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Bretisilocin

Phase 1

Healthy Volunteer | Small molecule | Other |AbbVie Inc.|Last Updated: May 22, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
CONTROLLEDBiomarker
Total Trials1
Total Enrollment26
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT07604558A Study to Assess the Adverse Events and How Bretisilocin Intramuscular Injection Moves Through the Body of Healthy Adult ParticipantsPHASE1 NOT YET_RECRUITING 26May 26, 2026Sep 1, 2026May 22, 2026 -
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Study Endpoints
Primary Endpoints
Number of Participants Experiencing Adverse Events
Up to approximately 32 days

An AE is defined as any untoward medical occurrence in a patient or clinical investigation participant administered a pharmaceutical product which does not necessarily have a causal relationship with this treatment.

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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeBASIC_SCIENCE
Treatment Arms
ArmTypeDescription
Group 1-Bretisilocin-JapaneseEXPERIMENTALParticipants will receive bretisilocin intramuscular (IM) injection on day 1.
Group 1-Bretisilocin-Han ChineseEXPERIMENTALParticipants will receive bretisilocin intramuscular (IM) injection on day 1.
Group 1-Bretisilocin-Non-AsianEXPERIMENTALParticipants will receive bretisilocin intramuscular (IM) injection on day 1.
Interventions
NameTypeDescription
BretisilocinDRUGIntramuscular Injection
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Eligibility Criteria
Age Range18 Years — 65 Years
SexALL
Healthy VolunteersYes

Inclusion Criteria: * Group 1: Healthy adult Japanese male or female; • Japanese participants must be first-generation Japanese of full Japanese parentage residing outside of Japan for less than 5 years. * Group 2: Healthy adult Han Chinese male or female • Han Chinese participants must be fi...

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