Recent Updates
Recently added Catalysts

Ranibizumab

Phase 2

Neovascular Age-Related Macular Degeneration (nAMD) | Monoclonal antibody | Ophthalmology |AbbVie Inc.|Last Updated: Aug 5, 2026

Target and mechanism

Molecular targetVEGFA
Target classInhibitor
ModalityMonoclonal antibody

Also known as Ranibizumab (LUCENTIS®)

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

RandomizedACTIVE_CONTROLLEDDMC
Total Trials2
Total Enrollment262

FDA Designations

No designations recorded

Clinical trial landscape

Ranibizumab · 5 trials · 4 indications

Phase 2 5
NCT05210803Long-Term Follow-Up Study of RGX-314 Administered in the Suprachoroidal Space for Participants With nAMDNeovascular Age-Related Macular Degeneration (nAMD)
ENROLLING BY_INVITATION116 Analytics
NCT04514653RGX-314 Gene Therapy Administered in the Suprachoroidal Space for Participants With Neovascular Age-Related Macular Degeneration (nAMD)Neovascular Age-Related Macular Degeneration (nAMD)
ACTIVE NOT_RECRUITING146 Analytics
NCT01492400Safety and Efficacy Study of Dexamethasone Versus Ranibizumab in Patients With Diabetic Macular EdemaMacular Edema
COMPLETED363 Analytics
NCT00775411Safety and Efficacy of a New Therapy as Adjunctive Therapy to Anti-vascular Endothelial Growth Factor (Anti-VEGF) in Subjects With Wet Age-Related Macular Degeneration (AMD)Choroidal Neovascularization
COMPLETED44 Analytics
NCT00511706Safety and Efficacy of a New Treatment as Adjunctive Therapy to Anti-vascular Endothelial Growth Factor (Anti-VEGF) Treatment in Patients With Age-Related Macular Degeneration (AMD)Choroidal Neovascularization
COMPLETED243 Analytics
PHASE2ENROLLING BY_INVITATION
Long-Term Follow-Up Study of RGX-314 Administered in the Suprachoroidal Space for Participants With nAMD
Neovascular Age-Related Macular Degeneration (nAMD)Unlock trial analytics
PHASE2ACTIVE NOT_RECRUITING
RGX-314 Gene Therapy Administered in the Suprachoroidal Space for Participants With Neovascular Age-Related Macular Degeneration (nAMD)
Neovascular Age-Related Macular Degeneration (nAMD)Unlock trial analytics
PHASE2COMPLETED
Safety and Efficacy Study of Dexamethasone Versus Ranibizumab in Patients With Diabetic Macular Edema
Macular EdemaUnlock trial analytics
PHASE2COMPLETED
Safety and Efficacy of a New Therapy as Adjunctive Therapy to Anti-vascular Endothelial Growth Factor (Anti-VEGF) in Subjects With Wet Age-Related Macular Degeneration (AMD)
Choroidal NeovascularizationUnlock trial analytics
PHASE2COMPLETED
Safety and Efficacy of a New Treatment as Adjunctive Therapy to Anti-vascular Endothelial Growth Factor (Anti-VEGF) Treatment in Patients With Age-Related Macular Degeneration (AMD)
Choroidal NeovascularizationUnlock trial analytics

Study Endpoints

Primary Endpoints

Incidences of ocular Adverse Events and any Serious Adverse Events
5 years inclusive of parent study

To evaluate the long-term safety of ABBV-RGX-314

Mean change from baseline in BCVA to Week 40 based on the Early Treatment Diabetic Retinopathy Study (ETDRS) score
40 weeks

The scale used is the early treatment diabetic retinopathy study (ETDRS) letter score from 0-100 and higher score being better vision.

Average Change From Baseline in Best Corrected Visual Acuity (BCVA) in the Study Eye
Baseline, 12 Months

BCVA is measured using an eye chart and is reported as the number of letters read correctly (ranging from 0 to 100 letters) in the study eye. The lower the number of letters read correctly on the eye chart, the worse the vision (or visual acuity). The average BCVA is calculated across study visits for each patient. A positive number change from baseline indicates an improvement and a negative number change from baseline indicates a worsening.

Change From Baseline in Central Retinal Thickness as Measured by Optical Coherence Tomography (OCT) at Week 4
Baseline, Week 4

Optical Coherence Tomography (OCT), a laser based non-invasive diagnostic system providing high-resolution imaging sections of the retina, was performed on the study eye after pupil dilation at baseline and Week 4.

Injection Free Interval
Week 1 to Week 25

The injection free interval was defined as the number of days between receiving the second ranibizumab injection (day 7 to 14) to the investigator's determination of eligibility to receive a third ranibizumab injection in the study eye.

Secondary Endpoints

Incidences of non-ocular Adverse Events and any Adverse Events of Special Interest
5 years inclusive of parent study
Mean change from baseline (ie, prior to ABBV-RGX-314 administration in the parent study) in BCVA based on ETDRS score in the study eye at assessed timepoints
5 years inclusive of parent study
Mean change from baseline (ie, prior to ABBV-RGX-314 administration in the parent study) in CRT as measured by SD-OCT in the study eye at assessed timepoints
5 years inclusive of parent study
Unlock Study Endpoints

Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Standard of CareOTHERDose Level (DL) 1-3 participants who received ABBV-RGX- 314 in the parent study will continue to receive standard of care for the study duration.
Supplemental TreatmentOTHERDL 4 participants from the parent study will be able to receive supplement ranibizumab based on protocol-specified criteria if they develop worsening nAMD activity.
Ranibizumab controlACTIVE_COMPARATORControl treatment arm
ABBV-RGX-314 Treatment Arm (Dose 1)EXPERIMENTALABBV-RGX-314 Dose 1
ABBV-RGX-314 Treatment Arm (Dose 2)EXPERIMENTALABBV-RGX-314 Dose 2
ABBV-RGX-314 Treatment Arm (Dose 3)EXPERIMENTALABBV-RGX-314 Dose 3
ABBV-RGX-314 Treatment Arm (Dose 3) and Local SteroidEXPERIMENTALABBV-RGX-314 Dose 3 and Local Steroid
ABBV-RGX-314 Treatment Arm (Dose 3) and Topical SteroidEXPERIMENTALABBV-RGX-314 Dose 3 and Topical Steroid
ABBV-RGX-314 Treatment Arm (Dose 4) and Topical SteroidEXPERIMENTALABBV-RGX-314 Dose 4 and Topical Steroid
dexamethasone Intravitreal ImplantEXPERIMENTALInjection of 700 ug dexamethasone intravitreal implant into the study eye on Day 1, Month 5, and Month 10.
ranibizumabACTIVE_COMPARATORInjection of ranibizumab 0.5 mg into the study eye on Day 1. Patients may receive additional injections on a monthly basis, as needed, for disease progression.
700 µg dexamethasone and ranibizumabEXPERIMENTAL700 µg dexamethasone intravitreal injection at Day 1 in the study eye. Ranibizumab injection at Week 2 or 3 per specified criteria and starting at Week 4 at the investigator's discretion in the study eye.
dexamethasone and ranibizumabEXPERIMENTALIntravitreal injection of dexamethasone 700 µg at Day 1; ranibizumab 500 µg at Day -30 and Day 7-14.
sham and ranibizumabSHAM_COMPARATORSham injection at Day 1; ranibizumab 500 µg at day -30 and Day 7-14.

Interventions

NameTypeDescription
Standard of CareDRUGStandard of Care
RanibizumabDRUGInjection
ABBV-RGX-314 Dose 1GENETICAAV8 vector containing a transgene for anti-VEGF fab (Dose 1)
ABBV-RGX-314 Dose 2GENETICAAV8 vector containing a transgene for anti-VEGF fab (Dose 2)
ABBV-RGX-314 Dose 3GENETICAAV8 vector containing a transgene for anti-VEGF fab (Dose 3)
Local SteroidDRUGLocal steroid
Topical SteroidDRUGTopical steroid
ABBV-RGX-314 Dose 4GENETICAAV8 vector containing a transgene for anti-VEGF fab (Dose 4)
dexamethasone Intravitreal ImplantDRUGInjection of 700 ug dexamethasone intravitreal implant into the study eye on Day 1, Month 5, and Month 10.
dexamethasoneDRUG700 µg dexamethasone intravitreal injection at Day 1 in the study eye.
shamOTHERSham needle-less injection administered in the study eye at Day 1.
Unlock Study Design Details

Eligibility Criteria

Age Range50 Years to 89 Years
SexALL
Healthy VolunteersNo
Study Sites16

Inclusion Criteria: 1. Must provide written, signed informed consent for this study. 2. Must have been enrolled in a previous clinical study of ABBV-RGX-314 in the treatment of nAMD and must have received an SCS injection of ABBV-RGX-314 in that study. 3. Must be willing and able to comply with all...

Countries:United StatesBelgiumDenmarkFranceGermanyIsraelItalyNetherlandsPortugalSouth AfricaSpainUnited KingdomAustraliaPhilippinesNew ZealandSouth Korea
Unlock Eligibility Criteria

Recent Changes (Last 90 Days)

MEDIUMAug 5, 2026NCT05210803Enrollment: 115 → 116

Frequently asked questions about Ranibizumab

What is Ranibizumab used for?

Ranibizumab is used for the treatment of macular edema, neovascular age-related macular degeneration (nAMD), and choroidal neovascularization. It is a monoclonal antibody being developed by AbbVie Inc. for ophthalmology indications. The drug is currently in Phase 2 clinical trials.

What does Ranibizumab target?

Ranibizumab is a monoclonal antibody that targets vascular endothelial growth factor (VEGF). By binding to VEGF, it inhibits the growth of abnormal blood vessels in the eye, which is relevant to conditions like neovascular age-related macular degeneration and macular edema.

Who makes Ranibizumab?

Ranibizumab is being developed by AbbVie Inc., which is listed on the stock exchange under the ticker ABBV. The drug is also known by the brand name LUCENTIS. It is currently in Phase 2 clinical development for ophthalmology indications.

What phase is Ranibizumab in?

Ranibizumab is in Phase 2 clinical trials. It is an investigational drug and has not been approved by regulatory authorities. The ongoing trials are evaluating its safety and efficacy for conditions such as neovascular age-related macular degeneration and macular edema.

What clinical trials is Ranibizumab in?

Ranibizumab has been studied in several clinical trials, including NCT00775411 for choroidal neovascularization, NCT01492400 for diabetic macular edema, and NCT04514653 and NCT05210803 for neovascular age-related macular degeneration. These trials are Phase 2 studies with a total enrollment of 363 participants across multiple countries.

Is Ranibizumab the same as LUCENTIS?

Yes, Ranibizumab is the same as LUCENTIS. LUCENTIS is the brand name under which ranibizumab is known. The drug is being developed by AbbVie Inc. for the treatment of eye conditions such as macular edema and neovascular age-related macular degeneration.