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Pacritinib

Phase 2

Myelofibrosis | Small molecule | Oncology |Karyopharm Therapeutics Inc.|Last Updated: Mar 18, 2026

Target and mechanism

Molecular targetACVR1, JAK2, FLT3, IRAK1
Target classInhibitor
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDDMC
Total Trials1
Total Enrollment26

FDA Designations

No designations recorded

Clinical trial landscape

Pacritinib · 1 trial · 3 indications

Phase 2 1
NCT07447817Selinexor and Pacritinib in JAK Inhibitor-naïve MF Patients With CytopeniasMyelofibrosis
NOT YET_RECRUITING26 Analytics
PHASE2NOT YET_RECRUITING
Selinexor and Pacritinib in JAK Inhibitor-naïve MF Patients With Cytopenias
MyelofibrosisUnlock trial analytics

Study Endpoints

Primary Endpoints

Change in spleen volume
Baseline and 24 weeks

Evaluate clinical efficacy of pacritinib and selinexor in myelofibrosis patients who are JAK inhibitor-naïve and have anemia and thrombocytopenia by assessing spleen volume reduction (SVR) of 35% or greater compared to baseline as measured by imaging (MRI/CT)

Secondary Endpoints

Spleen response rate
At 24 weeks and 48 weeks
Change in the Myelofibrosis-Symptom Assessment Form Total Symptom Score (MF-SAF TSS)
At 24 weeks and 48 weeks
Change in Patient Global Impression of Change (PGIC)
At 24 weeks and 48 weeks
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Pacritinib/SelinexorEXPERIMENTALStudy participants will receive pacritinib monotherapy (200mg BID orally) for the first cycle (28 days). If they qualify to add on selinexor at any point from Cycle 2 Day 1 to Cycle 4 Day 1, participants will have selinexor (60mg QW orally) added onto their pacritinib regimen.

Interventions

NameTypeDescription
PacritinibDRUGPacritinib 200mg twice a day (BID) by mouth (PO)
SelinexorDRUGSelinexor 60mg once weekly (QW) by mouth (PO)
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites3

Inclusion Criteria: * Adults ≥ 18 years of age capable of providing informed consent * Pathologically confirmed diagnosis of PMF, post-ET MF, or post-PV MF as per the World Health Organization (WHO) diagnostic criteria - Intermediate-1, Intermediate-2, or High-Risk disease by the Dynamic Internatio...

Countries:United States
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Frequently asked questions about Pacritinib

What is Pacritinib used for in myelofibrosis?

Pacritinib is an investigational small molecule being studied for the treatment of myelofibrosis, including post-polycythemia vera myelofibrosis and post-essential thrombocythemia myelofibrosis. It is currently in Phase 2 clinical development for this indication.

What does Pacritinib target?

Pacritinib is a kinase inhibitor, belonging to the -tinib class of drugs. It works by inhibiting certain kinases, which are enzymes involved in cell signaling and growth. This mechanism is being explored as a potential treatment for myelofibrosis.

Who makes Pacritinib?

Pacritinib is being developed by Karyopharm Therapeutics Inc., a biopharmaceutical company. Karyopharm is listed on the stock exchange under the ticker symbol KPTI.

What phase is Pacritinib in?

Pacritinib is currently in Phase 2 clinical development. It is an investigational drug, meaning it has not yet been approved by regulatory authorities. It is being studied in a clinical trial for patients with myelofibrosis.

What clinical trials is Pacritinib in?

Pacritinib is being studied in a Phase 2 clinical trial with the identifier NCT07447817. This trial is investigating the combination of selinexor and pacritinib in JAK inhibitor-naive patients with myelofibrosis who have cytopenias. The trial is not yet recruiting and plans to enroll 26 participants in the United States.

Is Pacritinib the same as selinexor?

No, Pacritinib is not the same as selinexor. They are different drugs being studied in combination in a clinical trial for myelofibrosis. Pacritinib is a kinase inhibitor, while selinexor is a separate investigational agent. The trial NCT07447817 is evaluating both drugs together.