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AXS-12

Phase 3

Narcolepsy | Small molecule | Neurology |Axsome Therapeutics, Inc.|Last Updated: Jun 15, 2026

Success Probability

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials3
Total Enrollment179

FDA Designations

ORPHAN_DRUG

Clinical trial landscape

AXS-12 · 3 trials · 5 indications

Phase 3 2Phase 2 1
NCT05113745A Study to Assess the Long-term Efficacy and Safety of AXS-12 (Reboxetine) in Subjects With Narcolepsy (ENCORE)Narcolepsy
COMPLETED68 Analytics
NCT05059223A Study to Assess the Efficacy and Safety of AXS-12 (Reboxetine) in Patients With NarcolepsyNarcolepsy
COMPLETED90 Analytics
PHASE3COMPLETED
A Study to Assess the Long-term Efficacy and Safety of AXS-12 (Reboxetine) in Subjects With Narcolepsy (ENCORE)
NarcolepsyUnlock trial analytics
PHASE3COMPLETED
A Study to Assess the Efficacy and Safety of AXS-12 (Reboxetine) in Patients With Narcolepsy
NarcolepsyUnlock trial analytics

Study Endpoints

Primary Endpoints

Long-term safety as measured by the incidence of treatment-emergent adverse events
Up to 28 weeks
Efficacy as measured by change in frequency of cataplexy attacks from baseline.
Baseline to Week 27
Frequency of cataplexy attacks
Change from Baseline to Week 5

Average number of cataplexy attacks per week

Change From Baseline in the Weekly Average Total Number of Cataplexy Attacks
2 weeks

Presented as LSmeans. A positive change is indicative of improvement.

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Study Design & Arms

AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
AXS-12 (reboxetine)EXPERIMENTAL* Up to 24 weeks in open-label period * Up to 4 weeks in randomized double-blind period
PlaceboPLACEBO_COMPARATORUp to 4 weeks in randomized double-blind period

Interventions

NameTypeDescription
AXS-12 (reboxetine)DRUGAXS-12 tablets, taken twice daily
PlaceboDRUGPlacebo tablets, taken twice daily
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Eligibility Criteria

Age Range15 Years to 75 Years
SexALL
Healthy VolunteersNo
Study Sites25

Inclusion Criteria: * Completed the treatment period of Study AXS-12-301 * Willing and able to comply with the study requirements Exclusion Criteria: * Significant change in medical history or concomitant medications since enrolling in the AXS-12-301 study which, in the opinion of the Investigato...

Countries:United StatesCanada
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Recent Changes (Last 90 Days)

MEDIUMJul 16, 2026NCT03881852TRIAL_REMOVED: changed
MEDIUMJul 16, 2026NCT03881852TRIAL_REMOVED: changed
MEDIUMJul 16, 2026NCT03881852TRIAL_REMOVED: changed
MEDIUMJun 28, 2026NCT05059223TRIAL_REMOVED: changed
MEDIUMJun 28, 2026NCT05059223TRIAL_REMOVED: changed
MEDIUMJun 28, 2026NCT05059223TRIAL_REMOVED: changed
MEDIUMJun 28, 2026NCT05059223TRIAL_REMOVED: changed

Frequently asked questions about AXS-12

What is AXS-12 used for?

AXS-12 is an investigational small molecule being developed for the treatment of narcolepsy, including cataplexy and excessive daytime sleepiness. It is being studied in patients aged 15 years and older. AXS-12 has received orphan drug designation from the FDA for this condition.

What does AXS-12 target?

AXS-12 is a small molecule that targets the norepinephrine transporter. By inhibiting this transporter, it is believed to increase norepinephrine levels in the brain, which may help regulate sleep-wake cycles and reduce cataplexy episodes in patients with narcolepsy.

Who makes AXS-12?

AXS-12 is being developed by Axsome Therapeutics, Inc., a biopharmaceutical company traded on NASDAQ under the ticker symbol AXSM. The company is conducting clinical trials to evaluate the efficacy and safety of AXS-12 in patients with narcolepsy.

What phase is AXS-12 in?

AXS-12 is currently in Phase 3 clinical development for narcolepsy. It has completed three clinical trials, including two Phase 3 studies and one Phase 2 study. AXS-12 is investigational and has not been approved by the FDA for any use.

What clinical trials is AXS-12 in?

AXS-12 has been studied in three completed clinical trials. The Phase 2 CONCERT trial (NCT03881852) enrolled 21 patients, while the Phase 3 trials NCT05059223 and NCT05113745 enrolled 90 and 68 patients, respectively. All trials evaluated AXS-12 in patients with narcolepsy and cataplexy.

Is AXS-12 the same as reboxetine?

Yes, AXS-12 is also known as reboxetine. Clinical trials for AXS-12 use the name reboxetine in their titles, such as the CONCERT study. Reboxetine is a selective norepinephrine reuptake inhibitor being repurposed for the treatment of narcolepsy.