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BIIB033

Phase 2

Acute Optic Neuritis | Monoclonal antibody | Neurology |Biogen Inc.|Last Updated: Sep 23, 2019

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials2
Total Enrollment134

FDA Designations

No designations recorded

Clinical trial landscape

BIIB033 · 7 trials · 5 indications

Phase 2 3Phase 1 4
NCT02657915Long-Term Assessment of Remyelinating TherapyAcute Optic Neuritis
COMPLETED52 Analytics
NCT01864148Study to Assess the Efficacy, Safety, Tolerability, and Pharmacokinetics of BIIB033 in Participants With Relapsing Forms of Multiple Sclerosis When Used Concurrently With AvonexMultiple Sclerosis
COMPLETED419 Analytics
NCT01721161BIIB033 In Acute Optic Neuritis (AON)Acute Optic Neuritis
COMPLETED82 Analytics
PHASE2COMPLETED
Long-Term Assessment of Remyelinating Therapy
Acute Optic NeuritisUnlock trial analytics
PHASE2COMPLETED
Study to Assess the Efficacy, Safety, Tolerability, and Pharmacokinetics of BIIB033 in Participants With Relapsing Forms of Multiple Sclerosis When Used Concurrently With Avonex
Multiple SclerosisUnlock trial analytics
PHASE2COMPLETED
BIIB033 In Acute Optic Neuritis (AON)
Acute Optic NeuritisUnlock trial analytics

Study Endpoints

Primary Endpoints

FF-VEP Latency of the Affected Eye as Compared to the Baseline of the Fellow Eye at 2 Years (+ up to 12 Months) After the Last Study Visit Assessment (Week 32) in RENEW Study (NCT01721161)
Baseline (RENEW Study [NCT01721161]), Day 1 (NCT02657915)

A full field visual evoked potential (FF-VEP) is an evoked potential caused by a visual stimulus, such as an alternating checkerboard pattern on a computer screen. Responses are recorded from electrodes that are placed on the back of the head and are observed as a reading on an electroencephalogram (EEG). These responses usually originate from the occipital cortex, the area of the brain involved in receiving and interpreting visual signals.

Proportion of Participants Confirmed as Improvement Responders for Primary Multicomponent Endpoint
72 weeks

Estimated proportion of participants experiencing confirmed improvement in any 1 or more of the following components: a ≥1 point decrease in the Expanded Disability Status Scale (EDSS) score from a baseline score of \<=6.0 (decrease sustained for ≥3 months); a ≥15% improvement from baseline in time to complete 9-Hole Peg Test (9HPT) by either hand (improvement sustained for ≥3 months for the same hand), where the time is the average time of 2 trials per hand at the same visit; a ≥15% improvement from baseline in time to complete Timed 25-Foot Walk (T25FW) test (improvement sustained for ≥3 months), where the time is the average time of 2 trials at the same visit; or a ≥15% improvement from baseline 3-Second Paced Auditory Serial Addition Test (PASAT-3) score (improvement sustained for 3 months or greater). Estimated proportion of responders is based on logistic regression adjusted for multiple sclerosis (MS) type, region and baseline component assessments.

Change in Full-field Visual Evoked Potential (FF-VEP) Latency at Week 24: Intent-to-treat (ITT) Population
Baseline, Week 24

Adjusted mean change in optic nerve conduction velocity (NCV) at Week 24 for the affected eye from the baseline of unaffected fellow eye as determined by FF-VEP. Adjusted for the baseline latency of fellow eye.

Change in FF-VEP Latency at Week 24: Per-protocol Population
Baseline, Week 24

Adjusted mean change in optic nerve conduction velocity (NCV) at Week 24 for the affected eye from the baseline of unaffected fellow eye as determined by FF-VEP. Adjusted for the baseline latency of fellow eye.

PK parameter of BIIB033: Area under the concentration-time curve from time 0 to infinity (AUC0-inf)
Up to Day 89
PK parameter of BIIB033: Area under the concentration-time curve from time 0 to Day 85 (AUC84d)
Day 85
PK parameter of BIIB033: Maximum observed concentration (Cmax)
Up to Day 89
Number of participants experiencing Adverse Events (AEs) and Serious Adverse Events (SAEs)
Up to day 113
Number of participants with clinically significant laboratory parameters
Up to day 113
Number of participants with clinically significant vital sign abnormalities
Up to day 113
Number of participants with clinically significant electrocardiograms (ECGs) abnormalities
Up to day 113
Number of participants with clinically significant physical examination abnormalities
Up to day 113
Number of participants with clinically significant neurological examination abnormalities
Up to day 113
Evaluate safety and tolerability profile of two IV infusions of BIIB033 in subjects with MS
For duration of study / 6 months
Identify incidence and types of adverse events
For duration of study / 6 months
The incidence of serious adverse events
For duration of study / 6 months
Changes from baseline in clinical lab assessments and vital signs
For duration of study / 6 months
Changes form baseline in other safety measures: physical and neurological examinations, brain MRIs, and ECGs
For duration of study / 6 months
Safety as measured by adverse event monitoring, laboratory assessments and MRI
up to 4 months
Tolerability as measured by adverse event monitoring, laboratory assessments and MRI
up to 4 months

