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ONX-0801

Phase 1

Solid Tumours | Small molecule | Oncology |United Therapeutics Corporation|Last Updated: Sep 26, 2024

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
CONTROLLEDBiomarker
Total Trials1
Total Enrollment111
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT02360345Phase I Trial of ONX-0801 Once Weekly or Alternate WeeklyPHASE1 COMPLETED 111Sep 1, 2013Mar 1, 2021Sep 26, 20241 United Kingdom
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Study Endpoints
Primary Endpoints
Maximum Tolerated Dose
2 cycles (56 days)

Establish the maximum tolerated dose of ONX-0801 when given on a weekly or alternate weekly schedule.

Safety and Toxicity Profile 9adverse event to ONX-0801 and grading severity according to the National Cancer Institute (NCI) Common Terminology Criteria for Adverse Events (CTCAE) Version 4.0)
2 cycles (56 days)

Assign causality of each adverse event to ONX-0801 and grading severity according to the National Cancer Institute (NCI) Common Terminology Criteria for Adverse Events (CTCAE) Version 4.0

Secondary Endpoints
Pharmacokinetic profile of ONX-0801 (Cmax, AUC and volume of distribution)
36 months
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
q1week scheduleEXPERIMENTALONX-0801 will be administered over a 1-hour IV infusion on Days 1, 8, 15 and 22 of repeated 28-day treatment cycles.
q2week scheduleEXPERIMENTALONX-0801 will be administered over a 1-hour IV infusion on Days 1 and 15 of repeated 28-day treatment cycles.
Interventions
NameTypeDescription
ONX-0801DRUG -
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: * Patients with histologically or cytologically proven solid tumours (to include Non-Hodgkin's and Hodgkin's lymphoma). Patients must have disease which has failed standard therapy or for whom no standard curative therapy exists. At the dose expansion phase, entry will be limite...

Countries:United Kingdom
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