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APG2575

Phase 1

Waldenstrom Macroglobulinemia | Small molecule | Hematology |Ascentage Pharma Group International - American Depository Shares|Last Updated: Aug 19, 2025

Target and mechanism

Molecular targetBCL2
Target classInhibitor
ModalitySmall molecule

Also known as APG-2575, APG-2575(Lisaftoclax )

Success Probability

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Market & Valuation

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Trial Design

CONTROLLED
Total Trials1
Total Enrollment46

FDA Designations

No designations recorded

Clinical trial landscape

APG2575 · 1 trial · 1 indication

Phase 1 1
NCT04260217APG-2575 Single Agent or in Combination With Ibrutinib or Rituximab in Patients With Waldenström MacroglobulinemiaWaldenstrom Macroglobulinemia
COMPLETED46 Analytics
PHASE1COMPLETED
APG-2575 Single Agent or in Combination With Ibrutinib or Rituximab in Patients With Waldenström Macroglobulinemia
Waldenstrom MacroglobulinemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Primary Toxicity Endpoint: dose limiting toxicity (DLT)
42 days

DLT will be defined based on the rate of drug-related grade 3-5 adverse events experienced within the first 6 weeks (2 cycles) of study treatment. These will be assessed via CTCAE version 5.0

Maximally tolerated dose (MTD)
42 days

MTD will be determined based on DLTs observed during the first 6 weeks (2 cycles) of study treatment

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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
APG2575 400 mgEXPERIMENTALAPG2575 400mg ramp up arm
APG2575 600 mgEXPERIMENTALAPG2575 600 mg ramp up arm
APG2575 800 mg armEXPERIMENTALAPG2575 800 mg arm ramp up

Interventions

NameTypeDescription
APG2575 400 mgDRUGAPG2575 400 mg
APG2575 600 mgDRUGAPG2575 600 mg
APG2575 800 mgDRUGAPG2575 800 mg
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Eligibility Criteria

Age Range18 Years to 95 Years
SexALL
Healthy VolunteersNo
Study Sites14

Inclusion Criteria: * Criteria for inclusion: Patients must meet all of the following inclusion criteria to be eligible for participation in this study: 1. Local confirmed clinicopathological diagnosis of WM in accordance with the consensus panel of the Second International Workshop on WM (Owen 2...

Countries:United StatesAustraliaChina
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Frequently asked questions about APG2575

What is APG-2575 used for?

APG-2575, also known as Lisaftoclax, is an investigational small molecule being studied for several conditions, including Acute Myeloid Leukemia, Systemic Lupus Erythematosus (SLE), Waldenstrom Macroglobulinemia, Chronic Lymphocytic Leukemia, and other hematologic malignancies. It is also being evaluated in pharmacokinetic studies.

What does APG-2575 target?

APG-2575 is a small molecule that targets B-cell lymphoma 2 (BCL-2), a protein that helps cancer cells survive. By inhibiting BCL-2, APG-2575 is designed to induce apoptosis, or programmed cell death, in malignant cells. This mechanism is being explored in hematologic malignancies and autoimmune conditions like SLE.

Who makes APG-2575?

APG-2575 is being developed by Ascentage Pharma Group International, which trades under the ticker AAPG. The company is conducting clinical trials for this investigational drug across multiple indications, including Acute Myeloid Leukemia and Waldenstrom Macroglobulinemia.

What phase is APG-2575 in?

APG-2575 is in Phase 3 clinical development for Acute Myeloid Leukemia, as part of a pivotal study. It has also completed Phase 1 trials for Waldenstrom Macroglobulinemia and pharmacokinetics, and is currently recruiting for a Phase 1 study in Systemic Lupus Erythematosus.

What clinical trials is APG-2575 in?

APG-2575 is being studied in several clinical trials. NCT06389292 is a Phase 3 trial combining APG-2575 with azacitidine for Acute Myeloid Leukemia. NCT06182969 is a Phase 1 trial for SLE. Completed trials include NCT04260217 for Waldenstrom Macroglobulinemia and NCT05517616 for pharmacokinetics.

Is APG-2575 the same as Lisaftoclax?

Yes, APG-2575 is also known as Lisaftoclax. The drug is referred to by both names in clinical research, with Lisaftoclax being the generic name. It is an investigational BCL-2 inhibitor being developed by Ascentage Pharma for various cancers and autoimmune diseases.