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Part C: RM-718

Phase 1

Hypothalamic Obesity | Small molecule | Metabolic |Rhythm Pharmaceuticals, Inc.|Last Updated: Dec 22, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindCONTROLLEDBiomarker
Total Trials1
Total Enrollment150
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT06239116A Study of RM-718 in Healthy Subjects and Patients With MC4R Pathway ImpairmentPHASE1 RECRUITING 150Mar 5, 2024Nov 1, 2028Dec 22, 20257 United States
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Study Endpoints
Primary Endpoints
Parts A, B, C, D: Safety and Tolerability Assessed by Number of Study Participants with Treatment-Emergent Adverse Events (TEAEs) and Serious Adverse Events (SAEs)
From Day 1 through the Safety-Follow-up call (up to Day 43 for all Part A cohorts, up to Day 70 for all Part B cohorts, up to Day 140 for Part C cohort, up to Day 210 for Part D cohort)
Secondary Endpoints
AUCtau measurement of RM-718
up to 168 hours post-dose on Day 1 (Parts A, B and C) and 168 hours post-dose on Day 22 (Parts B and C).
Cmax measurement of RM-718
up to 168 hours post-dose on Day 1 (Parts A, B and C) and 168 hours post-dose on Day 22 (Parts B and C).
Cmin measurement of RM-718
up to 168 hours post-dose on Day 1 (Parts A, B and C) and 168 hours post-dose on Day 22 (Parts B and C).
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Study Design & Arms
AllocationRANDOMIZED
MaskingTRIPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
RM-718 (Cohort A1)EXPERIMENTALSingle dose of RM-718 (4) or placebo (2)
RM-718 (Cohort A2)EXPERIMENTALSingle dose of RM-718 (4) or placebo (2)
RM-718 (Cohort A3)EXPERIMENTALSingle dose of RM-718 (4) or placebo (2)
RM-718 (Cohort A4)EXPERIMENTALSingle dose of RM-718 (4) or placebo (2)
RM-718 (Cohort A5)EXPERIMENTALSingle dose of RM-718 (4) or placebo (2)
RM-718 (Cohort A6)EXPERIMENTALSingle dose of RM-718 (4) or placebo (2)
RM-718 (Cohort A7)EXPERIMENTALSingle dose of RM-718 (4) or placebo (2)
RM-718 (Cohort A8)EXPERIMENTALSingle dose of RM-718 (4) or placebo (2)
RM-718 (Cohort A9)EXPERIMENTALSingle dose of RM-718 (4) or placebo (2)
RM-718 (Cohort B1)EXPERIMENTALMultiple ascending doses of RM-718 (4) or placebo (2)
RM-718 (Cohort B2)EXPERIMENTALMultiple ascending doses of RM-718 (4) or placebo (2)
RM-718 (Cohort B3)EXPERIMENTALMultiple ascending doses of RM-718 (4) or placebo (2)
RM-718 (Cohort B4)EXPERIMENTALMultiple ascending doses of RM-718 (4) or placebo (2)
RM-718 (Cohort B5)EXPERIMENTALMultiple ascending doses of RM-718 (4) or placebo (2)
RM-718 (Cohort B6)EXPERIMENTALMultiple ascending doses of RM-718 (4) or placebo (2)
RM-718 (Cohort C1)EXPERIMENTALMultiple ascending doses of RM-718 (30)
RM-718 (Cohort D1)EXPERIMENTALMultiple ascending doses of RM-718 (up to 30)
Interventions
NameTypeDescription
Part A: RM-718 or placebo (matched to specific RM-718 dose cohort)DRUGSingle ascending dose of RM-718 or placebo (matched to specific RM-718 Part A dose cohort)
Part B: RM-718 or placebo (matched to specific RM-718 dose cohort)DRUGMultiple ascending doses of RM-718 or placebo (matched to specific RM-718 Part B dose cohorts)
Part C: RM-718DRUGMultiple ascending doses of RM-718
Part D: RM-718DRUGMultiple ascending doses of RM-718
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Eligibility Criteria
Age Range12 Years — 65 Years
SexALL
Healthy VolunteersYes
Study Sites7

Key Inclusion Criteria: Parts A and B: * Male and female subjects in good health aged 18-55 years of age at Screening. * Body mass index (BMI) ≥30 kg/m2. * Subjects who are medically healthy with normal or clinically insignificant screening results. * Subjects must use a highly effective form of c...

Countries:United States
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT06239116primaryCompletionDate: changed
LOWMay 24, 2026NCT06239116studyFirstPostDate: changed