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Tulmimetostat

Phase 1

Mycosis Fungoides | Small molecule | Other |Novartis AG|Last Updated: May 20, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment24
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT05944562Tulmimetostat (DZR123) in Patients With Mycosis Fungoides and Sézary SyndromePHASE1 ACTIVE NOT_RECRUITING 24Jan 9, 2024Jan 31, 2029May 20, 20261 United States
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Study Endpoints
Primary Endpoints
Frequency and grades of treatment-emergent adverse events (TEAE)
From start of treatment through 30 days after completion of treatment (estimated to be 13 months)
Rate of treatment discontinuation due to treatment-emergent adverse events (TEAE)
From start of treatment through 30 days after completion of treatment (estimated to be 13 months)
Secondary Endpoints
Recommended phase II dose/maximum tolerated dose of CPI-0209
Through completion of cycle 1 (28 days) of all dose de-escalation patients enrolled (each patient followed for 28 days)
Overall response rate (ORR)
At 4 months
Time to maximum response
Through completion of treatment (estimated to be 12 months)
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Dose De-Escalation Cohort: Tulmimetostat (DZR123)EXPERIMENTALDaily DZR123 by mouth for days 1-28 of each 28-day cycle. Dose will depend on dose level assignment of 300 mg daily, 250 mg daily, or 200 mg daily.
Dose Expansion Cohort: Tulmimetostat (DZR123) - 300 mgEXPERIMENTALDaily DZR123by mouth for days 1-28 of each 28-day cycle. Dose will be the maximum-tolerated dose found during the dose de-escalation cohort which was 300 mg.
Dose Expansion Cohort: Tulmimetostat (DZR123) - 200 mgEXPERIMENTALDaily DZR123 by mouth for days 1-28 of each 28-day cycle. Dose will be 200 mg as the maximum tolerated dose of 300 mg found during the initial dose expansion cohort caused numerous dose reductions.
Interventions
NameTypeDescription
TulmimetostatDRUGPatients should take DZR123 at approximately the same time every morning in a fasted state (no food for 2 hours prior and 1 hour following DZR123 dosing). Each dose of DZR123 should be taken with a glass of water and consumed over as short a time as possible.
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: * Histologically or cytologically confirmed mycosis fungoides or Sézary syndrome, stages IB to IVB with measurable disease and/or detectable blood involvement based on the Global Response Criteria for CTCL (Olsen et al., 2022). * Received at least one prior line of systemic ther...

Countries:United States
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Recent Changes (Last 90 Days)
LOWMay 24, 2026NCT05944562studyFirstPostDate: changed