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Ara-C

Phase 2

Acute Myeloid Leukemia | Small molecule | Oncology |BioLineRx Ltd.|Last Updated: Sep 19, 2024

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDDMC
Total Trials1
Total Enrollment42

FDA Designations

No designations recorded

Clinical trial landscape

Ara-C · 1 trial · 1 indication

Phase 2 1
NCT01838395Phase IIa Study Evaluating Safety and Efficacy of BL-8040 in Relapsed/Refractory AML PatientsAcute Myeloid Leukemia
COMPLETED42 Analytics
PHASE2COMPLETED
Phase IIa Study Evaluating Safety and Efficacy of BL-8040 in Relapsed/Refractory AML Patients
Acute Myeloid LeukemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Safety and Tolerability
Participants were followed for the duration of the hospital stay and the follow-up period, an expected average of 6 weeks.

Number of participants with Adverse event affecting the safety and tolerability of BL-8040 + Ara-C by dose level (overall, dose limiting events, related Adverse Events (AEs), Serious Adverse Events (SAEs), related SAEs, AE by severity and death) Toxicity grade was assessed according to version V4.03 of NCI-CTCAE

Secondary Endpoints

Response to Treatment by Dose
Final bone marrow evaluation - Between Day 20 and Day 44
Apoptotic Effect
Final evaluation - between Day 20 and Day 44
Assessment of the Pharmacokinetic Profile of BL-8040 - t1/2 (h)
Blood samples for the determination of BL-8040 were collected before dosing and at 0.25, 0.5, 1, 2, 4, 8, and 24 hours after BL-8040 administration on Day 1.
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
BL-8040 0.5mg/kg + Ara-C 1.5 or 3 g/m2/d per dose (based on age)EXPERIMENTALArm 1: Participants will be dosed with SC injections of BL-8040 over two days followed by concurrent administration of 0.5 mg/kg BL-8040 with cytarabine (Ara-C) 1.5 or 3 g/m2/d per dose (based on age) during 5 days.
BL-8040 0.75mg/kg + Ara-C 1.5 or 3 g/m2/d (based on age)EXPERIMENTALArm 2: Participants will be dosed with SC injections of BL-8040 over two days followed by concurrent administration of 0.75 mg/kg BL-8040 with cytarabine (Ara-C) 1.5 or 3 g/m2/d per dose (based on age) during 5 days.
BL-8040 1.0mg/kg + Ara-C 1.5 or 3 g/m2/d (based on age)EXPERIMENTALArm 3: Participants will be dosed with SC injections of BL-8040 over two days followed by concurrent administration of 1 mg/kg BL-8040 with cytarabine (Ara-C) 1.5 or 3 g/m2/d per dose (based on age) during 5 days.
BL-8040 1.25mg/kg + Ara-C 1.5 or 3 g/m2/d (based on age)EXPERIMENTALArm 4: Participants will be dosed with SC injections of BL-8040 over two days followed by concurrent administration of 1.25 mg/kg BL-8040 with cytarabine (Ara-C) 1.5 or 3 g/m2/d per dose (based on age) during 5 days.
BL-8040 1.5mg/kg + Ara-C 1.5 or 3 g/m2/d (based on age)EXPERIMENTALArm 5: Participants will be dosed with SC injections of BL-8040 over two days followed by concurrent administration of 1.5 mg/kg BL-8040 with cytarabine (Ara-C) 1.5 or 3 g/m2/d per dose (based on age) during 5 days.
BL-8040 2mg/kg + Ara-C 1.5 or 3 g/m2/d (based on age)EXPERIMENTALArm 6: Participants will be dosed with SC injections of BL-8040 over two days followed by concurrent administration of 2 mg/kg BL-8040 with cytarabine (Ara-C) 1.5 or 3 g/m2/d per dose (based on age) during 5 days.

Interventions

NameTypeDescription
Ara-CDRUGIV (intravenous administration)
BL-8040DRUGSC (subcutaneous injection)
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Eligibility Criteria

Age Range18 Years to 75 Years
SexALL
Healthy VolunteersNo
Study Sites10

Inclusion Criteria: 1. Adult men and women subjects aged 18 to 75, inclusive. 2. Confirmed diagnosis of relapsed/refractory AML (WHO criteria) Refractory subjects, up to second consecutive salvage . Relapsed subjects including first and second relapse. 3. AML relapse \> 6 months since autologous or...

Countries:United StatesIsrael
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Frequently asked questions about Ara-C

What is Ara-C used for in Acute Myeloid Leukemia?

Ara-C is a small molecule being studied for the treatment of Acute Myeloid Leukemia (AML). It is currently in Phase 2 clinical development as an investigational therapy. The drug is being evaluated in patients with relapsed or refractory AML, meaning the disease has not responded to or has returned after prior treatment.

Who makes Ara-C?

Ara-C is being developed by BioLineRx Ltd., a biopharmaceutical company. BioLineRx is publicly traded on the NASDAQ under the ticker symbol BLRX. The company is conducting clinical trials to evaluate the safety and efficacy of Ara-C in patients with Acute Myeloid Leukemia.

What phase is Ara-C in?

Ara-C is currently in Phase 2 clinical development. It has completed a Phase 2a study in patients with relapsed or refractory Acute Myeloid Leukemia. The drug is investigational and has not been approved by regulatory authorities for commercial use.

What clinical trials is Ara-C in?

Ara-C has been evaluated in one completed clinical trial, NCT01838395. This was a Phase 2a study titled "Phase IIa Study Evaluating Safety and Efficacy of BL-8040 in Relapsed/Refractory AML Patients." The trial enrolled 42 participants with Acute Myeloid Leukemia and was conducted in the United States and Israel.

Is Ara-C the same as BL-8040?

Yes, Ara-C is also known as BL-8040. The clinical trial NCT01838395, which evaluated the drug in relapsed or refractory Acute Myeloid Leukemia patients, refers to the investigational agent as BL-8040. Both names refer to the same drug candidate being developed by BioLineRx.