Recent Updates
Recently added Catalysts

Perifosine

Phase 2

Malignant Gliomas | Small molecule | Oncology |Akebia Therapeutics, Inc.|Last Updated: Oct 19, 2020

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
Premium
Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
Premium
Trial Design
UNCONTROLLEDBiomarker
Total Trials1
Total Enrollment32
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00590954Clinical and Molecular-Metabolic Phase II Trial of Perifosine for Recurrent/Progressive Malignant GliomasPHASE2 COMPLETED 32May 1, 2006Nov 11, 2019Oct 19, 20201 United States
Unlock Drug Trial Details
Study Endpoints
Primary Endpoints
Determine the Efficacy of Perifosine in Patients With Recurrent/Progressive GBMs Not Taking EIAEDs as Measured by 6 Month Progression Free Survival/PFS.
6 months
Secondary Endpoints
Determine Metabolic Effects of Perifosine on Malignant Gliomas by PET Imaging
2 years
Unlock Study Endpoints
Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
TreatmentEXPERIMENTALFollowing a diagnosis of tumor recurrence or progression, all patients will receive perifosine monotherapy until toxicity, progression, or death.
Interventions
NameTypeDescription
PerifosineDRUGDosing will be continuous, and for the purpose of this trial a cycle will be defined as 28 days. Perifosine will be given as a 600 mg loading dose on day 1. The loading dose will be divided into 4 equal doses of 150 mg each. The first 3 doses should be given with food in the adult day hospital to allow intravenous antiemetic prophylaxis, and 4th dose at bedtime at home. The interval between doses of perifosine should be no less than 4 hours. On day 2, patients will start the maintenance dose of 100 mg daily at bedtime at home. In addition to baseline serum, all patients will have weekly serum drawn during weeks 2-4.
Unlock Study Design Details
Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: * Patients must have shown unequivocal evidence for tumor progression by MRI or CT scan. * Patients must be on a stable or decreasing dose of corticosteroids for a minimum of 5 days before the baseline MRI and PET scans. * Patients must have failed prior radiation therapy. * Pat...

Countries:United States
Unlock Eligibility Criteria