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Tetrahydrobiopterin/kg

Phase 1

Claudication, Intermittent | Small molecule | Cardiovascular |BioMarin Pharmaceutical Inc.|Last Updated: Apr 15, 2026

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDBiomarker
Total Trials1
Total Enrollment10

FDA Designations

No designations recorded

Clinical trial landscape

Tetrahydrobiopterin/kg · 1 trial · 3 indications

Phase 1 1
NCT04800692The Effects of ATLAS Therapy on Nitric Oxide Bioavailability in Patients With Intermittent ClaudicationClaudication, Intermittent
ACTIVE NOT_RECRUITING10 Analytics
PHASE1ACTIVE NOT_RECRUITING
The Effects of ATLAS Therapy on Nitric Oxide Bioavailability in Patients With Intermittent Claudication
Claudication, IntermittentUnlock trial analytics

Study Endpoints

Primary Endpoints

Nitric Oxide bioavailability
90 days

Nitric Oxide bioavailability as measured by flow mediated dilatation (FMD).

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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeOTHER

Treatment Arms

ArmTypeDescription
Tetrahydrobiopterin Dose 1 (Day 0 to 44)EXPERIMENTALAll subjects will receive 3300mg l-Ascorbate , l-Arginine 3400mg and 10mg/kg of Tetrahydrobiopterin once a day.
Tetrahydrobiopterin Dose 2 (Day 45 to 90)EXPERIMENTALAll subjects will receive 3300mg l-Ascorbate, l-Arginine 3400mg and 20mg/kg of Tetrahydrobiopterin once a day.

Interventions

NameTypeDescription
Tetrahydrobiopterin 10 mg/kgDRUG10mg/kg of Tetrahydrobiopterin daily.
Tetrahydrobiopterin 20 mg/kgDRUG20mg/kg of Tetrahydrobiopterin daily.
L-AscorbateDRUG3300 mg of l-ascorbate once daily
L-ArginineDRUG3400mg of l-arginine once daily
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: * PAD as demonstrated by an ABI \<0 .9 in one leg or TBI less than \<0.7 in patients with an ABI \>1.3 (non compressible vessels) * Rutherford Classification II, III * Age \>18 years old * Willingness to discontinue phosphodiesterase (PDE) 5 inhibitors such as Viagra, Cialis, Le...

Countries:United States
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Frequently asked questions about Tetrahydrobiopterin/kg

What is Tetrahydrobiopterin/kg used for?

Tetrahydrobiopterin/kg is an investigational small molecule being studied for the treatment of intermittent claudication, a condition characterized by leg pain due to inadequate blood flow. It is being evaluated in patients with peripheral artery disease and peripheral vascular diseases. The drug is currently in Phase 1 clinical development.

How does Tetrahydrobiopterin/kg work?

Tetrahydrobiopterin/kg is being studied for its effects on nitric oxide bioavailability in patients with intermittent claudication. The ongoing clinical trial aims to assess how the drug influences nitric oxide levels, which are important for blood vessel function and blood flow. The exact mechanism of action is being investigated in this Phase 1 study.

Who makes Tetrahydrobiopterin/kg?

Tetrahydrobiopterin/kg is being developed by BioMarin Pharmaceutical Inc., a biopharmaceutical company. The company is conducting a Phase 1 clinical trial to evaluate the drug's effects in patients with intermittent claudication. BioMarin is listed on the stock market under the ticker symbol BMRN.

What phase is Tetrahydrobiopterin/kg in?

Tetrahydrobiopterin/kg is in Phase 1 clinical development. It is an investigational drug and has not been approved by regulatory authorities. The ongoing Phase 1 trial is active but not recruiting participants, with a planned enrollment of 10 patients.

What clinical trials is Tetrahydrobiopterin/kg in?

Tetrahydrobiopterin/kg is being studied in a Phase 1 clinical trial with the identifier NCT04800692. The trial is titled 'The Effects of ATLAS Therapy on Nitric Oxide Bioavailability in Patients With Intermittent Claudication' and is being conducted in the United States. The study is active but not recruiting, with an enrollment of 10 participants.

Is Tetrahydrobiopterin/kg the same as Tetrahydrobiopterin 10 mg/kg?

Yes, Tetrahydrobiopterin/kg is also known as Tetrahydrobiopterin 10 mg/kg. Both names refer to the same investigational drug being developed by BioMarin Pharmaceutical Inc. for the treatment of intermittent claudication. The drug is currently in Phase 1 clinical trials.