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APG-2575

Phase 3

Acute Myeloid Leukemia | Small molecule | Oncology |Ascentage Pharma Group International - American Depository Shares|Last Updated: May 1, 2026

Target and mechanism

Molecular targetBCL2
Target classInhibitor
ModalitySmall molecule

Also known as APG2575, APG-2575(Lisaftoclax )

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindACTIVE_CONTROLLEDDMC
Total Trials1
Total Enrollment486

FDA Designations

No designations recorded

Clinical trial landscape

APG-2575 · 7 trials · 7 indications

Phase 3 1Phase 2 1Phase 1 4Early Phase 1 1
NCT06389292A Pivotal Study of APG-2575 (Lisaftoclax) Combined With Azacitidine in the Treatment of Acute Myeloid LeukemiaAcute Myeloid Leukemia
RECRUITING486 Analytics
PHASE3RECRUITING
A Pivotal Study of APG-2575 (Lisaftoclax) Combined With Azacitidine in the Treatment of Acute Myeloid Leukemia
Acute Myeloid LeukemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Overall Survival(OS)
Up to 5 years

The primary endpoint was overall survival (OS), defined as the time from the date of randomization to the date of death of any cause.

Objective Response Rate (ORR)
Up to 9 months after the last subject enrolled.

ORR is defined by Complete Remission (CR)+ CR with incomplete marrow recovery (CRi) + Partial Remission (PR) (according to NCI-WG CLL(2018)) and by CR+PR ( according to Lugano (2014)).Response will be evaluated every 2 cycles (8 weeks) till complete treatment or one month after last dose.

Number of participants with treatment-related adverse events as assessed by CTCAE v5.0.
Up to 1 year

According to CTCAE v5.0, the number and frequency of adverse events of test drug were assessed.

Radioactivity concentration of each blood and plasma sample
Day 1- Day 8

Use liquid scintillation counter to evaluate Radioactivity concentration of each blood and plasma sample.

Radioactivity concentration in each urine and feces sample.
Day 1- Day 15

Use liquid scintillation counter to evaluate Radioactivity concentration of each sample.

Number of metabolites and its proportion in plasma, urine and feces.
Day 1- Day 15

To elucidate the pathways of biotransformation.

Adverse events of APG-2575 single agent
Up to 6 cycles (each cycle is 28 days).

Adverse events (AE) and serious adverse events (SAE) will be graded according to NCI CTCAE Version 5.0.

Objective Response Rate (ORR) of APG-2575 single agent
Up to 6 cycles (each cycle is 28 days).

ORR is defined by CR+ CRi + PR(according to NCI-WG CLL(2008)) and by CR+PR ( according to NHL Cheson (2007)).Response will be evaluated every 2 cycles (8 weeks) till complete 6 cycles treatment or one month after last dose.

Dose Limiting Toxicities (DLT) of combination therapy
28 days.

DLT will be graded according to NCI CTCAE Version 5.0. DLT will be defined as clinically significant drug-related adverse events during the cycle one.

Maximum Tolerated Dose (MTD)/Recommended Phase 2 Dose(RP2D)
28 days.

MTD/RP2D will be determined based on DLTs observed during cycle one.

Maximum Tolerated Dose (MTD)
28 days

Patients with APG-2575 treatment related adverse events (AE), serious adverse events (SAE) will be assessed according NCI CTCAE Version 5.0

Secondary Endpoints

Percentage of Participants with Objective Response Rate (ORR)
Up to 5 years
Safety evaluation based on the adverse event concurrence
Up to 5 years
Progress Free Survival (PFS)
Up to 9 months after the last subject enrolled.
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Study Design & Arms

AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
APG-2575 (Lisaftoclax) combined with AzacitidineEXPERIMENTAL -
Placebo combined with AzacitidineACTIVE_COMPARATOR -
APG-2575 single agent in Relapse/Refractory CLL/SLLEXPERIMENTALAPG-2575 orally once daily at 600mg dose levels, every 28 days as a cycle.
APG-2575EXPERIMENTALDose escalation
PlaceboPLACEBO_COMPARATOR -
[14C]APG-2575EXPERIMENTALTo investigate the absorption properties, as well as to evaluate the mass balance and elucidate the pathways of biotransformation after a single oral dose of 400mg, 200μCi \[14C\] APG-2575 to healthy subjects.
APG-2575+Rituximab in Relapse/Refractory CLL/SLLEXPERIMENTALStage 1:APG-2575 orally once daily starting from 200mg and will be increased in subsequent cohorts to 400mg, 600mg, 800mg. Rituximab 375mg/m2 ivgtt on C1D8 and 500mg/m2 ivgtt on C2-6D1. Every 28 days as a cycle. Stage 2: APG-2575 MTD/RP2D combined with rituximab. Every 28 days as a cycle.
APG-2575+ibrutinib in Relapse/Refractory CLL/SLLEXPERIMENTALStage 1: APG-2575 orally once daily starting from 200mg and will be increased in subsequent cohorts to 400mg, 600mg, 800mg.Ibrutinib 420mg orally once daily during C1D8-28 and following cycles. Every 28 days as a cycle. Stage 2: APG-2575 MTD/RP2D combined with ibrutinib. Every 28 days as a cycle.
single-agent, open-label, Phase I study of APG-2575EXPERIMENTALThe study consists of the dose escalation stage and the dose expansion stage

