and Week 12
Change in Peak VO2 From Baseline to Week 12
Baseline and Week 12
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Open LabelEXPERIMENTALMYK-461
MYK-461EXPERIMENTALOral Tablet x 28 days
PlaceboPLACEBO_COMPARATOROral Tablet x 28 days

Interventions

NameTypeDescription
MYK-461DRUG -
PlaceboDRUGPlacebo comparator
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Eligibility Criteria

Age Range18 Years to 70 Years
SexALL
Healthy VolunteersNo
Study Sites7

Key Inclusion Criteria: * Diagnosed with HCM (hypertrophied and non-dilated left ventricle in absence of systemic or other known cause), with LV wall thickness ≥ 15 mm at time of initial diagnosis or ≥ 13 mm with a positive family history of HCM. * Age 18-70 * BMI 18-37kg/m2 * Documented LVEF ≥ 55%...

Countries:United StatesAustraliaUnited Kingdom
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Frequently asked questions about MYK-461

What is MYK-461 used for?

MYK-461 is an investigational small molecule being studied for the treatment of hypertrophic cardiomyopathy, including hypertrophic obstructive cardiomyopathy with left ventricular outflow tract obstruction. It has also been evaluated in healthy volunteers in early-phase clinical trials. The drug is in Phase 2 development and is not yet approved by regulatory authorities.

What does MYK-461 target?

MYK-461 is a small molecule designed to modulate cardiac muscle contraction. While its specific molecular target is not publicly detailed in the available clinical trial information, it is being investigated for its effects on hypertrophic cardiomyopathy, a condition characterized by excessive thickening of the heart muscle.

Who makes MYK-461?

MYK-461 is being developed by Bristol-Myers Squibb Company, which trades under the ticker symbol BMY on the New York Stock Exchange. The company is conducting clinical trials to evaluate the drug's safety, tolerability, and efficacy in patients with hypertrophic cardiomyopathy and in healthy volunteers.

What phase is MYK-461 in?

MYK-461 is currently in Phase 2 clinical development. It has completed Phase 1 trials in healthy volunteers and patients with hypertrophic cardiomyopathy, and a Phase 2 open-label pilot study in patients with symptomatic hypertrophic obstructive cardiomyopathy has also been completed. The drug remains investigational and has not received FDA approval.

What clinical trials is MYK-461 in?

MYK-461 has been studied in four completed clinical trials. These include NCT02329184, a Phase 1 study in patients with hypertrophic cardiomyopathy; NCT02356289 and NCT02480296, Phase 1 single and multiple ascending dose studies in healthy volunteers; and NCT02842242, a Phase 2 open-label pilot study in patients with symptomatic hypertrophic obstructive cardiomyopathy and left ventricular outflow tract obstruction.

Is MYK-461 the same as mavacamten?

MYK-461 is an investigational drug that has been studied under this identifier in clinical trials. It is not stated in the available information whether MYK-461 is the same as mavacamten or any other named compound. The drug is being developed by Bristol-Myers Squibb for hypertrophic cardiomyopathy.