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TX200-TR101

Phase 1

Kidney Transplant Rejection | Monoclonal antibody | Nephrology |Sangamo Therapeutics, Inc.|Last Updated: Feb 10, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
NO_TREATMENT_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment26
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT04817774Safety & Tolerability Study of Chimeric Antigen Receptor T-Reg Cell Therapy in Living Donor Renal Transplant RecipientsPHASE1 ACTIVE NOT_RECRUITING 26Mar 17, 2021Oct 29, 2025Feb 10, 20255 Belgium, Netherlands +1
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Study Endpoints
Primary Endpoints
Safety and Tolerability
28 days post infusion

Safety and tolerability of TX200-TR101 infusion evaluated by incidence and grade of treatment-emergent adverse events (TEAEs), including serious adverse events (SAEs) according to CTCAE V5.0.

Secondary Endpoints
Acute graft related outcomes
Day of infusion through to Week 84
Long-term safety
Day of infusion through to Week 84
Immunosuppression
Day of infusion through to Week 84
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposePREVENTION
Treatment Arms
ArmTypeDescription
Treatment groupEXPERIMENTALSubjects undergo kidney transplant as per planned standard of care and are administered study drug post transplantation.
Control group and Transplant donorsNO_INTERVENTIONControl group: Subjects undergo kidney transplant as per planned standard of care with no study drug administered. Transplant donors: Transplant donors for each subject in the treatment and control groups.
Interventions
NameTypeDescription
TX200-TR101BIOLOGICALTX200-TR101 is an autologous gene therapy medicinal product composed of Treg cells (CD4+/CD45RA+/CD25+/CD127low/neg) that have been ex vivo expanded and transduced with a lentiviral vector encoding for a CAR to recognize HLA-A\*02. Treatment will be given via an IV infusion at a pre-defined timepoint several weeks after transplant. Four, single ascending dose cohorts of TX200-TR101 are planned and an additional expansion cohort.
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Eligibility Criteria
Age Range18 Years — 70 Years
SexALL
Healthy VolunteersNo
Study Sites5

Inclusion Criteria: * Written informed consent. * Male or female aged 18 - 70 years. * Diagnosis of End Stage Renal Disease and waiting for a new kidney from an identified live donor. * Subjects who will be single organ recipients (kidney). * Able and willing to use contraception. Exclusion Criter...

Countries:BelgiumNetherlandsUnited Kingdom
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT04817774primaryCompletionDate: changed
LOWMay 24, 2026NCT04817774studyFirstPostDate: changed