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R3R01

Phase 2

Alport Syndrome | Small molecule | Nephrology |Baxter International Inc.|Last Updated: Jun 29, 2026

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment43

FDA Designations

No designations recorded

Clinical trial landscape

R3R01 · 2 trials · 3 indications

Phase 2 2
NCT06600412The Evaluation of the Drug R3R01 for the Excretion of Protein in the Urine in Patients With Diabetic Kidney Disease.Diabetic Kidney Disease
RECRUITING60 Analytics
NCT05267262Study to Evaluate R3R01 in Patients With Alport Syndrome and Patients With Focal Segmental GlomerulosclerosisAlport Syndrome
COMPLETED43 Analytics
PHASE2RECRUITING
The Evaluation of the Drug R3R01 for the Excretion of Protein in the Urine in Patients With Diabetic Kidney Disease.
Diabetic Kidney DiseaseUnlock trial analytics
PHASE2COMPLETED
Study to Evaluate R3R01 in Patients With Alport Syndrome and Patients With Focal Segmental Glomerulosclerosis
Alport SyndromeUnlock trial analytics

Study Endpoints

Primary Endpoints

Urinary albumin-to-creatinine ratio (UACR)
12 weeks (84 days)

Urinary albumin-to-creatinine ratio (UACR) (Change from baseline to end of treatment at 12 weeks (84 days).

Incidence of adverse events (Safety and Tolerability)
12 weeks

Safety and tolerability as determined by the incidence of adverse events (AEs)

Assess change in urine creatinine protein ratio
12 weeks

Change from baseline in urine creatinine protein ratio for Cohort 1 (Alport Syndrome patient group) and Cohort 2(Focal Segmental Glomerulosclerosis patient group).

Secondary Endpoints

Measured or Estimated Glomerular Filtration Rate
12 weeks (84 days)
24 hours ambulatory blood pressure
12 weeks (84 days)
Plasma Pharmacokinetics
24 weeks (168 days)
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
R3R01EXPERIMENTALR3R01 oral tablet (200 mg twice daily) for 12 weeks
PlaceboPLACEBO_COMPARATORPlacebo oral tablet twice daily for 12 weeks
Cohort 2 (Alport Syndrome Patients)EXPERIMENTALR3R01 administered orally as 200 mg tablets twice daily for 84 days.
Cohort 3 (Focal Segmental Glomerulosclerosis Patients)EXPERIMENTALR3R01 administered orally as 200 mg tablets twice daily for the 84 days.

Interventions

NameTypeDescription
R3R01DRUGR3R01 is an ATP-binding cassette transporter A1 (ABCA1) inducer, which increases the efflux of cholesterol from the intracellular space in the kidney. Please refer to arm/group description for further information.
PlaceboDRUGPlease refer to arm/group description for further information.
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: 1. Adults (above 18 years of age) with controlled type 2 diabetes (hemoglobin A1c less than 10.5%). 2. Stable antihypertensive treatment 4 weeks before start of study drug and throughout study duration. 3. Titrated to the maximal dose or maximal tolerated dose of renin-angiotens...

Countries:DenmarkUnited StatesBelgiumFranceGermanyNetherlandsUnited Kingdom
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Frequently asked questions about R3R01

What is R3R01 used for?

R3R01 is an investigational small molecule being studied for Alport Syndrome and Diabetic Kidney Disease. It is in Phase 2 clinical development and is not yet approved by regulatory authorities. The drug is being evaluated for its effect on protein excretion in the urine in patients with these kidney conditions.

Who makes R3R01?

R3R01 is being developed by Baxter International Inc., a company traded on the New York Stock Exchange under the ticker BAX. The drug is currently in Phase 2 clinical trials for kidney-related conditions.

What phase is R3R01 in?

R3R01 is in Phase 2 clinical development. It is an investigational drug and has not been approved by regulatory agencies. Clinical trials are ongoing to evaluate its safety and efficacy in patients with Alport Syndrome and Diabetic Kidney Disease.

What clinical trials is R3R01 in?

R3R01 has been studied in two Phase 2 trials. One trial, NCT05267262, evaluated the drug in patients with Alport Syndrome and Focal Segmental Glomerulosclerosis and has been completed. Another trial, NCT06600412, is currently recruiting patients with Diabetic Kidney Disease in Denmark.

Is R3R01 the same as any other drug?

R3R01 is a distinct investigational drug candidate. It is being developed specifically for kidney diseases, including Alport Syndrome and Diabetic Kidney Disease. No alternative names for R3R01 have been reported in clinical trial registries.