Recent Updates
Recently added Catalysts

ARC-520

Phase 1

Healthy | Small molecule | Other |Arrowhead Pharmaceuticals, Inc.|Last Updated: Jan 13, 2026

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials2
Total Enrollment94

FDA Designations

No designations recorded

Clinical trial landscape

ARC-520 · 2 trials · 1 indication

Phase 1 2
NCT02535416A Study of ARC-520 at Varying Infusion Rates in Healthy Adult VolunteersHealthy
COMPLETED40 Analytics
NCT01872065Safety and Tolerability Study of ARC-520 in Healthy VolunteersHealthy
COMPLETED54 Analytics
PHASE1COMPLETED
A Study of ARC-520 at Varying Infusion Rates in Healthy Adult Volunteers
HealthyUnlock trial analytics
PHASE1COMPLETED
Safety and Tolerability Study of ARC-520 in Healthy Volunteers
HealthyUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of Participants With Treatment-Emergent Adverse Events (TEAEs)
post-dose through the end of study (Day 15 ± 1 day) plus 30 days

An adverse event (AE) is defined as any untoward medical occurrence that does not necessarily have a causal relationship with this treatment. TEAEs were defined as all AEs starting or worsening after commencement of treatment with investigational product.

To determine the incidence and frequency of adverse events as a measure of safety and tolerability of ARC-520
One month

The incidence and frequency of adverse events (AEs), serious adverse events (SAEs), related AEs, related SAEs, and AEs leading to withdrawal, dose modification, or treatment discontinuation will be summarized by dose and treatment group.

Secondary Endpoints

Pharmacokinetics: Area Under the Plasma Concentration Versus Time Curve From Zero to 24 Hours (AUC0-24) of the Analytes of ARC-520
Day 1 pre-dose through 48 hours post-dose
Pharmacokinetics: Area Under the Plasma Concentration-Time Curve From Time 0 to the Last Quantifiable Plasma Concentration (AUClast) of the Analytes of ARC-520
Day 1 pre-dose through 48 hours post-dose
Pharmacokinetics: Area Under the Plasma Concentration Versus Time Curve From Zero Extrapolated to Infinity (AUCinf) of the Analytes of ARC-520
Day 1 pre-dose through 48 hours post-dose
Unlock Study Endpoints

Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
ARC-520 Cohort 1EXPERIMENTALSingle dose, intravenous administration of ARC-520 at 4.0 mg/kg 0.6 mL/min + cetirizine
ARC-520 Cohort 2AEXPERIMENTALSingle dose, intravenous administration of ARC-520 at 4.0 mg/kg 0.9 mL/min + cetirizine
ARC-520 Cohort 2EXPERIMENTALSingle dose, intravenous administration of ARC-520 at 4.0 mg/kg 0.75 mL/min + diphenhydramine
ARC-520 Cohort 3EXPERIMENTALSingle dose, intravenous administration of ARC-520 at 4.0 mg/kg 0.9 mL/min + diphenhydramine
ARC-520 Cohort 4EXPERIMENTALSingle dose, intravenous administration of ARC-520 at 4.0 mg/kg 1.2 mL/min + diphenhydramine
ARC-520 Cohort 5EXPERIMENTALSingle dose, intravenous administration of ARC-520 at 4.0 mg/kg 1.5 mL/min + diphenhydramine
ARC-520 Cohort 6EXPERIMENTALSingle dose, intravenous administration of ARC-520 at 4.0 mg/kg 5 minute slow bolus push + diphenhydramine
ARC-520 Cohort 7EXPERIMENTALSingle dose, intravenous administration of ARC-520 at 5.0 mg/kg 0.9 mL/min + diphenhydramine
ARC-520 Cohort 8EXPERIMENTALSingle dose, intravenous administration of ARC-520 at 6.0 mg/kg 0.9 mL/min + diphenhydramine
ARC-520EXPERIMENTALSingle dose, intravenous administration of ARC-520.
Normal SalinePLACEBO_COMPARATORSingle dose, intravenous administration of Normal Saline

Interventions

NameTypeDescription
ARC-520DRUG -
cetirizineDRUG -
diphenhydramineDRUG -
PlaceboDRUG -
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to 55 Years
SexALL
Healthy VolunteersYes
Study Sites1

Inclusion Criteria: * Male or female, 18-55 years of age, inclusive * Able to provide written informed consent * BMI between 19.0 and 35.0 kg/m2, inclusive * 12-lead ECG at Screening and pre-dose with no clinically significant abnormalities * Highly effective, double barrier contraception (both mal...

Countries:Australia
Unlock Eligibility Criteria

Frequently asked questions about ARC-520

What is ARC-520 used for?

ARC-520 is an investigational drug being studied in healthy volunteers. It is being evaluated for safety and tolerability in Phase 1 clinical trials. The drug is not approved for any condition and remains in clinical development.

Who makes ARC-520?

ARC-520 is being developed by Arrowhead Pharmaceuticals, Inc., a biopharmaceutical company traded on the NASDAQ under the ticker ARWR. The company is conducting clinical trials to evaluate the drug's safety and tolerability in healthy volunteers.

What phase is ARC-520 in?

ARC-520 is in Phase 1 clinical development. Two Phase 1 trials have been completed, both involving healthy adult volunteers. The drug is investigational and has not been approved by regulatory authorities.

What clinical trials is ARC-520 in?

ARC-520 has been studied in two completed Phase 1 trials. The first, NCT01872065, assessed safety and tolerability in 54 healthy volunteers in Australia. The second, NCT02535416, evaluated varying infusion rates in 40 healthy adult volunteers, also in Australia.

Is ARC-520 a small molecule drug?

Yes, ARC-520 is classified as a small molecule drug. It is being studied in healthy volunteers to assess its safety and tolerability, with two completed Phase 1 trials involving a total of 94 participants.