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ARO-HSD

Phase 1

Non-alcoholic Steatohepatitis | Small molecule | Metabolic |Arrowhead Pharmaceuticals, Inc.|Last Updated: Oct 3, 2025

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment50

FDA Designations

No designations recorded

Clinical trial landscape

ARO-HSD · 1 trial · 1 indication

Phase 1 1
NCT04202354Study of ARO-HSD in Healthy Volunteers and Patients With Non-Alcoholic Steatohepatitis (NASH) or Suspected NASHNon-alcoholic Steatohepatitis
COMPLETED50 Analytics
PHASE1COMPLETED
Study of ARO-HSD in Healthy Volunteers and Patients With Non-Alcoholic Steatohepatitis (NASH) or Suspected NASH
Non-alcoholic SteatohepatitisUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of Participants With Treatment-Emergent Adverse Events (TEAEs) Possibly or Probably Related to Treatment
From first dose of study drug through Day 113 (±5 days)

Adverse event (AE)=any untoward medical occurrence that does not necessarily have to have a causal relationship with this treatment. TEAEs=AEs with onset after administration of the study drug, or when a pre-existing medical condition increases in severity or frequency after study drug administration. Serious adverse event (SAE)= an AE that results in death; is life-threatening; requires inpatient hospitalization or prolongation of an existing hospitalization; results in persistent or significant disability/incapacity; is a congenital anomaly/birth defect; is a medically important event or reaction.

Secondary Endpoints

Pharmacokinetics (PK) of ARO-HSD: Plasma Concentrations
Normal Healthy Volunteers: Day 1: 2 hours pre-dose, 15 minutes, 30 minutes, 1, 2, 4, 8, 12, 18, 24; Day 2: 48 hours post-dose, Days 8, 15, 29. NASH Participants: Day 1: 2 hours pre-dose, 30 minutes, 1, 2, 24, hours post-dose, Days 8, 15, 29
PK of ARO-HSD in Normal Healthy Volunteers: Maximum Observed Plasma Concentration (Cmax)
Day 1: Predose, 15 minutes, 30 minutes, 1, 2, 4, 8 12, 18, 24, 48 hours postdose
PK of ARO-HSD in Normal Healthy Volunteers: Time to Reach Cmax (Tmax)
Day 1: Predose, 15 minutes, 30 minutes, 1, 2, 4, 8 12, 18, 24, 48 hours postdose
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Cohort 1: ARO-HSD 25 mgEXPERIMENTALNormal healthy volunteers randomized to double blind ARO-HSD 25 mg on Day 1 only.
Cohort 1: PlaceboPLACEBO_COMPARATORNormal healthy volunteers randomized to double blind placebo on Day 1 only.
Cohort 2: ARO-HSD 50 mgEXPERIMENTALNormal healthy volunteers randomized to double blind ARO-HSD 50 mg on Day 1 only.
Cohort 2: PlaceboPLACEBO_COMPARATORNormal healthy volunteers randomized to double blind placebo on Day 1 only.
Cohort 3: ARO-HSD 100 mgEXPERIMENTALNormal healthy volunteers randomized to double blind ARO-HSD 100 mg on Day 1 only.
Cohort 3: PlaceboPLACEBO_COMPARATORNormal healthy volunteers randomized to double blind placebo on Day 1 only.
Cohort 4: ARO-HSD 200 mgEXPERIMENTALNormal healthy volunteers randomized to double blind ARO-HSD 200 mg on Day 1 only.
Cohort 4: PlaceboPLACEBO_COMPARATORNormal healthy volunteers randomized to double blind placebo on Day 1 only.
Cohort 1b: ARO-HSD 25 mgEXPERIMENTALParticipants with suspected non-alcoholic steatohepatitis (NASH) receive open-label ARO-HSD 25 mg on Days 1 and 29.
Cohort 3b: ARO-HSD 100 mgEXPERIMENTALParticipants with suspected NASH receive open-label ARO-HSD 100 mg on Days 1 and 29.
Cohort 4b: ARO-HSD 200 mgEXPERIMENTALParticipants with suspected NASH receive open-label ARO-HSD 200 mg on Days 1 and 29.

Interventions

NameTypeDescription
ARO-HSD InjectionDRUGsingle or multiple doses of ARO-HSD by subcutaneous (sc) injections
sterile normal saline (0.9% NaCl)DRUGcalculated volume to match active treatment, by sc injection
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Eligibility Criteria

Age Range19 Years to 65 Years
SexALL
Healthy VolunteersYes
Study Sites1

Inclusion Criteria: * Women of child bearing potential must have a negative pregnancy test, cannot be breastfeeding and must be willing to use contraception * Willing to provide written informed consent and to comply with study requirements * On a stable diet for at least 4 weeks with no plans to s...

Countries:New Zealand
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Frequently asked questions about ARO-HSD

What is ARO-HSD used for?

ARO-HSD is an investigational drug being developed for the treatment of non-alcoholic steatohepatitis (NASH), a condition characterized by fat accumulation and inflammation in the liver. It is currently in Phase 1 clinical development and has not been approved by regulatory authorities.

Who makes ARO-HSD?

ARO-HSD is being developed by Arrowhead Pharmaceuticals, Inc., a biopharmaceutical company traded on the NASDAQ under the ticker symbol ARWR. The company is conducting clinical trials to evaluate the safety and efficacy of this investigational drug.

What phase is ARO-HSD in?

ARO-HSD is in Phase 1 clinical development. A Phase 1 trial has been completed, which involved healthy volunteers and patients with non-alcoholic steatohepatitis (NASH) or suspected NASH. The drug remains investigational and is not yet approved for any use.

What clinical trials is ARO-HSD in?

ARO-HSD has one completed Phase 1 clinical trial, identified as NCT04202354. This study enrolled 50 participants in New Zealand and evaluated the drug in healthy volunteers and patients with non-alcoholic steatohepatitis (NASH) or suspected NASH. The trial was randomized, double-blind, and placebo-controlled.

Is ARO-HSD the same as any other drug?

No alternative names for ARO-HSD have been disclosed. The drug is identified solely by its code name ARO-HSD in clinical trial registries and by its developer, Arrowhead Pharmaceuticals.