Recent Updates
Recently added Catalysts

APR-246

Phase 2

Acute Myeloid Leukemia or Myelodysplastic Syndromes | Small molecule | Oncology |Aprea Therapeutics, Inc.|Last Updated: Mar 17, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
Premium
Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
Premium
Trial Design
UNCONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment33
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT03931291APR-246 in Combination With Azacitidine for TP53 Mutated AML (Acute Myeloid Leukemia) or MDS (Myelodysplastic Syndromes) Following Allogeneic Stem Cell TransplantPHASE2 COMPLETED 33Sep 16, 2019Jan 14, 2022Mar 17, 20257 United States
Unlock Drug Trial Details
Study Endpoints
Primary Endpoints
To Assess Relapse-free Survival (RFS) in Patients With TP53 Mutated AML or MDS After Undergoing Allogeneic Hematopoietic Stem Cell Transplant (HSCT).
Through study completion, an average of 1 year

Relapse-free survival (RFS) at 12 months or longer if data permits. RFS was defined as the time from HCT to relapse after HCT or death, whichever occurred first.

Unlock Study Endpoints
Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Experimental arm: APR-246 + azacitidineEXPERIMENTALAPR-246 and azacitidine maintenance therapy will continue for a maximum of 12 cycles
Interventions
NameTypeDescription
APR-246DRUGAPR-246 will be administered on Days 1-4, with azacitidine on Days 1-5, of every 28 day cycle. Patients may receive a maximum of 12 cycles.
Unlock Study Design Details
Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites7

Inclusion Criteria: 1. Patient must have previously met pre-transplantation eligibility. 2. Patient has received an allogeneic transplant for AML or MDS. 3. Any standard (non-study) conditioning \[MAC (myeloablative conditioning), RIC (reduced intensity conditioning), or NMA (non-myeloablative cond...

Countries:United States
Unlock Eligibility Criteria