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Cladribine

Phase 2

Acute Monocytic Leukemia | Small molecule | Oncology |AbbVie Inc.|Last Updated: Apr 17, 2026

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDBiomarker
Total Trials1
Total Enrollment40

FDA Designations

No designations recorded

Clinical trial landscape

Cladribine · 2 trials · 14 indications

Phase 2 1Phase 1 1
NCT06504459Venetoclax in Combination With Cladribine and Cytarabine Alternating With Azacitidine Plus Venetoclax for the Treatment of Newly Diagnosed Monocytic AML and Active Signaling Mutated AMLAcute Monocytic Leukemia
RECRUITING40 Analytics
PHASE2RECRUITING
Venetoclax in Combination With Cladribine and Cytarabine Alternating With Azacitidine Plus Venetoclax for the Treatment of Newly Diagnosed Monocytic AML and Active Signaling Mutated AML
Acute Monocytic LeukemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Composite complete remission (CRc) rate
At start of treatment to post-induction disease assessment (Cycle 1 Day 21 or Cycle 2 Day 21. Each cycle is 28 days)

CRc is defined as achievement of complete remission (CR), CR with partial hematologic recovery (CRh) or CR with incomplete blood count recovery (CRi) after induction (or re-induction). The CRc rate will be computed on the safety set and presented with a point-estimate and exact binomial 95% confidence interval (CI). CRc will also be modeled with univariable logistic regressions, applied to the efficacy set, to determine if any baseline patient or disease feature is correlated with clinical response.

Incidence of adverse events (Phase I)
Up to 12 months
Maximum tolerated dose of venetoclax in combination with CLAG-M (Phase I)
Up to 12 months
Event free survival (Phase II)
At 6 months

Secondary Endpoints

Overall response rate (ORR)
At start of treatment to post-induction disease assessment (Cycle 1 Day 21 or Cycle 2 Day 21. Each cycle is 28 days)
Overall survival (OS)
At start of treatment to death up to 2 years
Event-free survival (EFS)
At start of treatment to primary refractory disease, hematologic relapse, discontinuation of treatment due to toxicity, disease progression or death up to 2 years
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Treatment (venetoclax, cladribine, cytarabine, azacitidine)EXPERIMENTALSee Detailed Description
Treatment (CLAG-M, venetoclax)EXPERIMENTALPatients will receive induction with granulocyte colony-stimulating factor on days 0-5 (if peripheral white blood cell count is less than 20,000/uL), cladribine on days 1-5, cytarabine on 1-5, and mitoxantrone on days 1-3. Patients also receive venetoclax orally (PO) on days 1-14. Treatment repeats every 28-35 days for up to 2 induction cycles including mitoxantrone, and up to 4 consolidation cycles without mitoxantrone in the absence of disease progression or unacceptable toxicity. Patients undergo bone marrow biopsy and/or aspiration, and blood sample collection throughout the study.

Interventions

NameTypeDescription
AzacitidineDRUGGiven IV or SC
Biospecimen CollectionPROCEDUREUndergo blood sample collection
Bone Marrow AspirationPROCEDUREUndergo bone marrow aspiration and biopsy
Bone Marrow BiopsyPROCEDUREUndergo bone marrow aspiration and biopsy
CladribineDRUGGiven IV
CytarabineDRUGGiven SC
EchocardiographyPROCEDUREUndergo ECHO
Lumbar PuncturePROCEDUREUndergo LP
Multigated Acquisition ScanPROCEDUREUndergo MUGA
Questionnaire AdministrationOTHERAncillary studies
VenetoclaxDRUGGiven PO
MitoxantroneDRUGGiven IV
Recombinant Granulocyte Colony-Stimulating FactorBIOLOGICALGiven subcutaneously
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites2

Inclusion Criteria: * Ability to comprehend the investigational nature of the study and provide informed consent (i.e., participant or legally authorized representative \[LAR\]). Written informed consent must be obtained prior to any study-specific procedures or interventions • Sign informed con...

Countries:United States
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Frequently asked questions about Cladribine

What is Cladribine used for?

Cladribine is being studied for the treatment of acute biphenotypic leukemia and acute monocytic leukemia, both of which are types of acute leukemia. It is also being investigated in clinical trials for acute myeloid leukemia and related high-grade myeloid neoplasms.

Who makes Cladribine?

Cladribine is being developed by AbbVie Inc., a biopharmaceutical company traded on the New York Stock Exchange under the ticker symbol ABBV.

What phase is Cladribine in?

Cladribine is in clinical development. It is being evaluated in a Phase 1 trial and a Phase 2 trial, both of which are currently recruiting participants. It is an investigational drug and has not been approved by the FDA.

What clinical trials is Cladribine in?

Cladribine is being studied in two active clinical trials. NCT04797767 is a Phase 1 trial testing venetoclax and CLAG-M in acute myeloid leukemia and high-grade myeloid neoplasms. NCT06504459 is a Phase 2 trial combining venetoclax with cladribine and cytarabine, alternating with azacitidine plus venetoclax, in newly diagnosed monocytic AML.

What does Cladribine target?

Cladribine is a small molecule used in oncology. Its specific molecular target is not disclosed in the available clinical trial information, but it is being studied in combination with other agents for the treatment of acute leukemias.

Is Cladribine the same as CLAG-M?

Cladribine is not the same as CLAG-M. CLAG-M is a chemotherapy regimen that includes cladribine, cytarabine, granulocyte colony-stimulating factor, and mitoxantrone. Cladribine is one component of the CLAG-M regimen, which is being tested in combination with venetoclax in a clinical trial.