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Pacritinib

Phase 2

Myelofibrosis | Small molecule | Hematology |Karyopharm Therapeutics Inc.|Last Updated: Mar 18, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment26
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT07447817Selinexor and Pacritinib in JAK Inhibitor-naïve MF Patients With CytopeniasPHASE2 NOT YET_RECRUITING 26May 4, 2026May 24, 2030Mar 18, 20263 United States
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Study Endpoints
Primary Endpoints
Change in spleen volume
Baseline and 24 weeks

Evaluate clinical efficacy of pacritinib and selinexor in myelofibrosis patients who are JAK inhibitor-naïve and have anemia and thrombocytopenia by assessing spleen volume reduction (SVR) of 35% or greater compared to baseline as measured by imaging (MRI/CT)

Secondary Endpoints
Spleen response rate
At 24 weeks and 48 weeks
Change in the Myelofibrosis-Symptom Assessment Form Total Symptom Score (MF-SAF TSS)
At 24 weeks and 48 weeks
Change in Patient Global Impression of Change (PGIC)
At 24 weeks and 48 weeks
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Pacritinib/SelinexorEXPERIMENTALStudy participants will receive pacritinib monotherapy (200mg BID orally) for the first cycle (28 days). If they qualify to add on selinexor at any point from Cycle 2 Day 1 to Cycle 4 Day 1, participants will have selinexor (60mg QW orally) added onto their pacritinib regimen.
Interventions
NameTypeDescription
PacritinibDRUGPacritinib 200mg twice a day (BID) by mouth (PO)
SelinexorDRUGSelinexor 60mg once weekly (QW) by mouth (PO)
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites3

Inclusion Criteria: * Adults ≥ 18 years of age capable of providing informed consent * Pathologically confirmed diagnosis of PMF, post-ET MF, or post-PV MF as per the World Health Organization (WHO) diagnostic criteria - Intermediate-1, Intermediate-2, or High-Risk disease by the Dynamic Internatio...

Countries:United States
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT07447817primaryCompletionDate: changed
LOWMay 24, 2026NCT07447817studyFirstPostDate: changed