Interventions

NameTypeDescription
APG-2575(Lisaftoclax )DRUGQD, oral administration, every 28 days for a dosing cycle.
PlaceboOTHERQD, oral administration, every 28 days for a dosing cycle.
Azacitidine InjectionDRUGQD, subcutaneous or intravenous injection, D1-7 in 28-day cycle.
APG2575DRUGAPG-2575 orally once daily at 600mg dose levels, every 28 days as a cycle.
APG-2575DRUGTake orally once daily (QD) for 12 weeks.
[14C ]APG-2575DRUGorally, single dose of 400 mg / 200 μCi \[14C\] APG-2575
RituximabDRUGRituximab 375mg/m2 ivgtt on C1D8 and 500mg/m2 ivgtt on C2-6D1.
IbrutinibDRUGIbrutinib 420mg orally once daily during C1D8-28 and following cycles.
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites6

Inclusion Criteria: 1. Patients must have newly diagnosed AML that meets the criteria for acute myeloid leukemia (AML) and ineligible for standard chemotherapy. 2. Life expectancy of ≥3 months. 3. Be able to accept oral administration. 4. Patients aged ≥70 years with ECOG score of 0-2, or those age...

Countries:ChinaRussiaUnited StatesAustralia
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Recent Changes (Last 90 Days)

HIGHSep 1, 2026NCT03537482TRIAL_REMOVED: changed
HIGHSep 1, 2026NCT03537482TRIAL_REMOVED: changed
HIGHSep 1, 2026NCT03537482TRIAL_REMOVED: changed
MEDIUMAug 1, 2026NCT04494503Phase: PHASE2 → PHASE1
MEDIUMAug 1, 2026NCT06389292primaryCompletionDate: changed
MEDIUMAug 1, 2026NCT03537482primaryCompletionDate: changed
MEDIUMAug 1, 2026NCT05147467primaryCompletionDate: changed
MEDIUMAug 1, 2026NCT06182969Phase: PHASE2 → PHASE1
MEDIUMAug 1, 2026NCT03913949primaryCompletionDate: changed
MEDIUMAug 1, 2026NCT06389292primaryCompletionDate: changed
MEDIUMAug 1, 2026NCT06182969Phase: PHASE2 → PHASE1
MEDIUMAug 1, 2026NCT03537482primaryCompletionDate: changed
MEDIUMAug 1, 2026NCT05147467primaryCompletionDate: changed
MEDIUMAug 1, 2026NCT04494503Phase: PHASE2 → PHASE1
MEDIUMAug 1, 2026NCT03913949primaryCompletionDate: changed
MEDIUMAug 1, 2026NCT05147467primaryCompletionDate: changed
MEDIUMAug 1, 2026NCT04494503Phase: PHASE2 → PHASE1
MEDIUMAug 1, 2026NCT06182969Phase: PHASE2 → PHASE1
MEDIUMAug 1, 2026NCT06389292primaryCompletionDate: changed
MEDIUMAug 1, 2026NCT03537482primaryCompletionDate: changed

Frequently asked questions about APG-2575

What is APG-2575 used for?

APG-2575, also known as Lisaftoclax, is an investigational small molecule being studied for several conditions, including Acute Myeloid Leukemia, Systemic Lupus Erythematosus (SLE), Waldenstrom Macroglobulinemia, Chronic Lymphocytic Leukemia, and other hematologic malignancies. It is also being evaluated in pharmacokinetic studies.

What does APG-2575 target?

APG-2575 is a small molecule that targets B-cell lymphoma 2 (BCL-2), a protein that helps cancer cells survive. By inhibiting BCL-2, APG-2575 is designed to induce apoptosis, or programmed cell death, in malignant cells. This mechanism is being explored in hematologic malignancies and autoimmune conditions like SLE.

Who makes APG-2575?

APG-2575 is being developed by Ascentage Pharma Group International, which trades under the ticker AAPG. The company is conducting clinical trials for this investigational drug across multiple indications, including Acute Myeloid Leukemia and Waldenstrom Macroglobulinemia.

What phase is APG-2575 in?

APG-2575 is in Phase 3 clinical development for Acute Myeloid Leukemia, as part of a pivotal study. It has also completed Phase 1 trials for Waldenstrom Macroglobulinemia and pharmacokinetics, and is currently recruiting for a Phase 1 study in Systemic Lupus Erythematosus.

What clinical trials is APG-2575 in?

APG-2575 is being studied in several clinical trials. NCT06389292 is a Phase 3 trial combining APG-2575 with azacitidine for Acute Myeloid Leukemia. NCT06182969 is a Phase 1 trial for SLE. Completed trials include NCT04260217 for Waldenstrom Macroglobulinemia and NCT05517616 for pharmacokinetics.

Is APG-2575 the same as Lisaftoclax?

Yes, APG-2575 is also known as Lisaftoclax. The drug is referred to by both names in clinical research, with Lisaftoclax being the generic name. It is an investigational BCL-2 inhibitor being developed by Ascentage Pharma for various cancers and autoimmune diseases.