Secondary Endpoints

Number of Participants That Developed Clinically Definite Multiple Sclerosis (CDMS) After Enrollment in RENEW Study (NCT01721161)
RENEW Study (NCT01721161) to Day 1 (NCT02657915)
Time to Diagnosis of CDMS
RENEW Study (NCT01721161) to Day 1 (NCT02657915)
Severity of Central Nervous System (CNS) Demyelinating Disease as Assessed Using the Expanded Disability Status Scale (EDSS)
Day 1 (NCT02657915)
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Study Design & Arms

AllocationRANDOMIZED
MaskingTRIPLE
ModelPARALLEL
PurposeOTHER

Treatment Arms

ArmTypeDescription
PlaceboPLACEBO_COMPARATORThis was a follow-up study, investigational product was administered in the previous study. Participants in the placebo arm have received at least 1 dose of placebo.
BIIB033 100mg/KgEXPERIMENTALThis was a follow-up study, investigational product was administered in the previous study. Participants in the BIIB033 arm have received at least 1 dose of 100 mg/kg BIIB033.
BIIB033, 3 mg/kgEXPERIMENTALBIIB033 3 mg/kg once every 4 weeks intravenous (IV) infusion up to Week 72. Avonex once-weekly intramuscular (IM) injection up to Week 84.
BIIB033, 10 mg/kgEXPERIMENTALBIIB033 10 mg/kg once every 4 weeks IV infusion up to Week 72. Avonex once-weekly IM injection up to Week 84.
BIIB033, 30 mg/kgEXPERIMENTALBIIB033 30 mg/kg once every 4 weeks IV infusion up to Week 72. Avonex once-weekly IM injection up to Week 84.
BIIB033, 100 mg/kgEXPERIMENTALBIIB033 100 mg/kg once every 4 weeks IV infusion up to Week 72. Avonex once-weekly IM injection up to Week 84.
BIIB033EXPERIMENTALParticipants will receive BIIB033 once every 4 weeks for 20 weeks (a total of 6 doses).
BIIB033-AEXPERIMENTALStaggered single dosing schema
BIIB033-BEXPERIMENTALStaggered single dosing schema
Cohort 1EXPERIMENTALA single IV dose of 10 mg/kg BIIB033 or placebo given on Day 1
Cohort 2EXPERIMENTALA single IV dose of 30 mg/kg BIIB033 or placebo given on Day 1
Cohort 3EXPERIMENTALOne IV dose of 100 mg/kg BIIB033 or placebo given on Days 1 and 15
Active study drugEXPERIMENTALTreatment
ComparatorEXPERIMENTALDummy drug

Interventions

NameTypeDescription
PlaceboDRUGAdministered as specified in the treatment arm.
BIIB033 100mg/KgDRUGAdministered as specified in the treatment arm.
BIIB033DRUG -
AvonexDRUG -
BIIB033 (anti-LINGO-1 mAb)BIOLOGICAL100 mg/kg via IV infusion once every 4 weeks for 20 weeks (a total of 6 doses).
BIIB033 (opicinumab)DRUG -
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites23

Key Inclusion Criteria: * Must have participated in Study NCT01721161 and received at least 1 dose of BIIB033 or placebo, as per protocol, within 2 years (+ 4 months) from Day 1 of this study (2 years from Week 32 or projected Week 32 visit, if the subject did not complete all visits in Study NCT01...

Countries:AustraliaBelgiumCanadaCzechiaDenmarkGermanyHungaryItalySpainSwedenUnited KingdomUnited StatesFranceNetherlandsPolandRussiaSerbia
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Frequently asked questions about BIIB033

What is BIIB033 used for?

BIIB033 is an investigational monoclonal antibody being studied for central nervous system demyelinating diseases, including multiple sclerosis and acute optic neuritis. It has been evaluated in Phase 2 clinical trials for relapsing-remitting multiple sclerosis and acute optic neuritis, with completed studies involving over 400 participants.

Who is developing BIIB033?

BIIB033 is being developed by Biogen Inc., a biotechnology company traded on the NASDAQ under the ticker BIIB. Biogen has sponsored multiple clinical trials of BIIB033, including Phase 2 studies in multiple sclerosis and acute optic neuritis.

What phase is BIIB033 in?

BIIB033 has completed Phase 2 clinical trials. It is an investigational drug and has not been approved by the FDA. The completed Phase 2 studies assessed its efficacy, safety, tolerability, and pharmacokinetics in participants with relapsing forms of multiple sclerosis and acute optic neuritis.

What clinical trials has BIIB033 been in?

BIIB033 has been studied in several completed clinical trials, including NCT01721161 in acute optic neuritis (82 participants), NCT01864148 in relapsing forms of multiple sclerosis (419 participants), NCT02657915 as a long-term remyelinating therapy assessment (52 participants), and NCT02833142 evaluating pharmacokinetics and safety (28 participants).

Is BIIB033 the same as opicinumab?

Yes, BIIB033 is also known as opicinumab. In clinical trial NCT02833142, the drug is referred to as BIIB033 (opicinumab), confirming that both names refer to the same investigational monoclonal antibody being developed by Biogen.

Was BIIB033 studied in healthy volunteers?

Yes, one completed Phase 1 trial of BIIB033, NCT02833142, enrolled healthy volunteers. This study evaluated the pharmacokinetics, safety, and tolerability of single doses of BIIB033 produced by two manufacturing processes, with 28 participants in the United States.