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AL001

Phase 2

Frontotemporal Dementia | Small molecule | Neurology |Alector, Inc.|Last Updated: Dec 5, 2025

Success Probability
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Market & Valuation
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Trial Design
UNCONTROLLEDDMC
Total Trials1
Total Enrollment33
FDA Designations
No designations recorded
Clinical trial landscape

AL001 · 2 trials · 2 indications

Phase 2 1Phase 1 1
NCT03987295A Phase 2 Study to Evaluate Safety of Long-term AL001 Dosing in Frontotemporal Dementia (FTD) Patients (INFRONT-2)Frontotemporal Dementia
COMPLETED33 Analytics
PHASE2COMPLETED
A Phase 2 Study to Evaluate Safety of Long-term AL001 Dosing in Frontotemporal Dementia (FTD) Patients (INFRONT-2)
Frontotemporal DementiaUnlock trial analytics
Study Endpoints
Primary Endpoints
Severity of TEAEs
197 weeks

Number of TEAEs categorized by severity

Severity of Treatment-Related TEAEs
197 weeks

Number of treatment-related TEAEs categorized by severity

Any TEAE Leading to Study Drug Discontinuation
197 weeks

Number of TEAEs leading to study drug discontinuation

Immunogenicity Antidrug Antibodies (ADA) Titer
97 weeks

Titer values of antidrug antibodies (ADAs) in participants receiving latozinemab at week 97/Part 1 end of study

Confirmatory Immunogenicity Antidrug Antibodies (ADA) Responses
97 weeks

Presence of confirmatory antidrug antibodies (ADAs) in participants who test positive for ADA at week 97 (Part 1 End of Study).

Change From Baseline in Sheehan Suicidality Tracking Scale
197 weeks

The Sheehan Suicidality Tracking Scale (S-STS) is a structured assessment tool used to evaluate the presence, severity, and frequency of suicidal ideation and behavior. It includes items that address passive thoughts of death, active suicidal ideation, intent, planning, suicide attempts, and non-suicidal self-injury. The S-STS total score ranges from 0 to 64, based on 16 items each rated from 0 (not at all) to 4 (extremely), with higher scores indicating greater severity of suicidal ideation, intent, or behavior. The total score provides a quantitative measure of suicidality severity and is sensitive to change over time, making it suitable for clinical monitoring and research use.

Evaluation of safety and tolerability of AL001 measured by number of subjects with adverse events and Dose Limiting Adverse Event (DLAEs)
85 days

Incidence of adverse events and dose limiting Adverse Events during the DLAE observation period and/or study treatment periods.

Secondary Endpoints
Longitudinal Percent Change From Baseline of CSF PGRN
97 weeks
Longitudinal Percent Change From Baseline in Plasma PGRN
97 weeks
Longitudinal Levels of Sortilin in WBCs
97 weeks
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Granulin and C9orf72EXPERIMENTALIV administration of AL001; 60 mg/kg, every 4 weeks \[q4w\]
AL001EXPERIMENTALUp to six single ascending doses of AL001
Saline SolutionPLACEBO_COMPARATORSaline solution will be administered as a single infusion for each cohort in a ratio of 6 active and 2 placebo subjects
Interventions
NameTypeDescription
AL001DRUG60 mg/kg of AL001 every 4 weeks
PlaceboOTHERSaline solution administered as a single infusion as palcebo.
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Eligibility Criteria
Age Range18 Years to 85 Years
SexALL
Healthy VolunteersNo
Study Sites12

Inclusion Criteria: * At screening, female participants must be nonpregnant and nonlactating * In good physical health on the basis of no clinically significant findings from medical history, physical examinations (PEs), laboratory tests, ECGs, and vital signs. * Participant is a carrier of a loss ...

Countries:United StatesCanadaGermanyItalyNetherlandsUnited Kingdom
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