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tonapofylline

Phase 3

Renal Insufficiency | Small molecule | Cardiovascular |Biogen Inc.|Last Updated: Sep 11, 2023

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials1
Total Enrollment420
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00709865Study to Assess the Safety and Tolerability of IV Tonapofylline in Subjects With Acute Decompensated Heart Failure (ADHF) and Renal InsufficiencyPHASE3 COMPLETED 420Jul 31, 2008Dec 31, 2009Sep 11, 2023189 United States, Argentina +16
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Study Endpoints
Primary Endpoints
Assess the safety andtolerability of intravenous tonapofylline, when added to standard therapy in subjects hospitalized with ADHF and renal insufficiency.
0-60 days
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Study Design & Arms
AllocationRANDOMIZED
MaskingTRIPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
1EXPERIMENTAL.03 mg/kg
2EXPERIMENTAL.15 mg/kg
3EXPERIMENTAL.3 mg/kg
4PLACEBO_COMPARATORPlacebo
Interventions
NameTypeDescription
tonapofyllineDRUGIV
PlaceboDRUGIV
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites189

Inclusion Criteria: * Previous diagnosis of heart failure. * Must have ADHF, requiring hospitalization, with clinical evidence for volume overload Exclusion Criteria: * History of an allergic reaction to any xanthine-containing substance. * History of seizure * History of stroke * Myocardial infa...

Countries:United StatesArgentinaAustraliaBrazilBulgariaCanadaCzechiaFinlandFranceGermanyIndiaIsraelItalyNetherlandsPolandRomaniaRussiaSweden
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